Alagille Syndrome Pipeline Analysis report covers therapies which include companies and research organizations or institutes, in total 4 in number currently in different phases of development. Alagille syndrome (ALGS) is a genetic disorder which occurs due to the mutations caused in either of the JAG1 or NOTCH2 gene. The genes instruct in making proteins which are involved in building body structures in a developing embryo. Changes in the genes cause the disruption of the signaling pathway leading to the Notch signaling pathway disruption. The Alagille syndrome is autosomal dominant disorder and affects the liver, heart, kidneys and other parts of the body. Affected individuals have distinct facial features and may have unusual butterfly shaped vertebrae when seen through an x-ray. Many patients also have malformed liver ducts.
The report provides Alagille Syndrome treatment drugs by company, phases of development including products in early discovery stage and NDA filing, molecule type, route of administration and region. The report will help to evaluate the collaboration, in-licensing, and out-licensing opportunities, formulating business development strategies and tracking the activities of the key market players. Epidemiology, major drivers, restraints, and opportunities have been covered to provide an exhaustive picture of the market. The analysis presents in-depth information regarding the development, trends, and industry policies and regulations implemented to offer stakeholders a better understanding of the key factors affecting the overall market environment.
Various databases (for patents and Clinical Trials), studies and data published by industry associations, analyst reports, investor presentations, press releases and journals among others have been taken into consideration while conducting the secondary research.
Market intelligence is presented in the form of analysis, charts, and graphics to help the clients in gaining a faster and efficient understanding of the market.
Major companies and research organizations or institutes profiled as part of the report are Albireo Pharma, Inc., Mirum Pharmaceuticals, and Moderna.
Scope:
The report provides Alagille Syndrome treatment drugs by company, phases of development including products in early discovery stage and NDA filing, molecule type, route of administration and region. The report will help to evaluate the collaboration, in-licensing, and out-licensing opportunities, formulating business development strategies and tracking the activities of the key market players. Epidemiology, major drivers, restraints, and opportunities have been covered to provide an exhaustive picture of the market. The analysis presents in-depth information regarding the development, trends, and industry policies and regulations implemented to offer stakeholders a better understanding of the key factors affecting the overall market environment.
Various databases (for patents and Clinical Trials), studies and data published by industry associations, analyst reports, investor presentations, press releases and journals among others have been taken into consideration while conducting the secondary research.
Market intelligence is presented in the form of analysis, charts, and graphics to help the clients in gaining a faster and efficient understanding of the market.
Major companies and research organizations or institutes profiled as part of the report are Albireo Pharma, Inc., Mirum Pharmaceuticals, and Moderna.
Scope:
- By Company
- By Phase
- By Molecule Type
- By Region
- By Route of Administration
Table of Contents
1. Introduction
2. Disease Overview
4. Market Dynamics
5. Pipeline Analysis/Outlook
6. Company profiling
Companies Mentioned
- Albireo Pharma, Inc
- Mirum Pharmaceuticals
- Moderna
- *List is not exhaustive
Methodology
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