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Thalassemia - Pipeline Review, H2 2020

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    Drug Pipelines

  • 215 Pages
  • August 2020
  • Region: Global
  • Global Markets Direct
  • ID: 5146839
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Summary

The publisher's latest Pharmaceutical and Healthcare disease pipeline guide Thalassemia - Pipeline Review, H2 2020, provides an overview of the Thalassemia (Hematological Disorders) pipeline landscape.

Thalassemia is a group of inherited blood disorders that affect the body's ability to produce hemoglobin and red blood cells. Symptoms include fussiness, paleness, frequent infections, failure to thrive, poor appetite and jaundice. Predisposing factors include family history. Treatment includes blood transfusions and bone marrow transplant.

Report Highlights

The publisher's Pharmaceutical and Healthcare latest pipeline guide Thalassemia - Pipeline Review, H2 2020, provides comprehensive information on the therapeutics under development for Thalassemia (Hematological Disorders), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.

The Thalassemia (Hematological Disorders) pipeline guide also reviews the key players involved in therapeutic development for Thalassemia and features dormant and discontinued projects. The guide covers therapeutics under Development by Companies /Universities /Institutes, the molecules developed by Companies in Phase III, Phase II, Phase I, IND/CTA Filed, Preclinical and Discovery stages are 2, 15, 6, 1, 15 and 4 respectively. Similarly, the Universities portfolio in Phase II, Phase I, Preclinical and Discovery stages comprises 1, 1, 4 and 1 molecules, respectively.

Thalassemia (Hematological Disorders) pipeline guide helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage. The guide is built using data and information sourced from the publisher’s proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.

Note: Certain content/sections in the pipeline guide may be removed or altered based on the availability and relevance of data.

Scope
  • The pipeline guide provides a snapshot of the global therapeutic landscape of Thalassemia (Hematological Disorders).
  • The pipeline guide reviews pipeline therapeutics for Thalassemia (Hematological Disorders) by companies and universities/research institutes based on information derived from company and industry-specific sources.
  • The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages.
  • The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities.
  • The pipeline guide reviews key companies involved in Thalassemia (Hematological Disorders) therapeutics and enlists all their major and minor projects.
  • The pipeline guide evaluates Thalassemia (Hematological Disorders) therapeutics based on mechanism of action (MoA), drug target, route of administration (RoA) and molecule type.
  • The pipeline guide encapsulates all the dormant and discontinued pipeline projects.
  • The pipeline guide reviews latest news related to pipeline therapeutics for Thalassemia (Hematological Disorders)

Reasons to Buy
  • Procure strategically important competitor information, analysis, and insights to formulate effective R&D strategies.
  • Recognize the emerging players with potentially strong product portfolios and create effective counter-strategies to gain competitive advantage.
  • Find and recognize significant and varied types of therapeutics under development for Thalassemia (Hematological Disorders).
  • Classify potential new clients or partners in the target demographic.
  • Develop tactical initiatives by understanding the focus areas of leading companies.
  • Plan mergers and acquisitions meritoriously by identifying key players and it’s most promising pipeline therapeutics.
  • Formulate corrective measures for pipeline projects by understanding Thalassemia (Hematological Disorders) pipeline depth and focus of Indication therapeutics.
  • Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope.
  • Adjust the therapeutic portfolio by recognizing discontinued projects and understand from the know-how what drove them from the pipeline.

Table of Contents

Introduction
  • Thalassemia - Overview
  • Thalassemia - Therapeutics Development

Thalassemia - Therapeutics AssessmentThalassemia - Companies Involved in Therapeutics DevelopmentThalassemia - Drug Profiles
Thalassemia - Dormant Projects
  • Thalassemia - Discontinued Products
  • Thalassemia - Product Development Milestones

Appendix
List of Tables
  • Number of Products under Development for Thalassemia, H2 2020
  • Number of Products under Development by Companies, H2 2020
  • Number of Products under Development by Companies, H2 2020 (Contd..1), H2 2020
  • Number of Products under Development by Universities/Institutes, H2 2020
  • Products under Development by Companies, H2 2020
  • Products under Development by Companies, H2 2020 (Contd..1), H2 2020
  • Products under Development by Companies, H2 2020 (Contd..2), H2 2020
  • Products under Development by Universities/Institutes, H2 2020
  • Number of Products by Stage and Target, H2 2020
  • Number of Products by Stage and Mechanism of Action, H2 2020
  • Number of Products by Stage and Route of Administration, H2 2020
  • Number of Products by Stage and Molecule Type, H2 2020
  • Thalassemia - Pipeline by Acceleron Pharma Inc, H2 2020
  • Thalassemia - Pipeline by Agios Pharmaceuticals Inc, H2 2020
  • Thalassemia - Pipeline by Allife Medical Science and Technology Co Ltd, H2 2020
  • Thalassemia - Pipeline by Aruvant Sciences Inc, H2 2020
  • Thalassemia - Dormant Projects, H2 2020
  • Thalassemia - Dormant Projects, H2 2020 (Contd..1), H2 2020
  • Thalassemia - Discontinued Products, H2 2020

List of Figures
  • Number of Products under Development for Thalassemia, H2 2020
  • Number of Products under Development by Companies, H2 2020
  • Number of Products under Development by Universities/Institutes, H2 2020
  • Number of Products by Top 10 Targets, H2 2020
  • Number of Products by Stage and Top 10 Targets, H2 2020
  • Number of Products by Top 10 Mechanism of Actions, H2 2020
  • Number of Products by Stage and Top 10 Mechanism of Actions, H2 2020
  • Number of Products by Routes of Administration, H2 2020
  • Number of Products by Stage and Routes of Administration, H2 2020
  • Number of Products by Top 10 Molecule Types, H2 2020
  • Number of Products by Stage and Top 10 Molecule Types, H2 2020

Companies Mentioned

A selection of companies mentioned in this report includes:

  • Acceleron Pharma Inc
  • Agios Pharmaceuticals Inc
  • Allife Medical Science and Technology Co Ltd
  • Aruvant Sciences Inc
  • ASC Therapeutics Inc
  • Beam Therapeutics Inc
  • bluebird bio Inc
  • Cell Source Inc
  • Cetya Therapeutics Inc
  • CRISPR Therapeutics AG
  • CSL Ltd
  • Disc Medicine Inc
  • DisperSol Technologies LLC
  • EdiGene Inc
  • Editas Medicine Inc
  • EmeraMed Ltd
  • Errant Gene Therapeutics LLC
  • ExCellThera Inc
  • Fulcrum Therapeutics Inc
  • Gamida Cell Ltd
  • Gilead Sciences Inc
  • Imara Inc
  • Invenux LLC
  • Ionis Pharmaceuticals Inc
  • Kymab Ltd
  • Merganser Biotech Inc
  • Nanjing Transthera Biosciences Co Ltd
  • Nanomedic Inc
  • Orchard Therapeutics Plc
  • Phoenicia Biosciences Inc
  • Rare Partners Srl
  • Regenacy Pharmaceuticals LLC
  • Sangamo Therapeutics Inc
  • Sanquin Plasma Products BV
  • Shanghai Bioray Laboratory Inc
  • Silence Therapeutics Plc
  • Syros Pharmaceuticals Inc
  • Vera Therapeutics Inc
  • Vifor Pharma AG