The report covers forecast and analysis for the global phenylketonuria treatment market. The study provides historic data from 2016 to 2018 along with forecast from 2019 to 2025 based on revenue (USD Million). In-depth secondary research is used to ascertain overall market size, top industry players, top product, industry associations, etc. Macro-economic indicators such as healthcare industry outlook, healthcare spending, research funding, GDP along with company websites, company annual reports, white papers, financial reports and other sources have also been considered to arrive at the indicated market numbers.
Phenylketonuria or PKU is a genetic disorder in which the levels of phenylalanine increase in the blood. Phenylalanine is a building block of protein obtained through food. PKU can cause behavioral problems, seizures, psychiatric disorders, and delayed development if not treated on time. Children with classic PKU are at risk of brain damage and require treatment. PKU vary from mild to severe form, however classic PKU is considered as severe and variant PKU as less severe disease form. Rising prevalence of PKU globally is likely to accelerate the market growth for PKU treatment. As per the stats provided by Genetic Home Reference, in the U.S. 1 in 10,000 to 15,000 cases of PKU occur in newborns.
The study provides a decisive view on the phenylketonuria treatment market by segmenting the market based on type, route of administration, end user, and regions. All the segments have been analyzed based on present and future trends and the market is estimated from 2019 to 2025. Based on type the market is segmented into drugs and dietary supplements. The drugs market for phenylketonuria is further segmented into kuvan, and biopten. Kuvan segment accounted for major share of the market in 2018. BioMarin Pharmaceutical, Inc. manufactured oral drug Kuvan. This drug was approved in 2007 in the U.S. and in Europe in 2008. The patent of this drug expired in the year 2015 in the U.S. and is about to expire in the year 2020 in Europe. Nonetheless, BioMarin has entered with a settlement agreement with Par Pharmaceuticals to launch generic version of Kuvan tablets and powder form.
Based on route of administration the market is segmented into oral, and parenteral. Oral route of administration held major share of the market in 2018 since this route is mainly preferred by patients due to ease of administration and convenience. Besides, parenteral infusions are also difficult to administer. Based on end user the market is segmented into hospital pharmacies, drug stores, online pharmacies, pediatric clinics, and others. Hospital pharmacies segment held major share of the market in 2018. Regional segmentation includes the current and forecast demand for Asia Pacific, North America, Latin America, Europe, and Middle East & Africa with its further bifurcation into major countries. North America held major share of the market owing to rising government initiatives and favorable regulations to treat PKU in this region. Besides, continuous R&D and commercialization of novel drugs is likely to propel PKU treatment market growth in this region.
The study also includes drivers and restraints for the phenylketonuria treatment along with the impact they have on the demand over the forecast period. Besides, the report includes the study of opportunities and trends available in the phenylketonuria treatment market on global level. With the presence of large number of pipeline drugs, like the SYNB1618, RTX-134, and CNSA-001 are likely to fuel the market growth for phenylketonuria treatment. CNSA-001 has successfully completed its Phase I study and has initiated Phase II clinical trial whereas SYNB1618 is currently under Phase 2a clinical trial and has received the FDA’s fast-track designation. Besides, rising commercialization and development of new drugs is likely to boost market growth.
The report also provides company market share analysis in order to give a broader view of the key players in the market. Industry insights and information is delivered in the required format. ZMR develops a list of industry players (manufacturers), distributors, retailers and industry experts. Some of the players included in phenylketonuria treatment market are Censa Pharmaceutical, Inc., BioMarin Pharmaceuticals, Inc., Rubius Therapeutics, Inc., Retrophin, Inc., Synlogic, Inc., and Homology Medicines, Inc.
The report segments the phenylketonuria treatment market as follows:
Global Phenylketonuria Treatment Market: Type Segment Analysis
Global Phenylketonuria Treatment Market: Route of Administration Segment Analysis
Global Phenylketonuria Treatment Market: End User Segment Analysis
Global Phenylketonuria Treatment Market: Regional Segment Analysis
Phenylketonuria or PKU is a genetic disorder in which the levels of phenylalanine increase in the blood. Phenylalanine is a building block of protein obtained through food. PKU can cause behavioral problems, seizures, psychiatric disorders, and delayed development if not treated on time. Children with classic PKU are at risk of brain damage and require treatment. PKU vary from mild to severe form, however classic PKU is considered as severe and variant PKU as less severe disease form. Rising prevalence of PKU globally is likely to accelerate the market growth for PKU treatment. As per the stats provided by Genetic Home Reference, in the U.S. 1 in 10,000 to 15,000 cases of PKU occur in newborns.
The study provides a decisive view on the phenylketonuria treatment market by segmenting the market based on type, route of administration, end user, and regions. All the segments have been analyzed based on present and future trends and the market is estimated from 2019 to 2025. Based on type the market is segmented into drugs and dietary supplements. The drugs market for phenylketonuria is further segmented into kuvan, and biopten. Kuvan segment accounted for major share of the market in 2018. BioMarin Pharmaceutical, Inc. manufactured oral drug Kuvan. This drug was approved in 2007 in the U.S. and in Europe in 2008. The patent of this drug expired in the year 2015 in the U.S. and is about to expire in the year 2020 in Europe. Nonetheless, BioMarin has entered with a settlement agreement with Par Pharmaceuticals to launch generic version of Kuvan tablets and powder form.
Based on route of administration the market is segmented into oral, and parenteral. Oral route of administration held major share of the market in 2018 since this route is mainly preferred by patients due to ease of administration and convenience. Besides, parenteral infusions are also difficult to administer. Based on end user the market is segmented into hospital pharmacies, drug stores, online pharmacies, pediatric clinics, and others. Hospital pharmacies segment held major share of the market in 2018. Regional segmentation includes the current and forecast demand for Asia Pacific, North America, Latin America, Europe, and Middle East & Africa with its further bifurcation into major countries. North America held major share of the market owing to rising government initiatives and favorable regulations to treat PKU in this region. Besides, continuous R&D and commercialization of novel drugs is likely to propel PKU treatment market growth in this region.
The study also includes drivers and restraints for the phenylketonuria treatment along with the impact they have on the demand over the forecast period. Besides, the report includes the study of opportunities and trends available in the phenylketonuria treatment market on global level. With the presence of large number of pipeline drugs, like the SYNB1618, RTX-134, and CNSA-001 are likely to fuel the market growth for phenylketonuria treatment. CNSA-001 has successfully completed its Phase I study and has initiated Phase II clinical trial whereas SYNB1618 is currently under Phase 2a clinical trial and has received the FDA’s fast-track designation. Besides, rising commercialization and development of new drugs is likely to boost market growth.
The report also provides company market share analysis in order to give a broader view of the key players in the market. Industry insights and information is delivered in the required format. ZMR develops a list of industry players (manufacturers), distributors, retailers and industry experts. Some of the players included in phenylketonuria treatment market are Censa Pharmaceutical, Inc., BioMarin Pharmaceuticals, Inc., Rubius Therapeutics, Inc., Retrophin, Inc., Synlogic, Inc., and Homology Medicines, Inc.
The report segments the phenylketonuria treatment market as follows:
Global Phenylketonuria Treatment Market: Type Segment Analysis
- Drugs
- Kuvan
- Biopten
- Dietary Supplements
Global Phenylketonuria Treatment Market: Route of Administration Segment Analysis
- Oral
- Parenteral
Global Phenylketonuria Treatment Market: End User Segment Analysis
- Hospital Pharmacies
- Drug Stores
- Online Pharmacies
- Pediatric Clinics
- Others
Global Phenylketonuria Treatment Market: Regional Segment Analysis
- North America
- U.S.
- Europe
- UK
- France
- Germany
- Asia Pacific
- China
- Japan
- India
- Latin America
- Brazil
- Middle East and Africa
Table of Contents
- Chapter 1. Preface
- 1.1. Report Description and Scope
- 1.2. Research Scope
- 1.3. Research Methodology
- 1.3.1. Market Research Process
- 1.3.2. Market Research Methodology
- Chapter 2. Executive Summary
- 2.1. Global Media Electronics Market, 2015–2025 (USD Million)
- 2.2. Global Media Electronics Market: Snapshot
- Chapter 3. Global Phenylketonuria Treatment Market – Industry Analysis
- 3.1. Introduction
- 3.2. Industry ecosystem analysis
- 3.3. Deployment landscape
- 3.4. Phenylketonuria Treatment: Market Dynamics
- 3.5. Phenylketonuria Treatment Market: Market Dynamics
- 3.6. Market Drivers
- 3.6.1. Driver 1
- 3.6.2. Driver 2
- 3.7. Restraints
- 3.7.1. Restraint 1
- 3.7.2. Restraint 2
- 3.8. Opportunity
- 3.8.1. Opportunity 1
- 3.9. Porter’s Five Forces Analysis
- 3.10. Market Attractiveness Analysis
- 3.10.1. Market Attractiveness Analysis by Type
- 3.10.2. Market Attractiveness Analysis by Route
- 3.10.3. Market Attractiveness Analysis by End User
- 3.10.4. Market Attractiveness Analysis by Region
- Chapter 4. Global Phenylketonuria Treatment Market– Competitive Landscape
- 4.1. Company Market Share Analysis
- 4.1.1. Global Phenylketonuria Treatment Market: Company Market Share, 2019
- 4.2. Strategic Development
- 4.2.1. Acquisitions & Mergers
- 4.2.2. New Type Launches
- 4.2.3. Agreements, Partnerships, collaborations and Joint Ventures
- 4.2.4. Research and Development and Regional Expansion
- 4.3. Price Trend Analysis
- 4.1. Company Market Share Analysis
- Chapter 5. Global Phenylketonuria Treatment Market –Type Analysis
- 5.1. Global Phenylketonuria Treatment Market Overview: by Type Type
- 5.1.1. Global Phenylketonuria Treatment Market Share, by Type,2019 and 2025
- 5.2. Drug
- 5.2.1. Global Phenylketonuria Treatment Market by Drug, 2015–2025 (USD Million)
- 5.3. Dietary Supplements
- 5.3.1. Global Phenylketonuria Treatment Market by Dietary Supplements, 2015–2025 (USD Million)
- 5.1. Global Phenylketonuria Treatment Market Overview: by Type Type
- Chapter 6. Global Phenylketonuria Treatment Market –Route Analysis
- 6.1. Global Phenylketonuria Treatment Market Overview: by Route
- 6.1.1. Global Phenylketonuria Treatment Market Share, by Route, 2019 and 2025
- 6.2. Oral
- 6.2.1. Global Phenylketonuria Treatment Market by Oral, 2015–2025 (USD Million)
- 6.3. Parenteral
- 6.3.1. Global Phenylketonuria Treatment Market by Parenteral, 2015–2025 (USD Million)
- 6.3.2.
- 6.1. Global Phenylketonuria Treatment Market Overview: by Route
- Chapter 7. Global Phenylketonuria Treatment Market –End User Analysis
- 7.1. Global Phenylketonuria Treatment Market Overview: by End User
- 7.1.1. Global Phenylketonuria Treatment Market Share, by End User, 2019 and 2025
- 7.2. Hospitals
- 7.2.1. Global Phenylketonuria Treatment Market by Hospitals, 2015–2025 (USD Million)
- 7.3. Drug Stores
- 7.3.1. Global Phenylketonuria Treatment Market by Drug Stores, 2015–2025 (USD Million)
- 7.4. Online Pharmacies
- 7.4.1. Global Phenylketonuria Treatment Market by Online Pharmacies, 2015–2025 (USD Million)
- 7.5. Paediatrics Clincs
- 7.5.1. Global Phenylketonuria Treatment Market by Paediatrics Clincs, 2015–2025 (USD Million)
- 7.6. Others
- 7.6.1. Global Phenylketonuria Treatment Market by Others, 2015–2025 (USD Million)
- 7.1. Global Phenylketonuria Treatment Market Overview: by End User
- Chapter 8. Global Phenylketonuria Treatment Market - Regional Analysis
- 8.1. Global Phenylketonuria Treatment Market Overview: by Region
- 8.1.1. Global Phenylketonuria Treatment Market share, by Region, 2019 and 2025
- 8.2. North America
- 8.2.1. North America Phenylketonuria Treatment Market, 2015–2025 (USD Million)
- 8.2.2. North America Phenylketonuria Treatment Market Revenue, by Type,2015–2025 (USD Million)
- 8.2.3. North America Phenylketonuria Treatment Market Revenue, by Route, 2015–2025 (USD Million)
- 8.2.4. North America Phenylketonuria Treatment Market Revenue, by End User, 2015–2025 (USD Million)
- 8.2.5. The U.S.
- 8.2.5.1. The U.S.Phenylketonuria Treatment Market Revenue, by Type,2015–2025 (USD Million)
- 8.2.5.2. The U.S.Phenylketonuria Treatment Market Revenue, by Route, 2015–2025 (USD Million)
- 8.2.5.3. The U.S.Phenylketonuria Treatment Market Revenue, by End User, 2015–2025 (USD Million)
- 8.2.6. Rest of North America
- 8.2.6.1. Rest of North America Phenylketonuria Treatment Market Revenue, by Type,2015–2025 (USD Million)
- 8.2.6.2. Rest of North America Phenylketonuria Treatment Market Revenue, by Route, 2015–2025 (USD Million)
- 8.2.6.3. Rest of North America Phenylketonuria Treatment Market Revenue, by End User, 2015–2025 (USD Million)
- 8.3. Europe
- 8.3.1. Europe Phenylketonuria Treatment Market, 2015–2025 (USD Million)
- 8.3.2. Europe Phenylketonuria Treatment Market Revenue, by Type,2015–2025 (USD Million)
- 8.3.3. Europe Phenylketonuria Treatment Market Revenue, by Route, 2015–2025 (USD Million)
- 8.3.4. Europe Phenylketonuria Treatment Market Revenue, by End User, 2015–2025 (USD Million)
- 8.3.5. UK
- 8.3.5.1. U.K.Phenylketonuria Treatment Market Revenue, by Type,2015–2025 (USD Million)
- 8.3.5.2. U.K.Phenylketonuria Treatment Market Revenue, by Route, 2015–2025 (USD Million)
- 8.3.5.3. U.K. Phenylketonuria Treatment Market # Revenue, by End User, 2015–2025 (USD Million)
- 8.3.6. France
- 8.3.6.1. France Phenylketonuria Treatment Market Revenue, by Type,2015–2025 (USD Million)
- 8.3.6.2. France Phenylketonuria Treatment Market Revenue, by Route, 2015–2025 (USD Million)
- 8.3.6.3. France Phenylketonuria Treatment Market Revenue, by End User, 2015–2025 (USD Million)
- 8.3.7. Germany
- 8.3.7.1. Germany Phenylketonuria Treatment Market Revenue, by Type,2015–2025 (USD Million)
- 8.3.7.2. Germany Phenylketonuria Treatment Market Revenue, by Route, 2015–2025 (USD Million)
- 8.3.7.3. Germany Phenylketonuria Treatment Market Revenue, by End User, 2015–2025 (USD Million)
- 8.3.8. Rest of Europe
- 8.3.8.1. Rest of Europecast Pulypropylene(CPP) Films Market Revenue, by Type,2015–2025 (USD Million)
- 8.3.8.2. Rest of Europecast Pulypropylene(CPP) Films Market Revenue, by Route, 2015–2025 (USD Million)
- 8.3.8.3. Rest of Europe Phenylketonuria Treatment Market Revenue, by End User, 2015–2025 (USD Million)
- 8.4. Asia Pacific
- 8.4.1. Asia Pacific Phenylketonuria Treatment Market, 2015–2025 (USD Million)
- 8.4.2. Asia Pacific Phenylketonuria Treatment Market # Revenue, by Type,2015–2025 (USD Million)
- 8.4.3. Asia Pacific Phenylketonuria Treatment Market Revenue, by Route, 2015–2025 (USD Million)
- 8.4.4. Asia Pacific Phenylketonuria Treatment Market Revenue, by End User, 2015–2025 (USD Million)
- 8.4.5. China
- 8.4.5.1. China Phenylketonuria Treatment Market Revenue, by Type,2015–2025 (USD Million)
- 8.4.5.2. China Phenylketonuria Treatment Market Revenue, by Route, 2015–2025 (USD Million)
- 8.4.5.3. China Phenylketonuria Treatment Market # Revenue, by End User, 2015–2025 (USD Million)
- 8.4.6. Japan
- 8.4.6.1. Japan Phenylketonuria Treatment Market Revenue, by Type,2015–2025 (USD Million)
- 8.4.6.2. Japan Phenylketonuria Treatment Market Revenue, by Route, 2015–2025 (USD Million)
- 8.4.6.3. Japan Phenylketonuria Treatment Market Revenue, by End User, 2015–2025 (USD Million)
- 8.4.7. India
- 8.4.7.1. India Phenylketonuria Treatment Market Revenue, by Type,2015–2025 (USD Million)
- 8.4.7.2. India Phenylketonuria Treatment Market Revenue, by Route, 2015–2025 (USD Million)
- 8.4.7.3. India Phenylketonuria Treatment Market Revenue, by End User, 2015–2025 (USD Million)
- 8.4.8. Rest of Asia Pacific
- 8.4.8.1. Rest of Asia Pacific Phenylketonuria Treatment Market Revenue, by Type,2015–2025 (USD Million)
- 8.4.8.2. Rest of Asia Pacific Phenylketonuria Treatment Market Revenue, by Route, 2015–2025 (USD Million)
- 8.4.8.3. Rest of Asia Pacific Phenylketonuria Treatment Market Revenue, by End User, 2015–2025 (USD Million)
- 8.5. Latin America
- 8.5.1. Latin America Phenylketonuria Treatment Market, 2015–2025 (USD Million)
- 8.5.2. Latin America Phenylketonuria Treatment Market Revenue, by Type,2015–2025 (USD Million)
- 8.5.3. Latin America Phenylketonuria Treatment Market Revenue, by Route, 2015–2025 (USD Million)
- 8.5.4. Latin America Phenylketonuria Treatment Market Revenue, by End User, 2015–2025 (USD Million)
- 8.5.5. Brazil
- 8.5.5.1. Brazil Phenylketonuria Treatment Market Revenue, by Type,2015–2025 (USD Million)
- 8.5.5.2. Brazil Phenylketonuria Treatment Market Revenue, by Route, 2015–2025 (USD Million)
- 8.5.5.3. Brazil Phenylketonuria Treatment Market Revenue, by End User, 2015–2025 (USD Million)
- 8.5.6. Rest of Latin America
- 8.5.6.1. Rest of Latin America Phenylketonuria Treatment Market Revenue, by Type,2015–2025 (USD Million)
- 8.5.6.2. Rest of Latin America Phenylketonuria Treatment Market Revenue, by Route, 2015–2025 (USD Million)
- 8.5.6.3. Rest of Latin America Phenylketonuria Treatment Market # Revenue, by End User, 2015–2025 (USD Million)
- 8.6. The Middle East and Africa
- 8.6.1. The Middle East and Africa Phenylketonuria Treatment Market, 2015–2025 (USD Million)
- 8.6.2. The Middle East and Africa Phenylketonuria Treatment Market Revenue, by Type,2015–2025 (USD Million)
- 8.6.3. The Middle East and Africa Phenylketonuria Treatment Market Revenue, by Route, 2015–2025 (USD Million)
- 8.6.4. The Middle East and Africa Phenylketonuria Treatment Market Revenue, by End User, 2015–2025 (USD Million)
- 8.1. Global Phenylketonuria Treatment Market Overview: by Region
- Chapter 9. Company Profiles
- 9.1. Homulogy Medicines, Inc.
- 9.1.1. Overview
- 9.1.2. Financials
- 9.1.3. Product portfolio
- 9.1.4. Business Strategy
- 9.1.5. Recent Developments
- 9.2. Rubius Therapeutics. Inc
- 9.2.1. Overview
- 9.2.2. Financials
- 9.2.3. Product portfolio
- 9.2.4. Business Strategy
- 9.2.5. Recent Developments
- 9.3. Retrophin, Inc
- 9.3.1. Overview
- 9.3.2. Financials
- 9.3.3. Product portfolio
- 9.3.4. Business Strategy
- 9.3.5. Recent Developments
- 9.4. Synlogic, Inc
- 9.4.1. Overview
- 9.4.2. Financials
- 9.4.3. Product portfolio
- 9.4.4. Business Strategy
- 9.4.5. Recent Development
- 9.5. Homulogy Medicines, Inc
- 9.5.1. Overview
- 9.5.2. Financials
- 9.5.3. Product portfolio
- 9.5.4. Business Strategy
- 9.5.5. Recent Development
- 9.1. Homulogy Medicines, Inc.
