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Pompe Disease Market by Product, Patient Type, Treatment Regimen, Distribution Channel - Global Forecast to 2030

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  • 182 Pages
  • May 2025
  • Region: Global
  • 360iResearch™
  • ID: 4968988
UP TO OFF until Dec 31st 2025
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The Pompe Disease market is rapidly evolving with significant clinical, scientific, and policy-driven changes shaping future care models and investment priorities. For leadership teams, understanding current dynamics and anticipating upcoming shifts will be critical to navigate both complexity and opportunity in rare disease management.

POMPE DISEASE MARKET SNAPSHOT

The Pompe Disease Market expanded from USD 1.59 billion in 2024 to USD 1.68 billion in 2025 and is projected to sustain momentum, achieving a CAGR of 5.63% to reach USD 2.21 billion by 2030. This trajectory reflects ongoing innovation in genetic therapeutics, evolving regulatory landscapes, and increasing stakeholder advocacy. Market participants face a complex interplay among new therapies, shifting access pathways, and regional adoption patterns, making informed decisions more critical than ever.

Scope & Segmentation

This market research provides multi-dimensional insights across product, patient cohort, therapeutic regimen, and distribution channel, as well as region and company analysis:

  • Product: Alglucosidase Alfa, Avalglucosidase Alfa
  • Patient Type: Infantile Onset, Late Onset
  • Treatment Regimen: Biweekly Infusion, Monthly Infusion
  • Distribution Channel: Hospital Pharmacy, Retail Pharmacy, Specialty Pharmacy
  • Regional Coverage: Americas (United States, Canada, Mexico, Brazil, Argentina), Europe, Middle East & Africa (including United Kingdom, Germany, France, Russia, Italy, Spain, United Arab Emirates, Saudi Arabia, among others), Asia-Pacific (China, India, Japan, Australia, South Korea, and additional APAC countries)
  • Leading Companies: Sanofi S.A., Amicus Therapeutics, Inc., Shionogi Inc., Maze Therapeutics, GeneCradle Pharmaceutical

The segmentation embraces evolving therapies, highlights access points, and captures the diversity of global reimbursement trends, technological adoption, and patient support initiatives.

Key Takeaways

  • Clinical demand is increasingly defined by differentiated therapeutic profiles, with advanced gene therapies and pharmacological chaperones advancing alongside established enzyme replacement protocols.
  • Patient subgroups, such as those with infantile-onset or late-onset Pompe disease, require tailored management, driving innovation in both dosing strategies and support services.
  • Distribution channel optimization is becoming essential; hospital pharmacies support acute, complex cases while specialty and retail pharmacies offer scalable solutions for stable patients.
  • Regional market heterogeneity persists due to varying reimbursement systems, with local clinical evidence and public-private partnerships influencing treatment uptake.
  • Industry leadership is marked by robust strategic alliances, gene therapy pipeline progress, and integrated patient programs encompassing genetic counseling and remote monitoring.

Tariff Impact: Navigating 2025 Policy Shifts

Upcoming U.S. tariff adjustments in 2025 are reshaping procurement costs for imported biologicals and critical Pompe disease therapies. These changes are prompting manufacturers to reevaluate supply chain strategies, with some leaning on local production partnerships and others leveraging logistics optimization to mitigate increased duties. Healthcare systems are expected to respond with tighter formulary controls and creative value-based agreements, which could intensify negotiations and recalibrate budget allocations. Stakeholders proactively building supply chain resilience and flexible pricing models will be best equipped to sustain patient access and support market continuity.

Methodology & Data Sources

This analysis employs rigorous triangulation of primary interviews with clinicians, payers, patient advocates, and executives, complemented by reviews of regulatory filings, scientific literature, and health technology assessment dossiers. Each insight is validated across multiple reputable sources, and an expert advisory panel ensures relevance and integrity throughout the research cycle.

Why This Report Matters

  • Equips senior decision-makers with actionable intelligence on emerging therapies, access dynamics, and commercial strategies in a complex rare disease sector.
  • Supports resource allocation and market entry by mapping regional adoption patterns and regulatory requirements specific to Pompe disease.
  • Enables effective engagement with key stakeholders—from clinicians to payers and advocacy leaders—by providing credible, up-to-date evidence guiding investment and collaboration.

Conclusion

This executive summary consolidates core insights needed to act decisively in the changing Pompe Disease market. Integrating these findings will inform strategies, foster resilience, and deliver value for organizations and patients alike.

 

Additional Product Information:

  • Purchase of this report includes 1 year online access with quarterly updates.
  • This report can be updated on request. Please contact our Customer Experience team using the Ask a Question widget on our website.

Table of Contents

1. Preface
1.1. Objectives of the Study
1.2. Market Segmentation & Coverage
1.3. Years Considered for the Study
1.4. Currency & Pricing
1.5. Language
1.6. Stakeholders
2. Research Methodology
2.1. Define: Research Objective
2.2. Determine: Research Design
2.3. Prepare: Research Instrument
2.4. Collect: Data Source
2.5. Analyze: Data Interpretation
2.6. Formulate: Data Verification
2.7. Publish: Research Report
2.8. Repeat: Report Update
3. Executive Summary
4. Market Overview
4.1. Introduction
4.2. Market Sizing & Forecasting
5. Market Dynamics
6. Market Insights
6.1. Porter’s Five Forces Analysis
6.2. PESTLE Analysis
7. Cumulative Impact of United States Tariffs 2025
8. Pompe Disease Market, by Product
8.1. Introduction
8.2. Alglucosidase Alfa
8.3. Avalglucosidase Alfa
9. Pompe Disease Market, by Patient Type
9.1. Introduction
9.2. Infantile Onset
9.3. Late Onset
10. Pompe Disease Market, by Treatment Regimen
10.1. Introduction
10.2. Biweekly Infusion
10.3. Monthly Infusion
11. Pompe Disease Market, by Distribution Channel
11.1. Introduction
11.2. Hospital Pharmacy
11.3. Retail Pharmacy
11.4. Specialty Pharmacy
12. Americas Pompe Disease Market
12.1. Introduction
12.2. United States
12.3. Canada
12.4. Mexico
12.5. Brazil
12.6. Argentina
13. Europe, Middle East & Africa Pompe Disease Market
13.1. Introduction
13.2. United Kingdom
13.3. Germany
13.4. France
13.5. Russia
13.6. Italy
13.7. Spain
13.8. United Arab Emirates
13.9. Saudi Arabia
13.10. South Africa
13.11. Denmark
13.12. Netherlands
13.13. Qatar
13.14. Finland
13.15. Sweden
13.16. Nigeria
13.17. Egypt
13.18. Turkey
13.19. Israel
13.20. Norway
13.21. Poland
13.22. Switzerland
14. Asia-Pacific Pompe Disease Market
14.1. Introduction
14.2. China
14.3. India
14.4. Japan
14.5. Australia
14.6. South Korea
14.7. Indonesia
14.8. Thailand
14.9. Philippines
14.10. Malaysia
14.11. Singapore
14.12. Vietnam
14.13. Taiwan
15. Competitive Landscape
15.1. Market Share Analysis, 2024
15.2. FPNV Positioning Matrix, 2024
15.3. Competitive Analysis
15.3.1. Sanofi S.A.
15.3.2. Amicus Therapeutics, Inc.
15.3.3. Shionogi Inc.
15.3.4. Maze Therapeutics
15.3.5. GeneCradle Pharmaceutical
16. ResearchAI
17. ResearchStatistics
18. ResearchContacts
19. ResearchArticles
20. Appendix
List of Figures
FIGURE 1. POMPE DISEASE MARKET MULTI-CURRENCY
FIGURE 2. POMPE DISEASE MARKET MULTI-LANGUAGE
FIGURE 3. POMPE DISEASE MARKET RESEARCH PROCESS
FIGURE 4. GLOBAL POMPE DISEASE MARKET SIZE, 2018-2030 (USD MILLION)
FIGURE 5. GLOBAL POMPE DISEASE MARKET SIZE, BY REGION, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 6. GLOBAL POMPE DISEASE MARKET SIZE, BY COUNTRY, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 7. GLOBAL POMPE DISEASE MARKET SIZE, BY PRODUCT, 2024 VS 2030 (%)
FIGURE 8. GLOBAL POMPE DISEASE MARKET SIZE, BY PRODUCT, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 9. GLOBAL POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2024 VS 2030 (%)
FIGURE 10. GLOBAL POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 11. GLOBAL POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2024 VS 2030 (%)
FIGURE 12. GLOBAL POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 13. GLOBAL POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2024 VS 2030 (%)
FIGURE 14. GLOBAL POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 15. AMERICAS POMPE DISEASE MARKET SIZE, BY COUNTRY, 2024 VS 2030 (%)
FIGURE 16. AMERICAS POMPE DISEASE MARKET SIZE, BY COUNTRY, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 17. UNITED STATES POMPE DISEASE MARKET SIZE, BY STATE, 2024 VS 2030 (%)
FIGURE 18. UNITED STATES POMPE DISEASE MARKET SIZE, BY STATE, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 19. EUROPE, MIDDLE EAST & AFRICA POMPE DISEASE MARKET SIZE, BY COUNTRY, 2024 VS 2030 (%)
FIGURE 20. EUROPE, MIDDLE EAST & AFRICA POMPE DISEASE MARKET SIZE, BY COUNTRY, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 21. ASIA-PACIFIC POMPE DISEASE MARKET SIZE, BY COUNTRY, 2024 VS 2030 (%)
FIGURE 22. ASIA-PACIFIC POMPE DISEASE MARKET SIZE, BY COUNTRY, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 23. POMPE DISEASE MARKET SHARE, BY KEY PLAYER, 2024
FIGURE 24. POMPE DISEASE MARKET, FPNV POSITIONING MATRIX, 2024
List of Tables
TABLE 1. POMPE DISEASE MARKET SEGMENTATION & COVERAGE
TABLE 2. UNITED STATES DOLLAR EXCHANGE RATE, 2018-2024
TABLE 3. GLOBAL POMPE DISEASE MARKET SIZE, 2018-2030 (USD MILLION)
TABLE 4. GLOBAL POMPE DISEASE MARKET SIZE, BY REGION, 2018-2030 (USD MILLION)
TABLE 5. GLOBAL POMPE DISEASE MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
TABLE 6. GLOBAL POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 7. GLOBAL POMPE DISEASE MARKET SIZE, BY ALGLUCOSIDASE ALFA, BY REGION, 2018-2030 (USD MILLION)
TABLE 8. GLOBAL POMPE DISEASE MARKET SIZE, BY AVALGLUCOSIDASE ALFA, BY REGION, 2018-2030 (USD MILLION)
TABLE 9. GLOBAL POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 10. GLOBAL POMPE DISEASE MARKET SIZE, BY INFANTILE ONSET, BY REGION, 2018-2030 (USD MILLION)
TABLE 11. GLOBAL POMPE DISEASE MARKET SIZE, BY LATE ONSET, BY REGION, 2018-2030 (USD MILLION)
TABLE 12. GLOBAL POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 13. GLOBAL POMPE DISEASE MARKET SIZE, BY BIWEEKLY INFUSION, BY REGION, 2018-2030 (USD MILLION)
TABLE 14. GLOBAL POMPE DISEASE MARKET SIZE, BY MONTHLY INFUSION, BY REGION, 2018-2030 (USD MILLION)
TABLE 15. GLOBAL POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 16. GLOBAL POMPE DISEASE MARKET SIZE, BY HOSPITAL PHARMACY, BY REGION, 2018-2030 (USD MILLION)
TABLE 17. GLOBAL POMPE DISEASE MARKET SIZE, BY RETAIL PHARMACY, BY REGION, 2018-2030 (USD MILLION)
TABLE 18. GLOBAL POMPE DISEASE MARKET SIZE, BY SPECIALTY PHARMACY, BY REGION, 2018-2030 (USD MILLION)
TABLE 19. AMERICAS POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 20. AMERICAS POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 21. AMERICAS POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 22. AMERICAS POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 23. AMERICAS POMPE DISEASE MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
TABLE 24. UNITED STATES POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 25. UNITED STATES POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 26. UNITED STATES POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 27. UNITED STATES POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 28. UNITED STATES POMPE DISEASE MARKET SIZE, BY STATE, 2018-2030 (USD MILLION)
TABLE 29. CANADA POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 30. CANADA POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 31. CANADA POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 32. CANADA POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 33. MEXICO POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 34. MEXICO POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 35. MEXICO POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 36. MEXICO POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 37. BRAZIL POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 38. BRAZIL POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 39. BRAZIL POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 40. BRAZIL POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 41. ARGENTINA POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 42. ARGENTINA POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 43. ARGENTINA POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 44. ARGENTINA POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 45. EUROPE, MIDDLE EAST & AFRICA POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 46. EUROPE, MIDDLE EAST & AFRICA POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 47. EUROPE, MIDDLE EAST & AFRICA POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 48. EUROPE, MIDDLE EAST & AFRICA POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 49. EUROPE, MIDDLE EAST & AFRICA POMPE DISEASE MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
TABLE 50. UNITED KINGDOM POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 51. UNITED KINGDOM POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 52. UNITED KINGDOM POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 53. UNITED KINGDOM POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 54. GERMANY POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 55. GERMANY POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 56. GERMANY POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 57. GERMANY POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 58. FRANCE POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 59. FRANCE POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 60. FRANCE POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 61. FRANCE POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 62. RUSSIA POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 63. RUSSIA POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 64. RUSSIA POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 65. RUSSIA POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 66. ITALY POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 67. ITALY POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 68. ITALY POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 69. ITALY POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 70. SPAIN POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 71. SPAIN POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 72. SPAIN POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 73. SPAIN POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 74. UNITED ARAB EMIRATES POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 75. UNITED ARAB EMIRATES POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 76. UNITED ARAB EMIRATES POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 77. UNITED ARAB EMIRATES POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 78. SAUDI ARABIA POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 79. SAUDI ARABIA POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 80. SAUDI ARABIA POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 81. SAUDI ARABIA POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 82. SOUTH AFRICA POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 83. SOUTH AFRICA POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 84. SOUTH AFRICA POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 85. SOUTH AFRICA POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 86. DENMARK POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 87. DENMARK POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 88. DENMARK POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 89. DENMARK POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 90. NETHERLANDS POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 91. NETHERLANDS POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 92. NETHERLANDS POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 93. NETHERLANDS POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 94. QATAR POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 95. QATAR POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 96. QATAR POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 97. QATAR POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 98. FINLAND POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 99. FINLAND POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 100. FINLAND POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 101. FINLAND POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 102. SWEDEN POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 103. SWEDEN POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 104. SWEDEN POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 105. SWEDEN POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 106. NIGERIA POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 107. NIGERIA POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 108. NIGERIA POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 109. NIGERIA POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 110. EGYPT POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 111. EGYPT POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 112. EGYPT POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 113. EGYPT POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 114. TURKEY POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 115. TURKEY POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 116. TURKEY POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 117. TURKEY POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 118. ISRAEL POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 119. ISRAEL POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 120. ISRAEL POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 121. ISRAEL POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 122. NORWAY POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 123. NORWAY POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 124. NORWAY POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 125. NORWAY POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 126. POLAND POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 127. POLAND POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 128. POLAND POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 129. POLAND POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 130. SWITZERLAND POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 131. SWITZERLAND POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 132. SWITZERLAND POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 133. SWITZERLAND POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 134. ASIA-PACIFIC POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 135. ASIA-PACIFIC POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 136. ASIA-PACIFIC POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 137. ASIA-PACIFIC POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 138. ASIA-PACIFIC POMPE DISEASE MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
TABLE 139. CHINA POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 140. CHINA POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 141. CHINA POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 142. CHINA POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 143. INDIA POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 144. INDIA POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 145. INDIA POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 146. INDIA POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 147. JAPAN POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 148. JAPAN POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 149. JAPAN POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 150. JAPAN POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 151. AUSTRALIA POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 152. AUSTRALIA POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 153. AUSTRALIA POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 154. AUSTRALIA POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 155. SOUTH KOREA POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 156. SOUTH KOREA POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 157. SOUTH KOREA POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 158. SOUTH KOREA POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 159. INDONESIA POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 160. INDONESIA POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 161. INDONESIA POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 162. INDONESIA POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 163. THAILAND POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 164. THAILAND POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 165. THAILAND POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 166. THAILAND POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 167. PHILIPPINES POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 168. PHILIPPINES POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 169. PHILIPPINES POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 170. PHILIPPINES POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 171. MALAYSIA POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 172. MALAYSIA POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 173. MALAYSIA POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 174. MALAYSIA POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 175. SINGAPORE POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 176. SINGAPORE POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 177. SINGAPORE POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 178. SINGAPORE POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 179. VIETNAM POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 180. VIETNAM POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 181. VIETNAM POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 182. VIETNAM POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 183. TAIWAN POMPE DISEASE MARKET SIZE, BY PRODUCT, 2018-2030 (USD MILLION)
TABLE 184. TAIWAN POMPE DISEASE MARKET SIZE, BY PATIENT TYPE, 2018-2030 (USD MILLION)
TABLE 185. TAIWAN POMPE DISEASE MARKET SIZE, BY TREATMENT REGIMEN, 2018-2030 (USD MILLION)
TABLE 186. TAIWAN POMPE DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 187. POMPE DISEASE MARKET SHARE, BY KEY PLAYER, 2024
TABLE 188. POMPE DISEASE MARKET, FPNV POSITIONING MATRIX, 2024

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Companies Mentioned

The companies profiled in this Pompe Disease market report include:
  • Sanofi S.A.
  • Amicus Therapeutics, Inc.
  • Shionogi Inc.
  • Maze Therapeutics
  • GeneCradle Pharmaceutical

Table Information