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Global Rare Disease Treatment Market (2023-2028) Competitive Analysis, Impact of Covid-19, Ansoff Analysis

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    Report

  • 220 Pages
  • February 2024
  • Region: Global
  • Infogence Global Research
  • ID: 5910252
The Global Rare Disease Treatment Market is estimated to be USD 139.34 Bn in 2023 and is expected to reach USD 235.86 Bn by 2028 growing at a CAGR of 11.1%.

Market dynamics, which refers to the ever-changing and evolving conditions, trends, and forces that impact the industries, is crucial for industry overview. It includes consumer demands, competition, technological advancements, economic shifts, and regulatory changes. We monitor the market and analyze the balance between demand and supply. Market dynamics that include drivers, restraints, opportunities, challenges, and insights are needed to make strategic decisions, whether entering new markets, launching new products, or setting pricing strategies.

The emerging trends in the market require market analysis to help set goals, make informed decisions about market entry and product development pricing, and inspire innovation to stay competitive and meet changing requirements. One of the most important elements is to analyze competitors to identify the gaps specific to the geographic location, product offerings, pricing, and opportunity areas for growth in internal and external development.

Understanding consumer behavior and market trends holistically is necessary to expand the company into new horizons and position itself in a new or existing market. It helps gain a competitive edge, save time & money, and reduce risks in the long term.

Market Segmentations

  • The Global Rare Disease Treatment Market is segmented based on Therapeutic Area, Drug Type, Drug Class, Mode of Administration, Distribution Channel, and Geography.
  • By Drug Class, the market is segmented based on Originator Drugs and Generic Drugs.
  • Originator drugs, often patented molecules, are innovative pharmaceuticals developed by research-based pharmaceutical companies. These drugs are typically the first of their kind and are protected by patents, granting the developer exclusive rights to produce and sell the drug for a specific period. Originator drugs are crucial in addressing unmet medical needs for rare diseases. Their development involves significant research, innovation, and investment to create effective treatments for conditions with limited therapeutic options. Patented molecules enjoy a period of market exclusivity, during which competing generic versions are not allowed. This exclusivity enables pharmaceutical companies to recoup their research and development costs and generate profits, encouraging continued investment in rare disease drug development. While originator drugs bring groundbreaking therapeutic options, they often come with a higher price tag due to the costs associated with research, development, and regulatory approval. This pricing model can pose challenges for accessibility and affordability, leading to discussions around healthcare equity and reimbursement policies.
  • Generic drugs are bioequivalent versions of originator drugs that become available after the originator drug's patent expires. Generic drugs provide the same therapeutic effects as the original drug but are typically more affordable. Generic drugs contribute to increased accessibility to rare disease treatments by offering more affordable alternatives. Once the patent protection for originator drugs expires, introducing generic versions fosters competition, driving down costs and expanding patient access. Generic drugs must demonstrate bioequivalence to the originator drug, ensuring comparable efficacy and safety. This regulatory requirement assures healthcare providers and patients that the generic version is a reliable alternative to the original treatment. Introducing generic drugs introduces market competition, promoting cost-effectiveness and potentially lowering healthcare expenditures. This competitive landscape can incentivize pharmaceutical companies to enhance manufacturing efficiency and explore new therapeutic areas.

Recent Development

  • The Indian government has instructed national and state governments to ensure the efficient implementation of health policies for treating patients afflicted with orphan diseases. This directive allows manufacturers to supply premium-quality orphan medicines to the government, presenting a chance to generate revenue. -July 2022

Company Profiles

The report provides a detailed analysis of the competitors in the market. It covers the financial performance analysis for the publicly listed companies in the market. The report also offers detailed information on the companies' recent development and competitive scenario. Some of the companies covered in this report are AbbVie Inc., AstraZeneca, Bayer AG, etc.

Countries Studied

  • America (Argentina, Brazil, Canada, Chile, Colombia, Mexico, Peru, United States, Rest of Americas)
  • Europe (Austria, Belgium, Denmark, Finland, France, Germany, Italy, Ireland, Luxembourg, Netherlands, Norway, Poland, Russia, Spain, Sweden, Switzerland, United Kingdom, Rest of Europe)
  • Middle East and Africa (Egypt, Israel, Qatar, Nigeria, Saudi Arabia, South Africa, United Arab Emirates, Rest of MEA)
  • Asia-Pacific (Australia, Bangladesh, China, India, Indonesia, Japan, Malaysia, Philippines, Singapore, South Korea, Sri Lanka, Thailand, Taiwan, Rest of Asia-Pacific)

Competitive Quadrant

The report includes Competitive Quadrant, a proprietary tool to analyse and evaluate the position of companies based on their Industry Position score and Market Performance score. The tool uses various factors for categorizing the players into four categories. Some of these factors considered for analysis are financial performance over the last 3 years, growth strategies, innovation score, new product launches, investments, growth in market share, etc.

Ansoff Analysis

  • The report presents a detailed Ansoff matrix analysis for the Global Rare Disease Treatment Market. Ansoff Matrix, also known as Product/Market Expansion Grid, is a strategic tool used to design strategies for the growth of the company. The matrix can be used to evaluate approaches in four strategies viz. Market Development, Market Penetration, Product Development and Diversification. The matrix is also used for risk analysis to understand the risk involved with each approach.
  • The publisher analyses the Global Rare Disease Treatment Market using the Ansoff Matrix to provide the best approaches a company can take to improve its market position.
  • Based on the SWOT analysis conducted on the industry and industry players, the publisher has devised suitable strategies for market growth.

Why buy this report?

  • The report offers a comprehensive evaluation of the Global Rare Disease Treatment Market. The report includes in-depth qualitative analysis, verifiable data from authentic sources, and projections about market size. The projections are calculated using proven research methodologies.
  • The report has been compiled through extensive primary and secondary research. The primary research is done through interviews, surveys, and observation of renowned personnel in the industry.
  • The report includes an in-depth market analysis using Porter's 5 forces model, PESTLE Analysis, and the Ansoff Matrix. In addition, the impact of COVID-19 and the impact of economic slowdown & impending recession on the market are also featured in the report.
  • The report also includes the regulatory scenario in the industry, which will help you make a well-informed decision. The report discusses major regulatory bodies and major rules and regulations imposed on this sector across various geographies.
  • The report also contains the competitive analysis using Positioning Quadrants, the Proprietary competitive positioning tool.

Report Highlights

  • A complete analysis of the market, including parent industry
  • Important market dynamics and trends
  • Market segmentation
  • Historical, current, and projected size of the market based on value and volume
  • Market shares and strategies of key players
  • Recommendations to companies for strengthening their foothold in the market

Table of Contents

1 Report Description
1.1 Study Objectives
1.2 Market Definition
1.3 Currency
1.4 Years Considered
1.5 Language
1.6 Key Stakeholders
2 Research Methodology
2.1 Research Process
2.2 Data Collection and Validation
2.2.1 Secondary Research
2.2.2 Primary Research
2.2.3 Models
2.3 Market Size Estimation
2.3.1 Bottom-Up Approach
2.3.2 Top-Down Approach
2.4 Assumptions of the Study
2.5 Limitations of the Study
3 Executive Summary
3.1 Introduction
3.2 Market Size, Segmentations and Outlook
4 Market Dynamics
4.1 Drivers
4.1.1 Increasing Awareness among People and Social Groups
4.1.2 Rising Facilities for Patients Affected by Rare Disease
4.2 Restraints
4.2.1 Lack of Government Regulatory Framework
4.3 Opportunities
4.3.1 Increasing Incentives for Research to Promote Health and Treat Rare Diseases
4.4 Challenges
4.4.1 Lack of Skilled Healthcare Personnel
5 Market Analysis
5.1 Regulatory Scenario
5.2 Porter's Five Forces Analysis
5.3 PESTEL Analysis
5.4 SWOT Analysis
5.5 Impact of Covid-19
5.6 Ansoff Matrix Analysis
6 Global Rare Disease Treatment Market, By Therapeutic Area
6.1 Introduction
6.2 Hematology
6.3 Genetic Diseases
6.4 Neurological Diseases
6.5 Oncology
6.6 Infectious Diseases
6.7 Inflammatory Diseases
6.8 Metabolic Diseases
6.9 Pulmonary Diseases
6.10 Kidney Diseases
6.11 Musculoskeletal Diseases
6.12 Endocrine Diseases
6.13 Skin Disorders
7 Global Rare Disease Treatment Market, By Drug Type
7.1 Introduction
7.2 Originator Drugs (Patented Molecules)
7.3 Generic Drugs
8 Global Rare Disease Treatment Market, By Drug Class
8.1 Introduction
8.2 Biologics
8.3 Organic Compounds
9 Global Rare Disease Treatment Market, By Mode of Administration
9.1 Introduction
9.2 Injectable
9.3 Oral
10 Global Rare Disease Treatment Market, By Distribution Channel
10.1 Introduction
10.2 Hospital Pharmacies
10.3 Specialty Pharmacies
10.4 Retail Pharmacies
11 Americas' Rare Disease Treatment Market
11.1 Introduction
11.2 Argentina
11.3 Brazil
11.4 Canada
11.5 Chile
11.6 Colombia
11.7 Mexico
11.8 Peru
11.9 United States
11.10 Rest of Americas
12 Europe's Rare Disease Treatment Market
12.1 Introduction
12.2 Austria
12.3 Belgium
12.4 Denmark
12.5 Finland
12.6 France
12.7 Germany
12.8 Italy
12.9 Ireland
12.10 Luxembourg
12.11 Netherlands
12.12 Norway
12.13 Poland
12.14 Russia
12.15 Spain
12.16 Sweden
12.17 Switzerland
12.18 United Kingdom
12.19 Rest of Europe
13 Middle East and Africa's Rare Disease Treatment Market
13.1 Introduction
13.2 Egypt
13.3 Israel
13.4 Nigeria
13.5 Qatar
13.6 Saudi Arabia
13.7 South Africa
13.8 United Arab Emirates
13.9 Rest of MEA
14 APAC's Rare Disease Treatment Market
14.1 Introduction
14.2 Australia
14.3 Bangladesh
14.4 China
14.5 India
14.6 Indonesia
14.7 Japan
14.8 Malaysia
14.9 Philippines
14.10 Singapore
14.11 South Korea
14.12 Sri Lanka
14.13 Thailand
14.14 Taiwan
14.15 Rest of Asia-Pacific
15 Competitive Landscape
15.1 Competitive Quadrant
15.2 Market Share Analysis
15.3 Strategic Initiatives
15.3.1 M&A and Investments
15.3.2 Partnerships and Collaborations
15.3.3 Product Developments and Improvements
16 Company Profiles
16.1 AbbVie Inc.
16.2 AstraZeneca
16.3 Bayer AG
16.4 Bristol Myers Squibb
16.5 F. Hoffmann-La Roche Ltd
16.6 Merck & Co. Inc.
16.7 Novartis AG
16.8 Novo Nordisk
16.9 Pfizer, Inc.
16.10 PTC Therapeutics
17 Appendix
17.1 Questionnaire

Companies Mentioned

  • AbbVie Inc.
  • AstraZeneca
  • Bayer AG
  • Bristol Myers Squibb
  • F. Hoffmann-La Roche Ltd
  • Merck & Co. Inc.
  • Novartis AG
  • Novo Nordisk
  • Pfizer, Inc.
  • PTC Therapeutics

Table Information