+353-1-416-8900REST OF WORLD
+44-20-3973-8888REST OF WORLD
1-917-300-0470EAST COAST U.S
1-800-526-8630U.S. (TOLL FREE)

PRINTER FRIENDLY

Primary Hyperoxaluria - Pipeline Review, H1 2019

  • ID: 4772682
  • Drug Pipelines
  • 60 pages
  • Global Markets Direct
1h Free Analyst Time

Speak directly to the analyst to clarify any post sales queries you may have.

1 of 4

FEATURED COMPANIES

  • BridgeBio Pharma LLC
  • Intellia Therapeutics Inc
  • OxThera AB
  • Precision Biosciences Inc
  • MORE
Primary Hyperoxaluria - Pipeline Review, H1 2019

Summary

This latest Pharmaceutical and Healthcare disease pipeline guide Primary Hyperoxaluria - Pipeline Review, H1 2019, provides an overview of the Primary Hyperoxaluria (Genito Urinary System And Sex Hormones) pipeline landscape.

Primary hyperoxaluria is a rare condition characterized by recurrent kidney and bladder stones. It results from the overproduction of a substance called oxalate. Symptoms include blood in the urine, pain when urinating, fever, sudden abdominal pain and frequent urge to urinate. Treatment includes Oral preparations of phosphates and diuretics.

Report Highlights

This Pharmaceutical and Healthcare latest pipeline guide Primary Hyperoxaluria - Pipeline Review, H1 2019, provides comprehensive information on the therapeutics under development for Primary Hyperoxaluria (Genito Urinary System And Sex Hormones), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.

The Primary Hyperoxaluria (Genito Urinary System And Sex Hormones) pipeline guide also reviews of key players involved in therapeutic development for Primary Hyperoxaluria and features dormant and discontinued projects. The guide covers therapeutics under Development by Companies /Universities /Institutes, the molecules developed by Companies in Phase III, Phase II, Preclinical and Discovery stages are 2, 2, 2 and 1 respectively.

Primary Hyperoxaluria (Genito Urinary System And Sex Hormones) pipeline guide helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage. The guide is built using data and information sourced from the publisher's proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.

Note: Certain content / sections in the pipeline guide may be removed or altered based on the availability and relevance of data.

Scope
  • The pipeline guide provides a snapshot of the global therapeutic landscape of Primary Hyperoxaluria (Genito Urinary System And Sex Hormones).
  • The pipeline guide reviews pipeline therapeutics for Primary Hyperoxaluria (Genito Urinary System And Sex Hormones) by companies and universities/research institutes based on information derived from company and industry-specific sources.
  • The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages.
  • The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities.
  • The pipeline guide reviews key companies involved in Primary Hyperoxaluria (Genito Urinary System And Sex Hormones) therapeutics and enlists all their major and minor projects.
  • The pipeline guide evaluates Primary Hyperoxaluria (Genito Urinary System And Sex Hormones) therapeutics based on mechanism of action (MoA), drug target, route of administration (RoA) and molecule type.
  • The pipeline guide encapsulates all the dormant and discontinued pipeline projects.
  • The pipeline guide reviews latest news related to pipeline therapeutics for Primary Hyperoxaluria (Genito Urinary System And Sex Hormones)
Reasons to buy
  • Procure strategically important competitor information, analysis, and insights to formulate effective R&D strategies.
  • Recognize emerging players with potentially strong product portfolio and create effective counter-strategies to gain competitive advantage.
  • Find and recognize significant and varied types of therapeutics under development for Primary Hyperoxaluria (Genito Urinary System And Sex Hormones).
  • Classify potential new clients or partners in the target demographic.
  • Develop tactical initiatives by understanding the focus areas of leading companies.
  • Plan mergers and acquisitions meritoriously by identifying key players and it’s most promising pipeline therapeutics.
  • Formulate corrective measures for pipeline projects by understanding Primary Hyperoxaluria (Genito Urinary System And Sex Hormones) pipeline depth and focus of Indication therapeutics.
  • Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope.
  • Adjust the therapeutic portfolio by recognizing discontinued projects and understand from the know-how what drove them from pipeline.
Note: Product cover images may vary from those shown
2 of 4

FEATURED COMPANIES

  • BridgeBio Pharma LLC
  • Intellia Therapeutics Inc
  • OxThera AB
  • Precision Biosciences Inc
  • MORE
Introduction

Report Coverage

Primary Hyperoxaluria - Overview

Primary Hyperoxaluria - Therapeutics Development

Pipeline Overview

Pipeline by Companies

Products under Development by Companies

Primary Hyperoxaluria - Therapeutics Assessment

Assessment by Target

Assessment by Mechanism of Action

Assessment by Route of Administration

Assessment by Molecule Type

Primary Hyperoxaluria - Companies Involved in Therapeutics Development

Allena Pharmaceuticals Inc

Alnylam Pharmaceuticals Inc

BridgeBio Pharma LLC

Dicerna Pharmaceuticals Inc

Intellia Therapeutics Inc

OxThera AB

Precision Biosciences Inc

Primary Hyperoxaluria - Drug Profiles

BBP-711 - Drug Profile

Product Description

Mechanism Of Action

R&D Progress

DCR-PHXC - Drug Profile

Product Description

Mechanism Of Action

R&D Progress

Gene Therapy to Inhibit HAO1 for Primary Hyperaxuluria - Drug Profile

Product Description

Mechanism Of Action

R&D Progress

Gene Therapy to Inhibit HAO1 for Primary Hyperoxaluria Type I - Drug Profile

Product Description

Mechanism Of Action

R&D Progress

lumasiran - Drug Profile

Product Description

Mechanism Of Action

R&D Progress

Oxabact - Drug Profile

Product Description

Mechanism Of Action

R&D Progress

reloxaliase - Drug Profile

Product Description

Mechanism Of Action

R&D Progress

Primary Hyperoxaluria - Dormant Projects

Primary Hyperoxaluria - Discontinued Products

Primary Hyperoxaluria - Product Development Milestones

Featured News & Press Releases

May 02, 2019: Dicerna submits updated IND application for DCR-PHXC for treatment of primary hyperoxaluria (PH) for the PHYOX 2 pivotal trial

May 02, 2019: Dicerna submits updated IND application for DCR-PHXC for treatment of primary hyperoxaluria (PH) for the PHYOX 2 pivotal trial

Apr 16, 2019: Alnylam begins late-stage paediatric trial of lumasiran

Apr 15, 2019: Intellia Therapeutics announces Oral Presentation on Gene Therapy to inhibit HAO1 for Primary Hyperoxaluria Type I at the 22nd Annual Meeting of the American Society of Gene and Cell Therapy

Mar 29, 2019: Dicerna announces the presentation of updated data demonstrating utility of its lead compound DCR-PHXC in treating primary hyperoxaluria type 1 (PH1) and type 2 (PH2)

Mar 29, 2019: Dicerna announces the presentation of updated data demonstrating utility of its lead compound DCR-PHXC in treating primary hyperoxaluria type 1 (PH1) and type 2 (PH2)

Nov 15, 2018: OxThera is being granted US patent for oxalobacter secretagogues

Oct 31, 2018: OxThera presents encouraging 52-week efficacy and safety data for Oxabact in primary hyperoxaluria type 1 (PH1) patients with ESRD

Oct 25, 2018: Dicerna Announces Late-Breaking Data Supporting Use of DCR-PHXC in Adults with Primary Hyperoxaluria Types 1 and 2 (PH1 and PH2)

Oct 25, 2018: Dicerna Announces Late-Breaking Data Supporting Use of DCR-PHXC in Adults with Primary Hyperoxaluria Types 1 and 2 (PH1 and PH2)

Oct 25, 2018: Alnylam expands Alnylam Act program to improve diagnosis of Primary Hyperoxaluria Type 1 and aligns with FDA on trial design for ILLUMINATE-B Phase 3 pediatric study of Lumasiran

Oct 08, 2018: Alnylam reports new positive Phase l/ll results from lumasiran trial

Oct 05, 2018: Dicerna Announces Late-Breaking Data from the PHYOX Phase 1 Clinical Trial of DCR-PHXC Will Be Presented at ASN Kidney Week 2018

Oct 05, 2018: Dicerna Announces Late-Breaking Data from the PHYOX Phase 1 Clinical Trial of DCR-PHXC Will Be Presented at ASN Kidney Week 2018

Sep 05, 2018: Dicerna announces proof of concept for DCR-PHXC in the treatment of primary hyperoxaluria

Appendix

Methodology

Coverage

Secondary Research

Primary Research

Expert Panel Validation

Contact Us

Disclaimer

List of Tables

Number of Products under Development for Primary Hyperoxaluria, H1 2019

Number of Products under Development by Companies, H1 2019

Products under Development by Companies, H1 2019

Number of Products by Stage and Target, H1 2019

Number of Products by Stage and Mechanism of Action, H1 2019

Number of Products by Stage and Route of Administration, H1 2019

Number of Products by Stage and Molecule Type, H1 2019

Primary Hyperoxaluria - Pipeline by Allena Pharmaceuticals Inc, H1 2019

Primary Hyperoxaluria - Pipeline by Alnylam Pharmaceuticals Inc, H1 2019

Primary Hyperoxaluria - Pipeline by BridgeBio Pharma LLC, H1 2019

Primary Hyperoxaluria - Pipeline by Dicerna Pharmaceuticals Inc, H1 2019

Primary Hyperoxaluria - Pipeline by Intellia Therapeutics Inc, H1 2019

Primary Hyperoxaluria - Pipeline by OxThera AB, H1 2019

Primary Hyperoxaluria - Pipeline by Precision Biosciences Inc, H1 2019

Primary Hyperoxaluria - Dormant Projects, H1 2019

Primary Hyperoxaluria - Discontinued Products, H1 2019

List of Figures

Number of Products under Development for Primary Hyperoxaluria, H1 2019

Number of Products under Development by Companies, H1 2019

Number of Products by Stage and Targets, H1 2019

Number of Products by Stage and Mechanism of Actions, H1 2019

Number of Products by Routes of Administration, H1 2019

Number of Products by Stage and Routes of Administration, H1 2019

Number of Products by Molecule Types, H1 2019

Number of Products by Stage and Molecule Types, H1
Note: Product cover images may vary from those shown
3 of 4

Loading
LOADING...

4 of 4
  • Allena Pharmaceuticals Inc
  • Alnylam Pharmaceuticals Inc
  • BridgeBio Pharma LLC
  • Dicerna Pharmaceuticals Inc
  • Intellia Therapeutics Inc
  • OxThera AB
  • Precision Biosciences Inc
Note: Product cover images may vary from those shown
Adroll
adroll