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Type 1 Gaucher Disease Treatment Market - Global Forecast to 2030

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    Report

  • 196 Pages
  • May 2025
  • Region: Global, United States
  • 360iResearch™
  • ID: 6079098
1h Free Analyst Time
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Type 1 Gaucher disease represents the most prevalent form of a rare lysosomal storage disorder, characterized by deficient glucocerebrosidase activity leading to lipid accumulation in macrophages and widespread organ involvement. Over the last decade, treatment paradigms have evolved from enzyme replacement therapy as the cornerstone to include substrate reduction strategies and pioneering gene therapy approaches. As patient advocacy groups push for more personalized care, stakeholders across the value chain-ranging from research institutions to pharmaceutical innovators-are recalibrating priorities to address unmet needs in pediatric, adult, male and female populations.

Against this backdrop, decision-makers must navigate an increasingly complex ecosystem shaped by shifting regulatory incentives, novel administration routes, partnership models, and emerging biomarker applications. This executive summary distills the critical trends, segmentation insights, regional dynamics, and competitive developments redefining the Type 1 Gaucher disease treatment landscape. It equips industry leaders with clear, actionable intelligence to inform strategic planning, investment decisions, and patient-centric program design, ensuring that advances in science translate into tangible clinical and commercial impact.

Transformative Shifts in Therapeutic Approaches and Innovations

In recent years, the Type 1 Gaucher disease market has undergone transformative shifts driven by breakthroughs in molecular biology, regulatory flexibility, and patient-centric innovation. Enzyme replacement therapy, once the sole standard of care, now competes alongside substrate reduction therapy options that target ceramide metabolism and increasingly sophisticated gene therapy candidates aiming to correct the underlying genetic defect. Moreover, the integration of diagnostic, predictive, and prognostic biomarkers has enabled clinicians to tailor treatment selection and monitor therapeutic efficacy with unprecedented precision.

Simultaneously, digital health solutions are gaining traction to enhance remote monitoring, adherence tracking, and real-world evidence generation. These advances align with broader industry trends toward outcome-based contracting and value-driven care. Strategic alliances between academic & research institutes, clinical research organizations, and leading pharmaceutical companies have accelerated development timelines, while fast track and orphan drug designations streamline regulatory pathways. Furthermore, life sciences collaborations are fostering cross-disciplinary expertise, enabling the design of combination regimens that harness complementary mechanisms of action.

As the landscape continues to evolve, market participants must stay agile, leveraging data analytics and patient insights to optimize clinical trial design, refine distribution strategies across hospital, online and retail pharmacies, and reinforce home healthcare capabilities. This shift underscores a new era of innovation-where personalized, accessible, and cost-effective treatments converge to redefine patient outcomes.

Assessing the Cumulative Impact of United States Tariffs in 2025

The introduction of new tariffs on biologic and pharmaceutical imports in the United States, effective 2025, has had a material influence on the Type 1 Gaucher disease treatment ecosystem. Components for enzyme replacement therapies and advanced gene therapy vectors now face incremental cost pressures, prompting manufacturers to revise supply chain strategies and negotiate pricing and reimbursement agreements with greater urgency. Payors, in response, are intensifying scrutiny of cost-effectiveness data and demanding robust real-world evidence to justify premium pricing.

These developments have driven companies to explore localized manufacturing partnerships and to invest in process optimization technologies that reduce production expenses. At the same time, stakeholders are diversifying procurement channels-shifting portions of inventory management toward hospital pharmacies and specialized clinics to mitigate tariff impacts. Reimbursement models have adapted, with payors increasingly favoring outcome-based contracts that tie payment to clinical milestones.

Looking ahead, industry leaders must account for these tariff-induced dynamics in forecasting operational budgets, negotiating terms with distributors, and calibrating market access strategies to maintain patient affordability without compromising innovation.

Key Insights from Comprehensive Market Segmentation

An in-depth segmentation analysis reveals distinct opportunities and challenges across multiple market dimensions. Based on type of treatment, enzyme replacement therapy remains the established backbone for moderate and severe cases, yet substrate reduction therapy is gaining adoption in mild to moderate presentations, and gene therapy holds promise for transformative, durable benefit. When examining patient demographics, treatment patterns vary significantly: pediatric patients often require parenteral administration of enzyme formulations, while adult and female cohorts show growing interest in oral substrate reduction options for convenience and quality of life. Male patients exhibit similar trends, though adherence programs must account for gender-specific support needs.

Assessing patient health status, those with mild disease benefit from early intervention with oral agents to forestall progression, whereas moderate and severe populations continue to rely on intravenous regimens in hospital or specialty clinic settings. End-user insights indicate that home healthcare is becoming a critical component of chronic treatment management, complemented by hospital-based infusions and specialist-led care pathways. By mode of administration, oral therapies are accelerating market penetration, but parenteral options remain indispensable for severe phenotypes and for ensuring consistent drug delivery.

Partnerships among academic & research institutes, clinical research organizations, and pharmaceutical companies are driving clinical trial diversity across Phase I to Phase IV studies, while preclinical investigational and research-stage programs expand the pipeline. Distribution channels reflect evolving patient preferences: hospital pharmacies handle high-touch therapies, online pharmacies enhance convenience for maintenance regimens, and retail outlets support urgent refill needs. Biomarker utilization spans diagnostic assays for early detection, predictive markers guiding therapy selection, and prognostic indicators monitoring long-term outcomes. Regulatory status-EMA authorized, FDA approved, orphan drug designation, and fast track designation-shapes market entry strategies, while associated syndromes such as bone disorders, liver complications, neurologic manifestations including cognitive impairment and seizures, and spleen enlargement inform clinical trial endpoints and label expansion initiatives.

Regional Variations Shaping Treatment Adoption and Access

Regional dynamics are pivotal in shaping treatment adoption, access, and reimbursement frameworks. In the Americas, robust payer networks and early adoption of innovative therapies support leading uptake of enzyme replacement and substrate reduction regimens. The United States market drives global trends, leveraging fast track designations and orphan drug incentives to accelerate time to market. Brazil and Canada are also expanding coverage programs, fostering greater patient access through public-private partnerships and patient support initiatives.

Within Europe, Middle East & Africa, the landscape varies significantly: Western Europe demonstrates high penetration of advanced therapies backed by national health services and centralized genomic screening programs. Conversely, emerging markets in Eastern Europe, the Gulf Cooperation Council states, and select African nations are strengthening regulatory harmonization, yet still face affordability barriers that impede widespread utilization of high-cost biologics. Efforts to introduce subcutaneous formulations and enhance local manufacturing capabilities aim to bridge access gaps.

Asia-Pacific presents a diverse spectrum of maturity: Japan and Australia lead with integrated care models and strong orphan drug pathways, while China’s evolving regulatory environment and growing clinical trial infrastructure accelerate the approval of novel therapeutic classes. South Korea, India, and Southeast Asian markets are pursuing public reimbursement expansions, digital health integration, and collaborative research agreements to bolster domestic capabilities and improve patient outcomes.

Profiles of Leading Industry Stakeholders Driving Progress

The competitive environment features a blend of established pharmaceutical giants, niche biotechs, and emerging innovators driving next-generation therapies. Industry stalwarts such as Pfizer Inc., Sanofi S.A., and Takeda Pharmaceutical Company Limited leverage deep expertise in biologics and global commercialization networks to maintain enzyme replacement therapy leadership, while Amicus Therapeutics, Inc., and BioMarin Pharmaceutical Inc. focus on both substrate reduction strategies and pioneering gene therapy platforms.

Specialty players including Protalix BioTherapeutics, Inc., and Ultragenyx Pharmaceutical Inc. differentiate through novel administration formats, patient support services, and targeted biomarker programs. Collaborative ventures among Actelion Pharmaceuticals Ltd. (now part of Johnson & Johnson), Greenovation Biotech GmbH, ISU ABXIS Co., Ltd., JCR Pharmaceuticals Co., Ltd., and M6P Therapeutics underscore a collective push to harness enzyme enhancement and gene editing technologies. These alliances facilitate shared risk, resource optimization, and accelerated clinical development, positioning the field for sustained innovation.

Actionable Recommendations for Industry Leaders

Leaders should prioritize investment in gene therapy research, expanding manufacturing capacity to meet future demand and capitalize on durable, one-time treatment potential. Strengthening partnerships with academic institutions and clinical research organizations will expedite biomarker validation and streamline trial enrollment. To counter tariff pressures and supply chain disruptions, companies must diversify sourcing strategies, localize production, and pursue outcome-based contracting with payers.

Enhancing patient engagement through digital adherence platforms and specialized support programs will improve long-term adherence and real-world evidence generation. Proactively engaging regulatory agencies under fast track and orphan drug frameworks can accelerate approval timelines, while tailored pricing strategies across hospital, online, and retail pharmacies will safeguard access. Finally, embedding neurologic and visceral endpoints in clinical studies will unlock label expansions and broaden therapeutic indications.

Conclusion: Navigating Future Growth

The Type 1 Gaucher disease treatment landscape stands at a pivotal intersection of scientific innovation, regulatory evolution, and shifting commercial dynamics. Breakthroughs in gene therapy and substrate reduction biology promise to redefine patient outcomes, yet successful translation hinges on strategic alignment across R&D, manufacturing, market access, and patient support functions. As tariffs reshape cost structures, companies must adopt agile supply chain models and reinforce value-based pricing strategies to sustain affordability.

Regional nuances underscore the need for localized market entry plans-leveraging reimbursement incentives in the Americas, harmonizing regulatory pathways in Europe, Middle East & Africa, and tapping into growing clinical research capacity in Asia-Pacific. Competitive differentiation will stem from robust biomarker integration, digital health innovation, and targeted partnerships that amplify development efficiency. By embracing a patient-centric ethos and fostering cross-sector collaboration, industry leaders can navigate complexity and deliver transformative therapies for those affected by Type 1 Gaucher disease.

Market Segmentation & Coverage

This research report categorizes the Type 1 Gaucher Disease Treatment Market to forecast the revenues and analyze trends in each of the following sub-segmentations:

  • Enzyme Replacement Therapy (ERT)
  • Gene Therapy
  • Substrate Reduction Therapy (SRT)
  • Adult Patients
  • Female Patients
  • Male Patients
  • Pediatric Patients
  • Mild Gaucher Disease
  • Moderate Gaucher Disease
  • Severe Gaucher Disease
  • Home Healthcare
  • Hospitals
  • Specialty Clinics
  • Oral
  • Parenteral
  • Academic & Research Institutes
  • Clinical Research Organizations
  • Pharmaceutical Companies
  • Hospital Pharmacies
  • Online Pharmacies
  • Retail Pharmacies
  • Approved Drugs
  • Clinical Trials ●
    • Phase I
    • Phase II
    • Phase III
    • Phase IV
  • Preclinical ●
    • Investigational Drugs
    • Research Stage
  • Diagnostic Biomarkers
  • Predictive Biomarkers
  • Prognostic Biomarkers
  • EMA Authorized
  • Fast Track Designation
  • FDA Approved
  • Orphan Drug Designation
  • Bone Disorders
  • Liver Disorders
  • Neurological Complications ●
    • Cognitive Impairment
    • Seizures
  • Spleen Enlargement

This research report categorizes the Type 1 Gaucher Disease Treatment Market to forecast the revenues and analyze trends in each of the following sub-regions:

  • Americas
    • Argentina
    • Brazil
    • Canada
    • Mexico
    • United States
      • California
      • Florida
      • Illinois
      • New York
      • Ohio
      • Pennsylvania
      • Texas
  • Asia-Pacific
    • Australia
    • China
    • India
    • Indonesia
    • Japan
    • Malaysia
    • Philippines
    • Singapore
    • South Korea
    • Taiwan
    • Thailand
    • Vietnam
  • Europe, Middle East & Africa
    • Denmark
    • Egypt
    • Finland
    • France
    • Germany
    • Israel
    • Italy
    • Netherlands
    • Nigeria
    • Norway
    • Poland
    • Qatar
    • Russia
    • Saudi Arabia
    • South Africa
    • Spain
    • Sweden
    • Switzerland
    • Turkey
    • United Arab Emirates
    • United Kingdom

This research report categorizes the Type 1 Gaucher Disease Treatment Market to delves into recent significant developments and analyze trends in each of the following companies:

  • Actelion Pharmaceuticals Ltd. (acquired by Johnson & Johnson)
  • Amicus Therapeutics, Inc.
  • BioMarin Pharmaceutical Inc.
  • Greenovation Biotech GmbH
  • ISU ABXIS Co., Ltd.
  • JCR Pharmaceuticals Co., Ltd.
  • M6P Therapeutics
  • Pfizer Inc.
  • Protalix BioTherapeutics, Inc.
  • Sanofi S.A.
  • Shire plc (acquired by Takeda)
  • Takeda Pharmaceutical Company Limited
  • Ultragenyx Pharmaceutical Inc.

This product will be delivered within 1-3 business days.

Table of Contents

1. Preface
1.1. Objectives of the Study
1.2. Market Segmentation & Coverage
1.3. Years Considered for the Study
1.4. Currency & Pricing
1.5. Language
1.6. Stakeholders
2. Research Methodology
2.1. Define: Research Objective
2.2. Determine: Research Design
2.3. Prepare: Research Instrument
2.4. Collect: Data Source
2.5. Analyze: Data Interpretation
2.6. Formulate: Data Verification
2.7. Publish: Research Report
2.8. Repeat: Report Update
3. Executive Summary
4. Market Overview
4.1. Introduction
4.2. Market Sizing & Forecasting
5. Market Dynamics
6. Market Insights
6.1. Porter’s Five Forces Analysis
6.2. PESTLE Analysis
7. Cumulative Impact of United States Tariffs 2025
8. Type 1 Gaucher Disease Treatment Market, by Type Of Treatment
8.1. Introduction
8.2. Enzyme Replacement Therapy (ERT)
8.3. Gene Therapy
8.4. Substrate Reduction Therapy (SRT)
9. Type 1 Gaucher Disease Treatment Market, by Patient Demographics
9.1. Introduction
9.2. Adult Patients
9.3. Female Patients
9.4. Male Patients
9.5. Pediatric Patients
10. Type 1 Gaucher Disease Treatment Market, by Patient Health Status
10.1. Introduction
10.2. Mild Gaucher Disease
10.3. Moderate Gaucher Disease
10.4. Severe Gaucher Disease
11. Type 1 Gaucher Disease Treatment Market, by End-User
11.1. Introduction
11.2. Home Healthcare
11.3. Hospitals
11.4. Specialty Clinics
12. Type 1 Gaucher Disease Treatment Market, by Mode Of Administration
12.1. Introduction
12.2. Oral
12.3. Parenteral
13. Type 1 Gaucher Disease Treatment Market, by Life Sciences Partnership
13.1. Introduction
13.2. Academic & Research Institutes
13.3. Clinical Research Organizations
13.4. Pharmaceutical Companies
14. Type 1 Gaucher Disease Treatment Market, by Distribution Channel
14.1. Introduction
14.2. Hospital Pharmacies
14.3. Online Pharmacies
14.4. Retail Pharmacies
15. Type 1 Gaucher Disease Treatment Market, by Stage Of Development
15.1. Introduction
15.2. Approved Drugs
15.3. Clinical Trials ?
15.3.1. Phase I
15.3.2. Phase II
15.3.3. Phase III
15.3.4. Phase IV
15.4. Preclinical ?
15.4.1. Investigational Drugs
15.4.2. Research Stage
16. Type 1 Gaucher Disease Treatment Market, by Biomarker Utilization
16.1. Introduction
16.2. Diagnostic Biomarkers
16.3. Predictive Biomarkers
16.4. Prognostic Biomarkers
17. Type 1 Gaucher Disease Treatment Market, by Regulatory Status
17.1. Introduction
17.2. EMA Authorized
17.3. Fast Track Designation
17.4. FDA Approved
17.5. Orphan Drug Designation
18. Type 1 Gaucher Disease Treatment Market, by Associated Syndromes
18.1. Introduction
18.2. Bone Disorders
18.3. Liver Disorders
18.4. Neurological Complications ?
18.4.1. Cognitive Impairment
18.4.2. Seizures
18.5. Spleen Enlargement
19. Americas Type 1 Gaucher Disease Treatment Market
19.1. Introduction
19.2. Argentina
19.3. Brazil
19.4. Canada
19.5. Mexico
19.6. United States
20. Asia-Pacific Type 1 Gaucher Disease Treatment Market
20.1. Introduction
20.2. Australia
20.3. China
20.4. India
20.5. Indonesia
20.6. Japan
20.7. Malaysia
20.8. Philippines
20.9. Singapore
20.10. South Korea
20.11. Taiwan
20.12. Thailand
20.13. Vietnam
21. Europe, Middle East & Africa Type 1 Gaucher Disease Treatment Market
21.1. Introduction
21.2. Denmark
21.3. Egypt
21.4. Finland
21.5. France
21.6. Germany
21.7. Israel
21.8. Italy
21.9. Netherlands
21.10. Nigeria
21.11. Norway
21.12. Poland
21.13. Qatar
21.14. Russia
21.15. Saudi Arabia
21.16. South Africa
21.17. Spain
21.18. Sweden
21.19. Switzerland
21.20. Turkey
21.21. United Arab Emirates
21.22. United Kingdom
22. Competitive Landscape
22.1. Market Share Analysis, 2024
22.2. FPNV Positioning Matrix, 2024
22.3. Competitive Analysis
22.3.1. Actelion Pharmaceuticals Ltd. (acquired by Johnson & Johnson)
22.3.2. Amicus Therapeutics, Inc.
22.3.3. BioMarin Pharmaceutical Inc.
22.3.4. Greenovation Biotech GmbH
22.3.5. ISU ABXIS Co., Ltd.
22.3.6. JCR Pharmaceuticals Co., Ltd.
22.3.7. M6P Therapeutics
22.3.8. Pfizer Inc.
22.3.9. Protalix BioTherapeutics, Inc.
22.3.10. Sanofi S.A.
22.3.11. Shire plc (acquired by Takeda)
22.3.12. Takeda Pharmaceutical Company Limited
22.3.13. Ultragenyx Pharmaceutical Inc.
23. ResearchAI
24. ResearchStatistics
25. ResearchContacts
26. ResearchArticles
27. Appendix
List of Figures
FIGURE 1. TYPE 1 GAUCHER DISEASE TREATMENT MARKET MULTI-CURRENCY
FIGURE 2. TYPE 1 GAUCHER DISEASE TREATMENT MARKET MULTI-LANGUAGE
FIGURE 3. TYPE 1 GAUCHER DISEASE TREATMENT MARKET RESEARCH PROCESS
FIGURE 4. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, 2018-2030 (USD MILLION)
FIGURE 5. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGION, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 6. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY COUNTRY, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 7. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY TYPE OF TREATMENT, 2024 VS 2030 (%)
FIGURE 8. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY TYPE OF TREATMENT, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 9. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT DEMOGRAPHICS, 2024 VS 2030 (%)
FIGURE 10. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT DEMOGRAPHICS, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 11. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT HEALTH STATUS, 2024 VS 2030 (%)
FIGURE 12. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT HEALTH STATUS, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 13. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY END-USER, 2024 VS 2030 (%)
FIGURE 14. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY END-USER, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 15. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODE OF ADMINISTRATION, 2024 VS 2030 (%)
FIGURE 16. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODE OF ADMINISTRATION, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 17. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIFE SCIENCES PARTNERSHIP, 2024 VS 2030 (%)
FIGURE 18. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIFE SCIENCES PARTNERSHIP, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 19. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DISTRIBUTION CHANNEL, 2024 VS 2030 (%)
FIGURE 20. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DISTRIBUTION CHANNEL, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 21. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STAGE OF DEVELOPMENT, 2024 VS 2030 (%)
FIGURE 22. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STAGE OF DEVELOPMENT, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 23. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BIOMARKER UTILIZATION, 2024 VS 2030 (%)
FIGURE 24. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BIOMARKER UTILIZATION, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 25. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGULATORY STATUS, 2024 VS 2030 (%)
FIGURE 26. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGULATORY STATUS, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 27. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ASSOCIATED SYNDROMES, 2024 VS 2030 (%)
FIGURE 28. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ASSOCIATED SYNDROMES, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 29. AMERICAS TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY COUNTRY, 2024 VS 2030 (%)
FIGURE 30. AMERICAS TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY COUNTRY, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 31. UNITED STATES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STATE, 2024 VS 2030 (%)
FIGURE 32. UNITED STATES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STATE, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 33. ASIA-PACIFIC TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY COUNTRY, 2024 VS 2030 (%)
FIGURE 34. ASIA-PACIFIC TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY COUNTRY, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 35. EUROPE, MIDDLE EAST & AFRICA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY COUNTRY, 2024 VS 2030 (%)
FIGURE 36. EUROPE, MIDDLE EAST & AFRICA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY COUNTRY, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 37. TYPE 1 GAUCHER DISEASE TREATMENT MARKET SHARE, BY KEY PLAYER, 2024
FIGURE 38. TYPE 1 GAUCHER DISEASE TREATMENT MARKET, FPNV POSITIONING MATRIX, 2024
List of Tables
TABLE 1. TYPE 1 GAUCHER DISEASE TREATMENT MARKET SEGMENTATION & COVERAGE
TABLE 2. UNITED STATES DOLLAR EXCHANGE RATE, 2018-2024
TABLE 3. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, 2018-2030 (USD MILLION)
TABLE 4. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGION, 2018-2030 (USD MILLION)
TABLE 5. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
TABLE 6. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY TYPE OF TREATMENT, 2018-2030 (USD MILLION)
TABLE 7. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ENZYME REPLACEMENT THERAPY (ERT), BY REGION, 2018-2030 (USD MILLION)
TABLE 8. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY GENE THERAPY, BY REGION, 2018-2030 (USD MILLION)
TABLE 9. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY (SRT), BY REGION, 2018-2030 (USD MILLION)
TABLE 10. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT DEMOGRAPHICS, 2018-2030 (USD MILLION)
TABLE 11. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ADULT PATIENTS, BY REGION, 2018-2030 (USD MILLION)
TABLE 12. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY FEMALE PATIENTS, BY REGION, 2018-2030 (USD MILLION)
TABLE 13. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MALE PATIENTS, BY REGION, 2018-2030 (USD MILLION)
TABLE 14. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PEDIATRIC PATIENTS, BY REGION, 2018-2030 (USD MILLION)
TABLE 15. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT HEALTH STATUS, 2018-2030 (USD MILLION)
TABLE 16. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MILD GAUCHER DISEASE, BY REGION, 2018-2030 (USD MILLION)
TABLE 17. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODERATE GAUCHER DISEASE, BY REGION, 2018-2030 (USD MILLION)
TABLE 18. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY SEVERE GAUCHER DISEASE, BY REGION, 2018-2030 (USD MILLION)
TABLE 19. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
TABLE 20. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY HOME HEALTHCARE, BY REGION, 2018-2030 (USD MILLION)
TABLE 21. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY HOSPITALS, BY REGION, 2018-2030 (USD MILLION)
TABLE 22. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY SPECIALTY CLINICS, BY REGION, 2018-2030 (USD MILLION)
TABLE 23. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 24. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ORAL, BY REGION, 2018-2030 (USD MILLION)
TABLE 25. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PARENTERAL, BY REGION, 2018-2030 (USD MILLION)
TABLE 26. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIFE SCIENCES PARTNERSHIP, 2018-2030 (USD MILLION)
TABLE 27. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ACADEMIC & RESEARCH INSTITUTES, BY REGION, 2018-2030 (USD MILLION)
TABLE 28. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY CLINICAL RESEARCH ORGANIZATIONS, BY REGION, 2018-2030 (USD MILLION)
TABLE 29. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PHARMACEUTICAL COMPANIES, BY REGION, 2018-2030 (USD MILLION)
TABLE 30. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 31. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY HOSPITAL PHARMACIES, BY REGION, 2018-2030 (USD MILLION)
TABLE 32. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ONLINE PHARMACIES, BY REGION, 2018-2030 (USD MILLION)
TABLE 33. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY RETAIL PHARMACIES, BY REGION, 2018-2030 (USD MILLION)
TABLE 34. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STAGE OF DEVELOPMENT, 2018-2030 (USD MILLION)
TABLE 35. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY APPROVED DRUGS, BY REGION, 2018-2030 (USD MILLION)
TABLE 36. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY CLINICAL TRIALS ?, BY REGION, 2018-2030 (USD MILLION)
TABLE 37. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PHASE I, BY REGION, 2018-2030 (USD MILLION)
TABLE 38. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PHASE II, BY REGION, 2018-2030 (USD MILLION)
TABLE 39. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PHASE III, BY REGION, 2018-2030 (USD MILLION)
TABLE 40. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PHASE IV, BY REGION, 2018-2030 (USD MILLION)
TABLE 41. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY CLINICAL TRIALS ?, 2018-2030 (USD MILLION)
TABLE 42. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PRECLINICAL ?, BY REGION, 2018-2030 (USD MILLION)
TABLE 43. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY INVESTIGATIONAL DRUGS, BY REGION, 2018-2030 (USD MILLION)
TABLE 44. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY RESEARCH STAGE, BY REGION, 2018-2030 (USD MILLION)
TABLE 45. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PRECLINICAL ?, 2018-2030 (USD MILLION)
TABLE 46. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BIOMARKER UTILIZATION, 2018-2030 (USD MILLION)
TABLE 47. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DIAGNOSTIC BIOMARKERS, BY REGION, 2018-2030 (USD MILLION)
TABLE 48. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PREDICTIVE BIOMARKERS, BY REGION, 2018-2030 (USD MILLION)
TABLE 49. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PROGNOSTIC BIOMARKERS, BY REGION, 2018-2030 (USD MILLION)
TABLE 50. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGULATORY STATUS, 2018-2030 (USD MILLION)
TABLE 51. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY EMA AUTHORIZED, BY REGION, 2018-2030 (USD MILLION)
TABLE 52. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY FAST TRACK DESIGNATION, BY REGION, 2018-2030 (USD MILLION)
TABLE 53. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY FDA APPROVED, BY REGION, 2018-2030 (USD MILLION)
TABLE 54. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ORPHAN DRUG DESIGNATION, BY REGION, 2018-2030 (USD MILLION)
TABLE 55. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ASSOCIATED SYNDROMES, 2018-2030 (USD MILLION)
TABLE 56. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BONE DISORDERS, BY REGION, 2018-2030 (USD MILLION)
TABLE 57. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIVER DISORDERS, BY REGION, 2018-2030 (USD MILLION)
TABLE 58. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY NEUROLOGICAL COMPLICATIONS ?, BY REGION, 2018-2030 (USD MILLION)
TABLE 59. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY COGNITIVE IMPAIRMENT, BY REGION, 2018-2030 (USD MILLION)
TABLE 60. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY SEIZURES, BY REGION, 2018-2030 (USD MILLION)
TABLE 61. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY NEUROLOGICAL COMPLICATIONS ?, 2018-2030 (USD MILLION)
TABLE 62. GLOBAL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY SPLEEN ENLARGEMENT, BY REGION, 2018-2030 (USD MILLION)
TABLE 63. AMERICAS TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY TYPE OF TREATMENT, 2018-2030 (USD MILLION)
TABLE 64. AMERICAS TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT DEMOGRAPHICS, 2018-2030 (USD MILLION)
TABLE 65. AMERICAS TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT HEALTH STATUS, 2018-2030 (USD MILLION)
TABLE 66. AMERICAS TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
TABLE 67. AMERICAS TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 68. AMERICAS TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIFE SCIENCES PARTNERSHIP, 2018-2030 (USD MILLION)
TABLE 69. AMERICAS TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 70. AMERICAS TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STAGE OF DEVELOPMENT, 2018-2030 (USD MILLION)
TABLE 71. AMERICAS TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY CLINICAL TRIALS ?, 2018-2030 (USD MILLION)
TABLE 72. AMERICAS TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PRECLINICAL ?, 2018-2030 (USD MILLION)
TABLE 73. AMERICAS TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BIOMARKER UTILIZATION, 2018-2030 (USD MILLION)
TABLE 74. AMERICAS TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGULATORY STATUS, 2018-2030 (USD MILLION)
TABLE 75. AMERICAS TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ASSOCIATED SYNDROMES, 2018-2030 (USD MILLION)
TABLE 76. AMERICAS TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY NEUROLOGICAL COMPLICATIONS ?, 2018-2030 (USD MILLION)
TABLE 77. AMERICAS TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
TABLE 78. ARGENTINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY TYPE OF TREATMENT, 2018-2030 (USD MILLION)
TABLE 79. ARGENTINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT DEMOGRAPHICS, 2018-2030 (USD MILLION)
TABLE 80. ARGENTINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT HEALTH STATUS, 2018-2030 (USD MILLION)
TABLE 81. ARGENTINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
TABLE 82. ARGENTINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 83. ARGENTINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIFE SCIENCES PARTNERSHIP, 2018-2030 (USD MILLION)
TABLE 84. ARGENTINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 85. ARGENTINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STAGE OF DEVELOPMENT, 2018-2030 (USD MILLION)
TABLE 86. ARGENTINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY CLINICAL TRIALS ?, 2018-2030 (USD MILLION)
TABLE 87. ARGENTINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PRECLINICAL ?, 2018-2030 (USD MILLION)
TABLE 88. ARGENTINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BIOMARKER UTILIZATION, 2018-2030 (USD MILLION)
TABLE 89. ARGENTINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGULATORY STATUS, 2018-2030 (USD MILLION)
TABLE 90. ARGENTINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ASSOCIATED SYNDROMES, 2018-2030 (USD MILLION)
TABLE 91. ARGENTINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY NEUROLOGICAL COMPLICATIONS ?, 2018-2030 (USD MILLION)
TABLE 92. BRAZIL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY TYPE OF TREATMENT, 2018-2030 (USD MILLION)
TABLE 93. BRAZIL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT DEMOGRAPHICS, 2018-2030 (USD MILLION)
TABLE 94. BRAZIL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT HEALTH STATUS, 2018-2030 (USD MILLION)
TABLE 95. BRAZIL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
TABLE 96. BRAZIL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 97. BRAZIL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIFE SCIENCES PARTNERSHIP, 2018-2030 (USD MILLION)
TABLE 98. BRAZIL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 99. BRAZIL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STAGE OF DEVELOPMENT, 2018-2030 (USD MILLION)
TABLE 100. BRAZIL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY CLINICAL TRIALS ?, 2018-2030 (USD MILLION)
TABLE 101. BRAZIL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PRECLINICAL ?, 2018-2030 (USD MILLION)
TABLE 102. BRAZIL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BIOMARKER UTILIZATION, 2018-2030 (USD MILLION)
TABLE 103. BRAZIL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGULATORY STATUS, 2018-2030 (USD MILLION)
TABLE 104. BRAZIL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ASSOCIATED SYNDROMES, 2018-2030 (USD MILLION)
TABLE 105. BRAZIL TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY NEUROLOGICAL COMPLICATIONS ?, 2018-2030 (USD MILLION)
TABLE 106. CANADA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY TYPE OF TREATMENT, 2018-2030 (USD MILLION)
TABLE 107. CANADA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT DEMOGRAPHICS, 2018-2030 (USD MILLION)
TABLE 108. CANADA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT HEALTH STATUS, 2018-2030 (USD MILLION)
TABLE 109. CANADA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
TABLE 110. CANADA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 111. CANADA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIFE SCIENCES PARTNERSHIP, 2018-2030 (USD MILLION)
TABLE 112. CANADA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 113. CANADA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STAGE OF DEVELOPMENT, 2018-2030 (USD MILLION)
TABLE 114. CANADA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY CLINICAL TRIALS ?, 2018-2030 (USD MILLION)
TABLE 115. CANADA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PRECLINICAL ?, 2018-2030 (USD MILLION)
TABLE 116. CANADA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BIOMARKER UTILIZATION, 2018-2030 (USD MILLION)
TABLE 117. CANADA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGULATORY STATUS, 2018-2030 (USD MILLION)
TABLE 118. CANADA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ASSOCIATED SYNDROMES, 2018-2030 (USD MILLION)
TABLE 119. CANADA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY NEUROLOGICAL COMPLICATIONS ?, 2018-2030 (USD MILLION)
TABLE 120. MEXICO TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY TYPE OF TREATMENT, 2018-2030 (USD MILLION)
TABLE 121. MEXICO TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT DEMOGRAPHICS, 2018-2030 (USD MILLION)
TABLE 122. MEXICO TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT HEALTH STATUS, 2018-2030 (USD MILLION)
TABLE 123. MEXICO TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
TABLE 124. MEXICO TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 125. MEXICO TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIFE SCIENCES PARTNERSHIP, 2018-2030 (USD MILLION)
TABLE 126. MEXICO TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 127. MEXICO TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STAGE OF DEVELOPMENT, 2018-2030 (USD MILLION)
TABLE 128. MEXICO TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY CLINICAL TRIALS ?, 2018-2030 (USD MILLION)
TABLE 129. MEXICO TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PRECLINICAL ?, 2018-2030 (USD MILLION)
TABLE 130. MEXICO TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BIOMARKER UTILIZATION, 2018-2030 (USD MILLION)
TABLE 131. MEXICO TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGULATORY STATUS, 2018-2030 (USD MILLION)
TABLE 132. MEXICO TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ASSOCIATED SYNDROMES, 2018-2030 (USD MILLION)
TABLE 133. MEXICO TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY NEUROLOGICAL COMPLICATIONS ?, 2018-2030 (USD MILLION)
TABLE 134. UNITED STATES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY TYPE OF TREATMENT, 2018-2030 (USD MILLION)
TABLE 135. UNITED STATES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT DEMOGRAPHICS, 2018-2030 (USD MILLION)
TABLE 136. UNITED STATES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT HEALTH STATUS, 2018-2030 (USD MILLION)
TABLE 137. UNITED STATES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
TABLE 138. UNITED STATES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 139. UNITED STATES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIFE SCIENCES PARTNERSHIP, 2018-2030 (USD MILLION)
TABLE 140. UNITED STATES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 141. UNITED STATES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STAGE OF DEVELOPMENT, 2018-2030 (USD MILLION)
TABLE 142. UNITED STATES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY CLINICAL TRIALS ?, 2018-2030 (USD MILLION)
TABLE 143. UNITED STATES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PRECLINICAL ?, 2018-2030 (USD MILLION)
TABLE 144. UNITED STATES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BIOMARKER UTILIZATION, 2018-2030 (USD MILLION)
TABLE 145. UNITED STATES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGULATORY STATUS, 2018-2030 (USD MILLION)
TABLE 146. UNITED STATES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ASSOCIATED SYNDROMES, 2018-2030 (USD MILLION)
TABLE 147. UNITED STATES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY NEUROLOGICAL COMPLICATIONS ?, 2018-2030 (USD MILLION)
TABLE 148. UNITED STATES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STATE, 2018-2030 (USD MILLION)
TABLE 149. ASIA-PACIFIC TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY TYPE OF TREATMENT, 2018-2030 (USD MILLION)
TABLE 150. ASIA-PACIFIC TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT DEMOGRAPHICS, 2018-2030 (USD MILLION)
TABLE 151. ASIA-PACIFIC TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT HEALTH STATUS, 2018-2030 (USD MILLION)
TABLE 152. ASIA-PACIFIC TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
TABLE 153. ASIA-PACIFIC TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 154. ASIA-PACIFIC TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIFE SCIENCES PARTNERSHIP, 2018-2030 (USD MILLION)
TABLE 155. ASIA-PACIFIC TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 156. ASIA-PACIFIC TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STAGE OF DEVELOPMENT, 2018-2030 (USD MILLION)
TABLE 157. ASIA-PACIFIC TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY CLINICAL TRIALS ?, 2018-2030 (USD MILLION)
TABLE 158. ASIA-PACIFIC TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PRECLINICAL ?, 2018-2030 (USD MILLION)
TABLE 159. ASIA-PACIFIC TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BIOMARKER UTILIZATION, 2018-2030 (USD MILLION)
TABLE 160. ASIA-PACIFIC TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGULATORY STATUS, 2018-2030 (USD MILLION)
TABLE 161. ASIA-PACIFIC TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ASSOCIATED SYNDROMES, 2018-2030 (USD MILLION)
TABLE 162. ASIA-PACIFIC TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY NEUROLOGICAL COMPLICATIONS ?, 2018-2030 (USD MILLION)
TABLE 163. ASIA-PACIFIC TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
TABLE 164. AUSTRALIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY TYPE OF TREATMENT, 2018-2030 (USD MILLION)
TABLE 165. AUSTRALIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT DEMOGRAPHICS, 2018-2030 (USD MILLION)
TABLE 166. AUSTRALIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT HEALTH STATUS, 2018-2030 (USD MILLION)
TABLE 167. AUSTRALIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
TABLE 168. AUSTRALIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 169. AUSTRALIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIFE SCIENCES PARTNERSHIP, 2018-2030 (USD MILLION)
TABLE 170. AUSTRALIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 171. AUSTRALIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STAGE OF DEVELOPMENT, 2018-2030 (USD MILLION)
TABLE 172. AUSTRALIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY CLINICAL TRIALS ?, 2018-2030 (USD MILLION)
TABLE 173. AUSTRALIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PRECLINICAL ?, 2018-2030 (USD MILLION)
TABLE 174. AUSTRALIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BIOMARKER UTILIZATION, 2018-2030 (USD MILLION)
TABLE 175. AUSTRALIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGULATORY STATUS, 2018-2030 (USD MILLION)
TABLE 176. AUSTRALIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ASSOCIATED SYNDROMES, 2018-2030 (USD MILLION)
TABLE 177. AUSTRALIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY NEUROLOGICAL COMPLICATIONS ?, 2018-2030 (USD MILLION)
TABLE 178. CHINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY TYPE OF TREATMENT, 2018-2030 (USD MILLION)
TABLE 179. CHINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT DEMOGRAPHICS, 2018-2030 (USD MILLION)
TABLE 180. CHINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT HEALTH STATUS, 2018-2030 (USD MILLION)
TABLE 181. CHINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
TABLE 182. CHINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 183. CHINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIFE SCIENCES PARTNERSHIP, 2018-2030 (USD MILLION)
TABLE 184. CHINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 185. CHINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STAGE OF DEVELOPMENT, 2018-2030 (USD MILLION)
TABLE 186. CHINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY CLINICAL TRIALS ?, 2018-2030 (USD MILLION)
TABLE 187. CHINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PRECLINICAL ?, 2018-2030 (USD MILLION)
TABLE 188. CHINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BIOMARKER UTILIZATION, 2018-2030 (USD MILLION)
TABLE 189. CHINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGULATORY STATUS, 2018-2030 (USD MILLION)
TABLE 190. CHINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ASSOCIATED SYNDROMES, 2018-2030 (USD MILLION)
TABLE 191. CHINA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY NEUROLOGICAL COMPLICATIONS ?, 2018-2030 (USD MILLION)
TABLE 192. INDIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY TYPE OF TREATMENT, 2018-2030 (USD MILLION)
TABLE 193. INDIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT DEMOGRAPHICS, 2018-2030 (USD MILLION)
TABLE 194. INDIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT HEALTH STATUS, 2018-2030 (USD MILLION)
TABLE 195. INDIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
TABLE 196. INDIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 197. INDIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIFE SCIENCES PARTNERSHIP, 2018-2030 (USD MILLION)
TABLE 198. INDIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 199. INDIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STAGE OF DEVELOPMENT, 2018-2030 (USD MILLION)
TABLE 200. INDIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY CLINICAL TRIALS ?, 2018-2030 (USD MILLION)
TABLE 201. INDIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PRECLINICAL ?, 2018-2030 (USD MILLION)
TABLE 202. INDIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BIOMARKER UTILIZATION, 2018-2030 (USD MILLION)
TABLE 203. INDIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGULATORY STATUS, 2018-2030 (USD MILLION)
TABLE 204. INDIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ASSOCIATED SYNDROMES, 2018-2030 (USD MILLION)
TABLE 205. INDIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY NEUROLOGICAL COMPLICATIONS ?, 2018-2030 (USD MILLION)
TABLE 206. INDONESIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY TYPE OF TREATMENT, 2018-2030 (USD MILLION)
TABLE 207. INDONESIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT DEMOGRAPHICS, 2018-2030 (USD MILLION)
TABLE 208. INDONESIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT HEALTH STATUS, 2018-2030 (USD MILLION)
TABLE 209. INDONESIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
TABLE 210. INDONESIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 211. INDONESIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIFE SCIENCES PARTNERSHIP, 2018-2030 (USD MILLION)
TABLE 212. INDONESIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 213. INDONESIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STAGE OF DEVELOPMENT, 2018-2030 (USD MILLION)
TABLE 214. INDONESIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY CLINICAL TRIALS ?, 2018-2030 (USD MILLION)
TABLE 215. INDONESIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PRECLINICAL ?, 2018-2030 (USD MILLION)
TABLE 216. INDONESIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BIOMARKER UTILIZATION, 2018-2030 (USD MILLION)
TABLE 217. INDONESIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGULATORY STATUS, 2018-2030 (USD MILLION)
TABLE 218. INDONESIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ASSOCIATED SYNDROMES, 2018-2030 (USD MILLION)
TABLE 219. INDONESIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY NEUROLOGICAL COMPLICATIONS ?, 2018-2030 (USD MILLION)
TABLE 220. JAPAN TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY TYPE OF TREATMENT, 2018-2030 (USD MILLION)
TABLE 221. JAPAN TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT DEMOGRAPHICS, 2018-2030 (USD MILLION)
TABLE 222. JAPAN TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT HEALTH STATUS, 2018-2030 (USD MILLION)
TABLE 223. JAPAN TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
TABLE 224. JAPAN TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 225. JAPAN TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIFE SCIENCES PARTNERSHIP, 2018-2030 (USD MILLION)
TABLE 226. JAPAN TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 227. JAPAN TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STAGE OF DEVELOPMENT, 2018-2030 (USD MILLION)
TABLE 228. JAPAN TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY CLINICAL TRIALS ?, 2018-2030 (USD MILLION)
TABLE 229. JAPAN TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PRECLINICAL ?, 2018-2030 (USD MILLION)
TABLE 230. JAPAN TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BIOMARKER UTILIZATION, 2018-2030 (USD MILLION)
TABLE 231. JAPAN TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGULATORY STATUS, 2018-2030 (USD MILLION)
TABLE 232. JAPAN TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ASSOCIATED SYNDROMES, 2018-2030 (USD MILLION)
TABLE 233. JAPAN TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY NEUROLOGICAL COMPLICATIONS ?, 2018-2030 (USD MILLION)
TABLE 234. MALAYSIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY TYPE OF TREATMENT, 2018-2030 (USD MILLION)
TABLE 235. MALAYSIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT DEMOGRAPHICS, 2018-2030 (USD MILLION)
TABLE 236. MALAYSIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT HEALTH STATUS, 2018-2030 (USD MILLION)
TABLE 237. MALAYSIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
TABLE 238. MALAYSIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 239. MALAYSIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIFE SCIENCES PARTNERSHIP, 2018-2030 (USD MILLION)
TABLE 240. MALAYSIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 241. MALAYSIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STAGE OF DEVELOPMENT, 2018-2030 (USD MILLION)
TABLE 242. MALAYSIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY CLINICAL TRIALS ?, 2018-2030 (USD MILLION)
TABLE 243. MALAYSIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PRECLINICAL ?, 2018-2030 (USD MILLION)
TABLE 244. MALAYSIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BIOMARKER UTILIZATION, 2018-2030 (USD MILLION)
TABLE 245. MALAYSIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGULATORY STATUS, 2018-2030 (USD MILLION)
TABLE 246. MALAYSIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ASSOCIATED SYNDROMES, 2018-2030 (USD MILLION)
TABLE 247. MALAYSIA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY NEUROLOGICAL COMPLICATIONS ?, 2018-2030 (USD MILLION)
TABLE 248. PHILIPPINES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY TYPE OF TREATMENT, 2018-2030 (USD MILLION)
TABLE 249. PHILIPPINES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT DEMOGRAPHICS, 2018-2030 (USD MILLION)
TABLE 250. PHILIPPINES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT HEALTH STATUS, 2018-2030 (USD MILLION)
TABLE 251. PHILIPPINES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
TABLE 252. PHILIPPINES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 253. PHILIPPINES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIFE SCIENCES PARTNERSHIP, 2018-2030 (USD MILLION)
TABLE 254. PHILIPPINES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 255. PHILIPPINES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STAGE OF DEVELOPMENT, 2018-2030 (USD MILLION)
TABLE 256. PHILIPPINES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY CLINICAL TRIALS ?, 2018-2030 (USD MILLION)
TABLE 257. PHILIPPINES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PRECLINICAL ?, 2018-2030 (USD MILLION)
TABLE 258. PHILIPPINES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BIOMARKER UTILIZATION, 2018-2030 (USD MILLION)
TABLE 259. PHILIPPINES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGULATORY STATUS, 2018-2030 (USD MILLION)
TABLE 260. PHILIPPINES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ASSOCIATED SYNDROMES, 2018-2030 (USD MILLION)
TABLE 261. PHILIPPINES TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY NEUROLOGICAL COMPLICATIONS ?, 2018-2030 (USD MILLION)
TABLE 262. SINGAPORE TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY TYPE OF TREATMENT, 2018-2030 (USD MILLION)
TABLE 263. SINGAPORE TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT DEMOGRAPHICS, 2018-2030 (USD MILLION)
TABLE 264. SINGAPORE TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT HEALTH STATUS, 2018-2030 (USD MILLION)
TABLE 265. SINGAPORE TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
TABLE 266. SINGAPORE TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 267. SINGAPORE TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIFE SCIENCES PARTNERSHIP, 2018-2030 (USD MILLION)
TABLE 268. SINGAPORE TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 269. SINGAPORE TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STAGE OF DEVELOPMENT, 2018-2030 (USD MILLION)
TABLE 270. SINGAPORE TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY CLINICAL TRIALS ?, 2018-2030 (USD MILLION)
TABLE 271. SINGAPORE TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PRECLINICAL ?, 2018-2030 (USD MILLION)
TABLE 272. SINGAPORE TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BIOMARKER UTILIZATION, 2018-2030 (USD MILLION)
TABLE 273. SINGAPORE TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY REGULATORY STATUS, 2018-2030 (USD MILLION)
TABLE 274. SINGAPORE TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY ASSOCIATED SYNDROMES, 2018-2030 (USD MILLION)
TABLE 275. SINGAPORE TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY NEUROLOGICAL COMPLICATIONS ?, 2018-2030 (USD MILLION)
TABLE 276. SOUTH KOREA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY TYPE OF TREATMENT, 2018-2030 (USD MILLION)
TABLE 277. SOUTH KOREA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT DEMOGRAPHICS, 2018-2030 (USD MILLION)
TABLE 278. SOUTH KOREA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PATIENT HEALTH STATUS, 2018-2030 (USD MILLION)
TABLE 279. SOUTH KOREA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY END-USER, 2018-2030 (USD MILLION)
TABLE 280. SOUTH KOREA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY MODE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 281. SOUTH KOREA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY LIFE SCIENCES PARTNERSHIP, 2018-2030 (USD MILLION)
TABLE 282. SOUTH KOREA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 283. SOUTH KOREA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY STAGE OF DEVELOPMENT, 2018-2030 (USD MILLION)
TABLE 284. SOUTH KOREA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY CLINICAL TRIALS ?, 2018-2030 (USD MILLION)
TABLE 285. SOUTH KOREA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY PRECLINICAL ?, 2018-2030 (USD MILLION)
TABLE 286. SOUTH KOREA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY BIOMARKER UTILIZATION, 2018-2030 (USD MILLION)
TABLE 287. SOUTH KOREA TYPE 1 GAUCHER DISEASE TREATMENT MARKET SIZE, BY R

Companies Mentioned

  • Actelion Pharmaceuticals Ltd. (acquired by Johnson & Johnson)
  • Amicus Therapeutics, Inc.
  • BioMarin Pharmaceutical Inc.
  • Greenovation Biotech GmbH
  • ISU ABXIS Co., Ltd.
  • JCR Pharmaceuticals Co., Ltd.
  • M6P Therapeutics
  • Pfizer Inc.
  • Protalix BioTherapeutics, Inc.
  • Sanofi S.A.
  • Shire plc (acquired by Takeda)
  • Takeda Pharmaceutical Company Limited
  • Ultragenyx Pharmaceutical Inc.

Methodology

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