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Gene Therapies for Rare and Genetic Diseases

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    Report

  • 15 Pages
  • May 2018
  • Region: Global
  • Frost & Sullivan
  • ID: 4580150

This edition of the Genetic Technology TOE provides insights across recent developments in gene therapies for rare and genetic disorders. The TOE also provides a clinical trial analysis for ex vivo gene therapy. The Genetic Technology TechVision Opportunity Engine (TOE) presents the latest R&D developments and advances with an emphasis on opportunities to profit in the explosive field of genetic technology through technology transfer, joint ventures, and acquisitions. The complete gamut of genetic technology applications is covered including the latest developments in omics technologies; genetic, cellular, and alternative therapies; sequencing technologies; and genetically altered animals and plants. The Health & Wellness cluster tracks developments in a myriad of areas including genetic engineering, regenerative medicine, drug discovery and development, nanomedicine, nutrition, cosmetic procedures, pain and disease management and therapies, drug delivery, personalized medicine, and smart healthcare.

Table of Contents

1. Gene Therapies for Rare and Genetic Diseases

Recent Advances in Gene Therapies that Address Rare and Genetic Diseases

  • Gene Therapy for Rare Neurological Genetic Diseases
  • Autologous Ex Vivo Gene Therapy for Neurodegenerative Disorders
  • Orphan Drug Accelerators to Improve Rare Diseases Business Model
  • Lentiviral Gene Therapy Solutions for Rare and Genetic Diseases

Clinical Trial Analysis and Key Contacts

  • Clinical Trial Analysis for Ex Vivo Gene Therapy
  • Key Contacts