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Mucopolysaccharidosis II - Pipeline Insight, 2020

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    Clinical Trials

  • 106 Pages
  • February 2020
  • Region: Global
  • DelveInsight
  • ID: 4989382
Mucopolysaccharidosis II Overview

Mucopolysaccharidosis II Pipeline Insight, 2020 report outlays comprehensive insights of present clinical development scenario and growth prospects across the Mucopolysaccharidosis II market. A detailed picture of the Mucopolysaccharidosis II pipeline landscape is provided, which includes the disease overview and Mucopolysaccharidosis II treatment guidelines. The assessment part of the report embraces in-depth Mucopolysaccharidosis II commercial assessment and clinical assessment of the Mucopolysaccharidosis II pipeline products from the pre-clinical developmental phase to the marketed phase. In the report, a detailed description of the drug is proffered including mechanism of action of the drug, clinical studies, NDA approvals (if any), and product development activities comprising the technology, Mucopolysaccharidosis II collaborations, licensing, mergers and acquisition, funding, designations, and other product-related details.

Mucopolysaccharidosis II of pipeline development activities

The report provides insights into:
  • All of the companies that are developing therapies for the treatment of Mucopolysaccharidosis II with aggregate therapies developed by each company for the same.
  • Different therapeutic candidates segmented into early-stage, mid-stage and late stage of development for the Mucopolysaccharidosis II treatment.
  • Mucopolysaccharidosis II key players involved in targeted therapeutics development with respective active and inactive (dormant or discontinued) projects.
  • Drugs under development based on the stage of development, route of administration, target receptor, monotherapy or combination therapy, a different mechanism of action, and molecular type.
  • Detailed analysis of collaborations (company-company collaborations and company-academia collaborations), licensing agreement and financing details for future advancement of Mucopolysaccharidosis II market.

The report is built using data and information traced from the researcher's proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations, and featured press releases from company/university web sites and industry-specific third-party sources, etc.

Mucopolysaccharidosis II Analytical Perspective

In-depth Mucopolysaccharidosis II Commercial Assessment Of Products

This report provides a comprehensive commercial assessment of therapeutic drugs that have been included, which comprises of collaborations, licensing, and acquisition deal value trends. The report also covers company-company collaborations (licensing/partnering), company-academia collaborations, and acquisition analysis in both graphical and tabulated form in a detailed manner.

Mucopolysaccharidosis II Clinical Assessment Of Products

The report comprises of comparative clinical assessment of products by development stage, product type, route of administration, molecule type, and MOA type across this indication.

Scope of the report
  • The Mucopolysaccharidosis II report provides an overview of therapeutic pipeline activity and therapeutic assessment of the products by development stage, product type, route of administration, molecule type, and MOA type for Mucopolysaccharidosis II across the complete product development cycle, including all clinical and nonclinical stages.
  • It comprises of detailed profiles of Mucopolysaccharidosis II therapeutic products with key coverage of developmental activities, including technology, collaborations, licensing, mergers and acquisition, funding, designations and other product-related details
  • Detailed Mucopolysaccharidosis II research and development progress and trial details, results wherever available, are also included in the pipeline study.
  • Coverage of dormant and discontinued pipeline projects along with the reasons if available across Mucopolysaccharidosis II .

Report Highlights
  • A better understanding of disease pathogenesis contributing to the development of novel therapeutics for Mucopolysaccharidosis II .
  • In the coming years, the Mucopolysaccharidosis II market is set to change due to the rising awareness of the disease, and incremental healthcare spending across the world; which would expand the size of the market to enable the drug manufacturers to penetrate more into the market.
  • The companies and academics that are working to assess challenges and seek opportunities that could influence Mucopolysaccharidosis II R&D. The therapies under development are focused on novel approaches to treat/improve the disease condition.
  • A detailed portfolio of major pharma players who are involved in fueling the Mucopolysaccharidosis II treatment market. Several potential therapies for Mucopolysaccharidosis II are under investigation. With the expected launch of these emerging therapies, it is expected that there will be a significant impact on the Mucopolysaccharidosis II market size in the coming years.
  • Our in-depth analysis of the pipeline assets (in early-stage, mid-stage and late stage of development for the treatment of Mucopolysaccharidosis II ) includes therapeutic assessment and comparative analysis. This will support the clients in the decision-making process regarding their therapeutic portfolio by identifying the overall scenario of the research and development activities.

Key Questions
  • What are the current options for Mucopolysaccharidosis II treatment?
  • How many companies are developing therapies for the treatment of Mucopolysaccharidosis II?
  • What are the principal therapies developed by these companies in the industry?
  • How many therapies are developed by each company for the treatment of Mucopolysaccharidosis II?
  • How many Mucopolysaccharidosis II emerging therapies are in early-stage, mid-stage, and late stage of development for the treatment of Mucopolysaccharidosis II?
  • Out of total pipeline products, how many therapies are given as a monotherapy and in combination with other therapies?
  • What are the key collaborations (Industry-Industry, Industry-Academia), Mergers and acquisitions, and major licensing activities that will impact Mucopolysaccharidosis II market?
  • Which are the dormant and discontinued products and the reasons for the same?
  • What is the unmet need for current therapies for the treatment of Mucopolysaccharidosis II?
  • What are the recent novel therapies, targets, mechanisms of action and technologies developed to overcome the limitation of existing Mucopolysaccharidosis II therapies?
  • What are the clinical studies going on for Mucopolysaccharidosis II and their status?
  • What are the results of the clinical studies and their safety and efficacy?
  • What are the key designations that have been granted for the emerging therapies for Mucopolysaccharidosis II?
  • How many patents are granted and pending for the emerging therapies for the treatment of Mucopolysaccharidosis II?

Table of Contents

1. Report Introduction
2. Mucopolysaccharidosis II
2.1. Overview
2.2. History
2.3. Mucopolysaccharidosis II Symptoms
2.4. Causes
2.6. Mucopolysaccharidosis II Diagnosis
2.6.1. Diagnostic Guidelines
3. Mucopolysaccharidosis II Current Treatment Patterns
3.1. Mucopolysaccharidosis II Treatment Guidelines
4. Mucopolysaccharidosis II - Analytical Perspective
4.1. In-depth Commercial Assessment
4.1.1. Mucopolysaccharidosis II companies collaborations, Licensing, Acquisition -Deal Value Trends Assessment Summary
4.1.2. Mucopolysaccharidosis II Collaboration Deals Company-Company Collaborations (Licensing / Partnering) Analysis Company-University Collaborations (Licensing / Partnering) Analysis Mucopolysaccharidosis II Acquisition Analysis
5. Therapeutic Assessment
5.1. Clinical Assessment of Pipeline Drugs
5.1.1. Assessment by Phase of Development
5.1.2. Assessment by Product Type (Mono / Combination) Assessment by Stage and Product Type
5.1.3. Assessment by Route of Administration Assessment by Stage and Route of Administration
5.1.4. Assessment by Molecule Type Assessment by Stage and Molecule Type
5.1.5. Assessment by MOA Assessment by Stage and MOA
5.1.6. Assessment by Target Assessment by Stage and Target
6. Mucopolysaccharidosis II Late Stage Products (Phase-III)7. Mucopolysaccharidosis II Mid Stage Products (Phase-II)8. Early Stage Products (Phase-I)9. Pre-clinical Products and Discovery Stage Products10. Inactive Products11. Dormant Products12. Mucopolysaccharidosis II Discontinued Products
13. Mucopolysaccharidosis II Product Profiles
13.1. Drug Name: Company
13.1.1. Product Description Product Overview Mechanism of action
13.1.2. Research and Development Clinical Studies
13.1.3. Product Development Activities Collaboration Agreements Acquisition Patent Detail
13.1.4. Tabulated Product Summary General Description Table
14. Mucopolysaccharidosis II Key Companies15. Mucopolysaccharidosis II Key Products
16. Dormant and Discontinued Products
16.1. Dormant Products
16.1.1. Reasons for being dormant
16.2. Discontinued Products
16.2.1. Reasons for the discontinuation
17. Mucopolysaccharidosis II Unmet Needs18. Mucopolysaccharidosis II Future Perspectives19. Mucopolysaccharidosis II Analyst Review20. Appendix
21. Report Methodology
21.1. Secondary Research
21.2. Expert Panel Validation

Companies Mentioned

A selection of companies mentioned in this report includes:

  • JCR Pharmaceuticals Co., Ltd.
  • Sangamo Therapeutics
  • Green Cross Corporation
  • Regenxbio Inc.
  • Shire
  • Abeona Therapeutics, Inc