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Global Canavan Disease Drug Pipeline Trends 2019: Discovery, Pre-clinical, Clinical, In Approval Therapeutics, Companies and Markets

  • ID: 4830028
  • Drug Pipelines
  • August 2019
  • Region: Global
  • 35 pages
  • VPA Research
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High levels of pipeline activity are being observed in Canavan Disease treatment during 2019. Clinical development activities are being undertaken by more than 5 companies including Orphan Star Therapeutics LLC, Pfizer Inc and others.

A Significant contribution to the Canavan Disease pipeline is being observed from emerging companies opting for new approaches to clinical development strategy. The early stage and late-stage Canavan Disease pipeline included 2 compounds, driven by increasing number of targeted therapies. Progress is being made in accelerating compounds into advanced stages. However, fluctuating trends are being observed in average duration across three phases.

Increased understanding of underlying causes of Canavan Disease condition and increased access to investments is encouraging growth of Canavan Disease drug pipeline. However, despite high levels of pipeline activity, increasing clinical trial costs and decreasing drug approval rates is requiring companies to focus more on understanding clinical development pipeline compounds.

The research study is structured to provide clear and actionable insights into Canavan Disease drug pipeline for companies to optimize spending levels by understanding competition, their pipeline products and prospect of further advances over the next few years.

The report addresses the discovery, research and pre-clinical stage active Canavan Disease therapeutic candidates. Further, drugs in clinical stage including phase 1, phase 2, phase 3 and pre-registration phases are also analyzed.

The current report examines the current Canavan Disease pipeline along with current development status, regulatory progress, mechanism of action, route of administration, collaborating companies, sponsors, molecule type, and research/discovery details.

In addition to drug overview, recent developments, the report also provides mechanism of action, Pre-clinical trial details and Clinical trial details for each of the drug candidates of Canavan Disease. Further, orphan drug status, fast track designation, grants awarded and other special status for Canavan Disease pipeline compounds are also included.

This study was produced independently by the publisher from their proprietary databases, primarily to assist users to develop in-depth understanding of 2019 Canavan Disease pipeline and formulate effective research and development strategies.

Research Methodology

Our integrated data reports are built through robust research methodology to ensure our users can build on the insights and data accuracy for their expansion plans. Both primary and secondary research methods are used with stringent quality checks at each stage to evaluate trends, analysis and forecasts.

Scope of the Research

Canavan Disease Pipeline candidates
  • Pre-clinical Phase: Discovery, research, pre-clinical
  • Early Phase: Phase 1 and Phase 2 Canavan Disease drugs
  • Late phase: Phase 3 and in-approval Canavan Disease drugs
Companies involved in the Pipeline
  • Company overview
  • Snapshot
  • Canavan Disease therapeutic treatment activities
Details for each Canavan Disease drug candidate
  • Snapshot
  • Drug Name
  • Alternative Names
  • Company
  • Originator
  • Phase
  • Molecule Type
  • Orphan Drug Status
  • Drug Overview
  • Mechanism of Action
  • Current Status
  • Trial Details
Other details
  • Pre-clinical trials for each drug candidate
  • Clinical trials for each drug candidate
Recent Canavan Disease therapeutic candidates, clinical trials, investments, grants, partnerships, licenses, awards and other news
Note: Product cover images may vary from those shown
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1.1 List of Tables
1.2 List of Figures

2 Executive Summary
2.1 Canavan Disease- Disease Overview
2.2 Canavan Disease- Pipeline Snapshot
2.3 Canavan Disease- Pipeline Drugs by Phase
2.4 Canavan Disease- Pipeline Drugs by Company
2.5 Canavan Disease- Pipeline Drugs by Mechanism of Action

3 Company wise Pipeline Analysis
3.1 Orphan Star Therapeutics LLC Canavan Disease Drug Pipeline, H2- 2019
3.2 Pfizer Inc Canavan Disease Drug Pipeline, H2- 2019

4 Phase 1 Pipeline Drug Details
4.1 Canavan Disease- Phase 1 Drug Details
4.2 Canavan Disease- Phase 1 Drug Overview
4.3 Canavan Disease- Phase 1 Mechanism of Action
4.4 Current Status
4.5 Trial Details

5 Phase 2 Pipeline Drug Details
5.1 Canavan Disease- Phase 2 Drug Details
5.2 Canavan Disease- Phase 2 Drug Overview
5.3 Canavan Disease- Phase 2 Mechanism of Action
5.4 Current Status
5.5 Trial Details

6 Phase 3 Pipeline Drug Details
6.1 Canavan Disease- Phase 3 Drug Details
6.2 Canavan Disease- Phase 3 Drug Overview
6.3 Canavan Disease- Phase 3 Drug Mechanism of Action
6.4 Current Status
6.5 Trial Details

7 Pre-clinical Phase Pipeline Drug Details
7.1 Canavan Disease- Pre-clinical Phase Drug Details
7.2 Canavan Disease- Pre-clinical Phase Drug Overview
7.3 Canavan Disease- Pre-clinical Phase Drug Mechanism of Action
7.4 Current Status
7.5 Trial Details

8 Recent News and Developments

9 Appendix
9.1 About the Publisher
9.2 Sources and Research Methodology
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  • Orphan Star Therapeutics LLC
  • Pfizer Inc
Note: Product cover images may vary from those shown