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Spinal Muscular Atrophy (SMA) - Pipeline Review, H2 2020

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    Drug Pipelines

  • 164 Pages
  • August 2020
  • Region: Global
  • Global Markets Direct
  • ID: 5146841
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Summary

The publisher's latest Pharmaceutical and Healthcare disease pipeline guide Spinal Muscular Atrophy - Pipeline Review, H2 2020, provides an overview of the Spinal Muscular Atrophy (Central Nervous System) pipeline landscape.

Spinal muscular atrophy (SMA) is a genetic disease that attacks nerve cells, called motor neurons, in the spinal cord. These critically important cells are responsible for supplying electrical and chemical messages to muscle cells. Without the proper input from the motor neurons, muscle cells cannot function properly. The muscle cells will, therefore, become much smaller (atrophy) and will produce symptoms of muscle weakness. This can affect walking, crawling, breathing, swallowing, and head and neck control.

Report Highlights

The publisher's Pharmaceutical and Healthcare latest pipeline guide Spinal Muscular Atrophy - Pipeline Review, H2 2020, provides comprehensive information on the therapeutics under development for Spinal Muscular Atrophy (Central Nervous System), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.

The Spinal Muscular Atrophy (Central Nervous System) pipeline guide also reviews the key players involved in therapeutic development for Spinal Muscular Atrophy (SMA) and features dormant and discontinued projects. The guide covers therapeutics under Development by Companies /Universities /Institutes, the molecules developed by Companies in Pre-Registration, Phase III, Phase II, Phase I, Preclinical and Discovery stages are 1, 2, 4, 3, 18 and 5 respectively. Similarly, the Universities portfolio in Phase II, Preclinical and Discovery stages comprises 2, 8 and 2 molecules, respectively.

Spinal Muscular Atrophy (Central Nervous System) pipeline guide helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage. The guide is built using data and information sourced from the publisher’s proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.

Note: Certain content/sections in the pipeline guide may be removed or altered based on the availability and relevance of data.

Scope
  • The pipeline guide provides a snapshot of the global therapeutic landscape of Spinal Muscular Atrophy (Central Nervous System).
  • The pipeline guide reviews pipeline therapeutics for Spinal Muscular Atrophy (Central Nervous System) by companies and universities/research institutes based on information derived from company and industry-specific sources.
  • The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages.
  • The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities.
  • The pipeline guide reviews key companies involved in Spinal Muscular Atrophy (Central Nervous System) therapeutics and enlists all their major and minor projects.
  • The pipeline guide evaluates Spinal Muscular Atrophy (Central Nervous System) therapeutics based on mechanism of action (MoA), drug target, route of administration (RoA) and molecule type.
  • The pipeline guide encapsulates all the dormant and discontinued pipeline projects.
  • The pipeline guide reviews latest news related to pipeline therapeutics for Spinal Muscular Atrophy (Central Nervous System)

Reasons to Buy
  • Procure strategically important competitor information, analysis, and insights to formulate effective R&D strategies.
  • Recognize the emerging players with potentially strong product portfolios and create effective counter-strategies to gain competitive advantage.
  • Find and recognize significant and varied types of therapeutics under development for Spinal Muscular Atrophy (Central Nervous System).
  • Classify potential new clients or partners in the target demographic.
  • Develop tactical initiatives by understanding the focus areas of leading companies.
  • Plan mergers and acquisitions meritoriously by identifying key players and it’s most promising pipeline therapeutics.
  • Formulate corrective measures for pipeline projects by understanding Spinal Muscular Atrophy (Central Nervous System) pipeline depth and focus of Indication therapeutics.
  • Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope.
  • Adjust the therapeutic portfolio by recognizing discontinued projects and understand from the know-how what drove them from the pipeline.

Table of Contents

Introduction
  • Spinal Muscular Atrophy (SMA) - Overview
  • Spinal Muscular Atrophy (SMA) - Therapeutics Development

Spinal Muscular Atrophy (SMA) - Therapeutics AssessmentSpinal Muscular Atrophy (SMA) - Companies Involved in Therapeutics DevelopmentSpinal Muscular Atrophy (SMA) - Drug Profiles
Spinal Muscular Atrophy (SMA) - Dormant Projects
  • Spinal Muscular Atrophy (SMA) - Discontinued Products
  • Spinal Muscular Atrophy (SMA) - Product Development Milestones

Appendix
List of Tables
  • Number of Products under Development for Spinal Muscular Atrophy (SMA), H2 2020
  • Number of Products under Development by Companies, H2 2020
  • Number of Products under Development by Companies, H2 2020 (Contd..1), H2 2020
  • Number of Products under Development by Universities/Institutes, H2 2020
  • Products under Development by Companies, H2 2020
  • Products under Development by Companies, H2 2020 (Contd..1), H2 2020
  • Products under Development by Companies, H2 2020 (Contd..2), H2 2020
  • Products under Development by Universities/Institutes, H2 2020
  • Number of Products by Stage and Target, H2 2020
  • Number of Products by Stage and Mechanism of Action, H2 2020
  • Number of Products by Stage and Route of Administration, H2 2020
  • Number of Products by Stage and Molecule Type, H2 2020
  • Spinal Muscular Atrophy (SMA) - Pipeline by Allianz Pharmascience Ltd, H2 2020
  • Spinal Muscular Atrophy (SMA) - Pipeline by AlphaCognition Inc, H2 2020
  • Spinal Muscular Atrophy (SMA) - Pipeline by Anima Biotech Inc, H2 2020
  • Spinal Muscular Atrophy (SMA) - Pipeline by Armgo Pharma Inc, H2 2020
  • Spinal Muscular Atrophy (SMA) - Dormant Projects, H2 2020
  • Spinal Muscular Atrophy (SMA) - Dormant Projects, H2 2020 (Contd..1), H2 2020
  • Spinal Muscular Atrophy (SMA) - Dormant Projects, H2 2020 (Contd..2), H2 2020
  • Spinal Muscular Atrophy (SMA) - Discontinued Products, H2 2020

List of Figures
  • Number of Products under Development for Spinal Muscular Atrophy (SMA), H2 2020
  • Number of Products under Development by Companies, H2 2020
  • Number of Products under Development by Universities/Institutes, H2 2020
  • Number of Products by Top 10 Targets, H2 2020
  • Number of Products by Stage and Top 10 Targets, H2 2020
  • Number of Products by Top 10 Mechanism of Actions, H2 2020
  • Number of Products by Stage and Top 10 Mechanism of Actions, H2 2020
  • Number of Products by Routes of Administration, H2 2020
  • Number of Products by Stage and Top 10 Routes of Administration, H2 2020
  • Number of Products by Molecule Types, H2 2020
  • Number of Products by Stage and Molecule Types, H2 2020

Companies Mentioned

A selection of companies mentioned in this report includes:

  • Allianz Pharmascience Ltd
  • AlphaCognition Inc
  • Anima Biotech Inc
  • Armgo Pharma Inc
  • AveXis Inc
  • Biogen Inc
  • Bioleaders Corp
  • BioMarin Pharmaceutical Inc
  • Biophytis SA
  • Cell Tech Pharmed Co
  • Enzerna Biosciences LLC
  • Exicure Inc
  • F. Hoffmann-La Roche Ltd
  • Genea Biocells
  • GNT Pharma Co Ltd
  • Imago Pharmaceuticals Inc
  • Kowa Co Ltd
  • Neurotune AG
  • Novartis AG
  • Ono Pharmaceutical Co Ltd
  • Ractigen Therapeutics Inc
  • Reborna Biosciences Inc
  • Sarepta Therapeutics Inc
  • Scholar Rock Inc
  • Shift Pharmaceuticals
  • Spotlight Innovation Inc
  • Vybion Inc
  • Xcelthera INC