Global Rett Syndrome Market: Industry Analysis & Outlook (2017-2025)

  • ID: 4318703
  • Drug Pipelines
  • Region: Global
  • 64 Pages
  • Koncept Analytics
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Growth of Rett Syndrome Market to be Supported by Upcoming Major Drugs

FEATURED COMPANIES

  • Neuroloxis
  • Newron Pharmaceuticals
  • MORE

Rett syndrome is a rare genetic neurological disorder. This genetic disorder affects females exclusively due to the presence of X chromosome, and is rarely seen in boys. Male children are less prone to this disorder because boys with mutations in MECP2 hardly survive till birth. Changes in MECP2 typically occur during spermatogenesis, and such changes are usually on the paternal copy of the X-chromosome.

The symptoms of Rett syndrome generally occur after 12 months of birth and include signs like slow growth, loss of normal movement and coordination, abnormal hands and eyes movements, and breathing problems. Other drastic symptoms also develop with age. This disorder generally occurs in stages and fourth stage is said to be its last stage. Rett syndrome has no cure and is often treated with off-label drugs which prove to give no relief to the affected patient. Few pharmaceuticals companies are realizing the need for target specific drugs and many therapeutics are being developed, which are in their clinical phases.

The global Rett syndrome market will grow over the years driven by increase in female population, rising spending on public healthcare programs, and increasing global healthcare expenditure. The major trends and developments of the market include efforts to use gene therapy to rectify this neurological disorder, development of new drugs and use of more efficient technologies. However, growth of the market is challenged by factors like high cost of treatment and high R&D expenditure.

The report "Global Rett Syndrome Market: Industry Analysis & Outlook (2017-2025)" analyzes the development of this market, with focus on Sarizotan drug and its market opportunities. The major players are: Newron Pharmaceuticals, Neurem Pharmaceuticals Limited, Anavex Life Sciences Corp., Neuroloxis, and Edison Pharmaceuticals.

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FEATURED COMPANIES

  • Neuroloxis
  • Newron Pharmaceuticals
  • MORE

1. Market Overview
1.1 Rett Syndrome
1.2 Signs and Symptoms
1.3 Stages of Rett Syndrome
1.4 Causes of Rett Syndrome
1.5 Diagnosis and Treatment

2. Global Market Analysis
2.1 Global Rett Syndrome Prevalence
2.1.1 Global Rett Syndrome Prevalence by Region
2.1.2 Global Rett Syndrome Prevalence Share by Region
2.2 Global Rett Syndrome Incidence
2.3 Global Sarizotan Drug Market
2.3.1 Global Sarizotan Drug Market Forecast by Value
2.3.2 Global Sarizotan Drug Market Forecast by Region

3. Regional Analysis
3.1 Europe’s Rett Syndrome Patient Volume Forecast
3.2 Europe’s Rett Syndrome Population with Breathing Disorder
3.3 Europe’s Rett Syndrome Patient Diagnosis Rate
3.4 Europe Sarizotan Drug Market
3.4.1 Europe’s Sarizotan Drug Market Forecast by Value
3.4.2 Europe’s Sarizotan Drug Treatment by Patient Volume
3.5 The US Rett Syndrome Patient Volume Forecast
3.6 The US Rett Syndrome Population with Breathing Disorder
3.7 The US Rett Syndrome Patient Diagnosis Rate
3.8 The US Sarizotan Drug Market
3.8.1 The US Sarizotan Drug Market Forecast by Value
3.8.2 The US Sarizotan Drug Treatment by Patient Volume

4. Market Dynamics
4.1 Growth Drivers
4.1.1 Increasing Female Population Worldwide
4.1.2 Rising Spending on Public Health Programs for Females
4.1.3 Increased Spending on Medicines
4.1.4 Increasing Global Healthcare Expenditure
4.2 Trends and Developments
4.2.1 Gene Therapy for Rett Syndrome
4.2.2 Development of New Drugs
4.2.3 Development of More Efficient and Advanced Technology
4.3 Issues and Challenges
4.3.1 High Cost of Treatment
4.3.2 High R&D Costs
4.3.3 Drug Progress Challenges in Developing Countries

5. Competitive Landscape
5.1 Global Rett Syndrome Market
5.1.1 Major Companies Comparison by Drug Segments
5.1.2 Comparison by Market Cap

6. Company Profiles
6.1 Newron Pharmaceuticals
6.1.1 Business Overview
6.1.2 Financial Overview
6.1.3 Business Strategies
6.2 Neuren Pharmaceuticals Limited
6.2.1 Business Overview
6.2.2 Financial Overview
6.2.3 Business Strategies
6.3 Anavex Life Sciences Corp.
6.3.1 Business Overview
6.3.2 Financial Overview
6.3.3 Business Strategies
6.4 Neuroloxis
6.4.1 Business Overview
6.5 Edison Pharmaceuticals
6.5.1 Business Overview

List of Charts

  • Global Rett Syndrome Prevalence Share by Region (2016)
  • Global Sarizotan Drug Market Forecast by Value (2018-2025)
  • Global Sarizotan Drug Market Forecast by Region (2025)
  • Europe’s Rett Syndrome Patient Volume Forecast (2016-2025)
  • Europe’s Rett Syndrome Population with Breathing Disorder (2016-2025)
  • Europe’s Rett Syndrome Patient Diagnosis Rate (2016-2025)
  • Europe’s Sarizotan Drug Market Forecast by Value (2018-2025)
  • Europe’s Sarizotan Drug Treatment by Patient Volume (2018-2025)
  • The US Rett Syndrome Patient Volume Forecast (2016-2025)
  • The US Rett Syndrome Population with Breathing Disorder (2016-2025)
  • The US Rett Syndrome Patient Diagnosis Rate (2016-2025)
  • The US Sarizotan Drug Market Forecast by Value (2018-2025)
  • The US Sarizotan Drug Treatment by Patient Volume (2018-2025)
  • Global Female Population (2012-2016)
  • Global Spending on Medicines (2010-2020E)
  • Total Spending on Medicines in the US (2012-2016)
  • Global Healthcare Expenditure (2012-2016)
  • Comparison by Market Cap (2016)
  • Newron Pharmaceuticals Revenue and Net Loss (2012-2016)
  • Neuren Pharmaceuticals Operating Revenue and Net Loss (2013-2016)
  • Anavex Life Sciences Corp. Operating Expenses and Net Loss (2014-2016)

List of Tables

  • Global Rett Syndrome Prevalence by Region (2016)
  • Global Rett Syndrome Incidence (2016)
  • Major Drugs for Rett Syndrome in their Development Phases (2016)
  • Major Companies Comparison by Drug Segments (2016)
  • Clinical Pipeline of Newron Pharmaceuticals (2016)
  • Neuren Pharmaceuticals Limited’s Product Pipeline (2016)
  • Anavex Life Sciences Corp.’s Clinical Pipeline with Drug Candidates (2016)
  • Neuroloxis’s Drug Developments (2016)
  • Edison Pharmaceutical’s Drug Pipeline (2016)
  • Edison Pharmaceutical’s Clinical Developments
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FEATURED COMPANIES

  • Neuroloxis
  • Newron Pharmaceuticals
  • MORE

Rett syndrome is caused by mutation in the gene MECP2 located in the X chromosomes, which can arise sporadically or from germline mutation. Since the major cause of this syndrome is located in the X chromosomes, therefore girls are exclusively at its risk rather than boys. It is commonly divided into four stages i.e. early onset, rapid destruction, plateau and last stage being late motor deterioration.

The major symptoms of Rett syndrome start at an early age of 12 months after birth. The most significant symptom of this syndrome is slowed growth and loss of normal movement, coordination, communication. Also, children with every stage start to experience other symptoms like agitation, irritability, seizures, breathing disorders and many others severe signs.

The global Rett syndrome market has no direct indication approved drug and till date is treated by off label drugs. There is no cure to this disease. But many therapeutics are in their clinical phases and are being developed to treat severe symptoms of it like breathing disorder or seizure. With launch of potential drug candidates, the market will experience robust growth with higher penetration rate to treat this disease. The US will promulgate the introduction of these drugs and will be the largest market for Rett syndrome.

The major trends of the market include development of new drugs, use of gene therapy and expansion of new technologies. However, the market will be hindered by high R&D costs and high cost of treatment.

The research report, "Global Rett Syndrome Market: Industry Analysis & Outlook: 2017 Edition" provides an extensive research and detailed analysis of the market performance at present and future outlook of the global and regional market.

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  • Anavex Life Sciences Corp.
  • Neuren Pharmaceuticals Limited
  • Neuroloxis
  • Newron Pharmaceuticals
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