The Gene Therapy R&D Market Report 2022-2032: This report will prove invaluable to leading firms striving for new revenue pockets if they wish to better understand the industry and its underlying dynamics. It will be useful for companies that would like to expand into different industries or to expand their existing operations in a new region.
The costliest medication in the world right now is Zolgensma, which treats spinal muscular atrophy, a rare hereditary illness that harms nerve cells and causes muscle degeneration. The life-saving medication's one-time treatment for a young child costs $2.1 million. While Zolgensma's excessive cost is an incongruity at present times, there will be several cell & gene therapies available over the next ten years, with prices ranging from thousands to millions of dollars for a single dose. By 2025, the FDA is anticipated to approve 10-20 cell & gene therapies annually.
Diversification of Technical Risks is a Key Strategy for Winning in the Gene Therapy R&D Market
The majority of the biotechnology firms associated with gene therapies are established across a special technology platform i.e., novel viral capsid that could have favoured acceptance in an organ system. Most of them continue to de-risk the technology as soon as possible, with the underlying technology platform that gave birth to the gene therapy candidates often being the main feature across chosen indications. This focuses risk on the technology platform & exposes the company to a catastrophic event that would have a negative impact on the entire portfolio. When it comes to this challenge, early-stage gene therapy firms often lack this choice; and once the newly founded technology achieves traction, executives will often follow adjacent plans that diversify risk & optimize prospects for the company. Companies working on gene therapies may evolve distinct viral delivery vectors or technologies for in vivo & ex vivo applications. Furthermore, balancing spending levels between developed and emerging channels, as well as deciding whether to implement new innovations in-house or obtain them from outside sources, is difficult. Importantly, strategic decisions about technology should be matched with strategic decisions about indication mix to ensure a clear future path.400 million People Suffer from One or More of Over 7,000 Rare Diseases
About 400 million people globally suffer from one or more of over 7,000 rare diseases reported. Rare disease affects between 3.5% and 5.9% of the world's population. The cause of 72% of rare diseases is hereditary, while others are triggered by pathogens (bacterial or viral), asthma, and environmental conditions, or are degenerative and proliferative in nature. Approximately, 70% of genetic rare diseases begin in childhood. Symptoms that are relatively normal can obscure underlying unusual disorders, resulting in misdiagnosis and treatment delays. The lack of loss of mobility caused by the chronic, worsening, degenerative, and often life-threatening manifestations of the condition has a significant effect on the patient's quality of life. Thus, the rising number of rare disease patients around the world is anticipated to drive the gene therapy application in this segment during the forecast period.The costliest medication in the world right now is Zolgensma, which treats spinal muscular atrophy, a rare hereditary illness that harms nerve cells and causes muscle degeneration. The life-saving medication's one-time treatment for a young child costs $2.1 million. While Zolgensma's excessive cost is an incongruity at present times, there will be several cell & gene therapies available over the next ten years, with prices ranging from thousands to millions of dollars for a single dose. By 2025, the FDA is anticipated to approve 10-20 cell & gene therapies annually.
Asia-Pacific Region Remains a Hub for Advanced Therapy Medicinal Products
With the many legislative initiatives put forth by the governments to promote innovation, research, and development in Asia-Pacific, the area remains a hub for advanced therapy medicinal products. Over the course of the projected period, this is expected to propel market expansion. A*STAR's Bioprocessing Technology Institute (BTI) and WuXi Advanced Therapies, a fully owned subsidiary of WuXi AppTec, established a new agreement in May 2022 to introduce WuXi ATU's unique Tetracycline-Enabled Self-Silencing Adenovirus (TESSA) technology in the Asia-Pacific area. WuXi ATU will provide the resources, tools, funds, and training necessary to advance the development and commercialization of TESSA technology in Singapore as part of this partnership. BTI will support WuXi ATU in its research and development of cell and gene therapy in Singapore by providing research skills, facilities, and access to its network of partners.What Are These Questions You Should Ask Before Buying A Market Research Report?
- How is the gene therapy R&D market evolving?
- What is driving and restraining the gene therapy R&D market?
- How will each gene therapy R&D submarket segment grow over the forecast period and how much revenue will these submarkets account for in 2032?
- How will the market shares for each gene therapy R&D submarket develop from 2022 to 2032?
- What will be the main driver for the overall market from 2022 to 2032?
- Will leading gene therapy R&D markets broadly follow the macroeconomic dynamics, or will individual national markets outperform others?
- How will the market shares of the national markets change by 2032 and which geographical region will lead the market in 2032?
- Who are the leading players and what are their prospects over the forecast period?
- What are the gene therapy R&D projects for these leading companies?
- How will the industry evolve during the period between 2022 and 2032? What are the implication of gene therapy R&D projects taking place now and over the next 10 years?
- Is there a greater need for product commercialisation to further scale the gene therapy R&D market?
- Where is the gene therapy R&D market heading? And how can you ensure you are at the forefront of the market?
- What can be the best investment options for new product and service lines?
- What are the key prospects for moving companies into a new growth path? C-suite?
You need to discover how this will impact the Gene Therapy R&D Market today, and over the next 10 years:
- Our 461-page report provides 169 tables and 228 charts/graphs exclusively to you.
- The report highlights key lucrative areas in the industry so you can target them - NOW.
- Contains in-depth analysis of global, regional and national sales and growth
- Highlights for you the key successful trends, changes and revenue projections made by your competitors
Forecasts to 2032 and other analyses reveal the commercial prospects
- In addition to revenue forecasting to 2032, the new study provides you with recent results, growth rates, and market shares.
- You find original analyses, with business outlooks and developments.
- Discover qualitative analyses (including market dynamics, drivers, opportunities, restraints and challenges), PEST analysis, Porter’s Five Forces and recent developments.
Segments Covered in the Report
Disease
- Cancer
- Rare Diseases
- Oncologic
- Non-oncologic
- Cardiovascular Diseases
- Ophthalmic Diseases
- Haematology
- Neurological
- Diabetes Mellitus
- Other Diseases
Vector
- Viral
- Retrovirus
- Adenovirus
- AAV
- Lentivirus
- Others
- Non-viral
- Naked DNA
- Gene Gun
- Electroporation
- Lipofection
Techniques
- Gene Augmentation Therapy
- Gene Replacement Therapy
Participants
- Small/Medium Pharma & Biotech
- Universities & Research Institutes
- Hospitals
- Government & Public Bodies
- Big Pharma
North America
- U.S.
- Canada
Europe
- Germany
- UK
- France
- Italy
- Spain
- Russia
- Rest of Europe
Asia Pacific
- Japan
- China
- India
- Australia
- South Korea
- South East Asia
- Rest of Asia Pacific
Latin America
- Brazil
- Mexico
- Rest of Latin America
MEA
- GCC
- South Africa
- Rest of MEA
Leading companies and the potential for market growth
- Astellas Pharma Inc.
- American Gene Technologies
- Applied Genetic
- Bayer
- Benitec BioPharma
- Biogen
- Bluebird Bio
- Bristol Myers Squibb
- Calimmune, Inc. (CSL Behiring)
- Cellectis
- F. Hoffmann-La Roche Ltd.
- GeneQuine Biotherapeutics
- GenSight Biologics
- Gilead Lifesciences, Inc.
- Novartis AG
- OCUGEN, INC.
- Orchard Therapeutics
- Oxford Biomedica
- Pfizer, Inc.
- REGENXBIO Inc.
- Sangamo Therapeutics, Inc.
- Sanofi
- Sarepta Therapeutics, Inc.
- Spark Therapeutics (Subsidiary of Roche)
- Takeda Pharmaceuticals
- Taysha GTx
- Transgene
- UniQure NV
- Voyager Therapeutics
- ViGeneron.
How the Gene Therapy R&D Market, 2022 to 2032 Market report helps you?
In summary, this 460+ page report provides you with the following knowledge:- Revenue forecasts to 2032 for Gene Therapy R&D Market, 2022 to 2032 Market, with forecasts for disease, vector, techniques, and participants size each forecasted at a global and regional level- discover the industry’s prospects, finding the most lucrative places for investments and revenues
- Revenue forecasts to 2032 for 5 regional and 18 key national markets - See forecasts for the Gene Therapy R&D Market, 2022 to 2032 market in North America, Europe, Asia-Pacific, Latin America and MEA. Also forecasted is the market in the US, Canada, Mexico, Brazil, Germany, France, UK, Italy, China, India, Japan, and Australia among other prominent economies.
- Prospects for established firms and those seeking to enter the market- including company profiles for 30 of the major companies involved in the Gene Therapy R&D Market, 2022 to 2032 Market.
Information found nowhere else
With this new report title, you are less likely to fall behind in knowledge or miss out on opportunities. See how this work could benefit your research, analyses, and decisions. The study is for everybody needing commercial analyses for the Gene Therapy R&D Market, 2022 to 2032 Market and leading companies. You will find data, trends and predictions.Table of Contents
1 Report Overview
3 Market Overview
4 Gene Therapy R&D Market Analysis by Disease
5 Gene Therapy R&D Market Analysis by Vector
6 Gene Therapy R&D Market Analysis by Techniques
7 Gene Therapy R&D Market Analysis by Participants
8 Gene Therapy R&D Market Analysis by Region
9 North America Gene Therapy R&D Market Analysis
10 Europe Gene Therapy R&D Market Analysis
11 Asia Pacific Gene Therapy R&D Market Analysis
12 Latin America Gene Therapy R&D Market Analysis
13 MEA Gene Therapy R&D Market Analysis
14 Company Profiles
15 Conclusion and Recommendations
List of Tables
List of Figures
Companies Mentioned
- American Gene Technologies
- Applied Genetic
- Astellas Pharma Inc.
- Bayer
- Benitec BioPharma
- Biogen
- Bluebird Bio
- Bristol Myers Squibb
- Calimmune, Inc. (CSL Behiring)
- Cellectis
- F. Hoffmann-La Roche Ltd.
- GeneQuine Biotherapeutics
- GenSight Biologics
- Gilead Lifesciences, Inc.
- Novartis AG
- Ocugen, Inc.
- Orchard Therapeutics
- Oxford Biomedica
- Pfizer, Inc.
- REGENXBIO Inc.
- Sangamo Therapeutics, Inc.
- Sanofi
- Sarepta Therapeutics, Inc.
- Spark Therapeutics (Subsidiary of Roche)
- Takeda Pharmaceuticals
- Taysha GTx
- Transgene
- UniQure N. V.
- ViGeneron
- Voyager Therapeutics
- 4D Molecular Therapeutics
- Abeona Therapeutics
- Actus Therapeutics
- Adrenas
- Adverum Biotechnologies
- Akouos
- Amicus Therapeutics
- Apollo Therapeutics
- Aruvant Sciences
- Aspa Therapeutics
- Audentes
- AVROBIO
- Axovant Sciences Ltd
- BioVec Pharma
- Brainvectis SAS
- Catalyst Biosciences
- CavoGene Lifesciences
- Copernicus Therapeutics
- CRISPR Therapeutics AG
- Editas Medicine
- Enzo Biochem
- Errant Gene Therapeutics
- Esteve Pharmaceuticals SA
- Excision BioTherapeutics
- Exonics Therapeutics
- Expression Therapeutics
- Fibrocell Science
- Freeline Therapeutics
- Gemini Therapeutics
- Generation Bio Corp.
- Genethon SA
- GenSight Biologics SA
- Gyroscope Therapeutics
- Hemera Biosciences
- Holostem Terapie Avanzate Srl
- Homology Medicines
- Horama SA
- Immusoft Corp.
- iTherapeutics Corp.
- IVERIC bio
- Krystal Biotech
- Lamellar Biomedical
- Logicbio Therapeutics
- Lysogene
- Lysogene SAS/ Sarepta Therapeutics
- MeiraGTx
- Milo Biotechnology
- Mustang Bio
- NanoScope Technologies
- NeuExcell Therapeutics
- Nightstar Therapeutics/
- Passage Bio
- Therapeutics
- PTC Therapeutics
- Renova Therapeutics
- Rocket Pharmaceuticals
- Rubius Therapeutics
- SanBio Co
- Tamid Bio
- Telocyte
- Temprian Therapeutics
- Tocagen
- Tolerion
- Ultragenyx Pharmaceutical
- ViroMed Co Ltd
- Vivet Therapeutics SAS
- Gene Therapy Net
- Informa UK Limited
- IntechOpen
- JOURNAL OF GENERAL VIROLOGY
- Massachusetts Medical Society
- National Center for Biotechnology Information
- Pan European Networks Ltd
- Pharma Manufacturing
- Pharmaceutical-Networking.com
- The Alliance for Regenerative Medicine
- The Royal Society