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Batten Disease Market by Product Type, Clinical Form, Route Of Administration, Distribution Channel, End User - Global Forecast to 2030

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    Report

  • 188 Pages
  • May 2025
  • Region: Global
  • 360iResearch™
  • ID: 6083644
UP TO OFF until Dec 31st 2025
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The Batten Disease Market grew from USD 57.61 million in 2024 to USD 60.65 million in 2025. It is expected to continue growing at a CAGR of 5.23%, reaching USD 78.23 million by 2030.

Navigating the Complex World of Batten Disease

Batten disease represents a formidable challenge in pediatric neurology, marked by progressive neurodegeneration and a devastating impact on young lives and their families. Despite advances in our understanding of lysosomal storage disorders, the absence of definitive cures underscores the urgent need for comprehensive research into emerging therapies, market dynamics, and policy influences. This executive summary distills critical developments shaping the Batten disease arena, offering decision-makers a clear line of sight into the innovations, disruptions, and strategic imperatives defining this specialized field.

Through a structured exploration of transformative scientific breakthroughs, regulatory shifts, tariff implications, segmentation analyses, regional nuances, and competitive movements, this overview equips stakeholders with the knowledge required to anticipate market evolution and optimize resource allocation. By synthesizing diverse data streams and expert perspectives, we illuminate the pathways for investment, collaboration, and policy advocacy that are essential for accelerating therapeutic progress and improving patient outcomes.

Pioneering Advances Reshaping Batten Disease Treatment

In recent years, the Batten disease landscape has experienced a profound metamorphosis as gene therapies have transitioned from experimental concepts to advanced clinical candidates. AAV-based and lentiviral vector platforms now promise targeted genetic correction, while innovations in oligonucleotide design and substrate reduction strategies are refining approaches to slow disease progression. Concurrently, regulators have demonstrated increased flexibility, issuing guidance that accommodates adaptive trial designs and expedited review pathways.

This synergy between biotechnological ingenuity and progressive policy frameworks has spurred strategic alliances among biotech firms, academic institutions, and patient advocacy groups. As research consortia pool resources and share genomic databases, the pace of discovery accelerates. Transitional milestones-such as first-in-human gene therapy dosing and real-world evidence integration-signal a shift toward personalized, disease-modifying interventions, moving beyond the reliance on symptomatic therapies that have traditionally dominated care.

Assessing the Ripple Effects of 2025 Tariff Policy

The imposition of new tariff measures in 2025 has generated tangible ramifications across the Batten disease supply chain, particularly for imported biologics and specialized reagents. Increased duties on raw materials have elevated production costs, compelling manufacturers to reassess supplier networks and localize critical processes. As a result, research and development budgets face compression, with companies prioritizing high-impact projects to offset tariff-induced expenses.

Moreover, downstream pricing negotiations have become more complex, as payers push back against cost escalation. This dynamic compels industry leaders to devise creative contracting solutions, such as outcome-based agreements and tiered pricing, to maintain patient access. Despite these headwinds, some stakeholders are exploring dual-sourcing strategies and onshore manufacturing partnerships to mitigate future trade disruptions. In sum, the 2025 tariff landscape demands adaptive resilience and proactive risk management across the Batten disease ecosystem.

Decoding Market Dynamics Through Comprehensive Segmentation

A comprehensive segmentation lens reveals multiple dimensions driving the Batten disease market’s complexity. Product innovations span enzyme replacement therapies delivered via intrathecal and intravenous administrations, gene therapies harnessing AAV and lentiviral vectors, substrate reduction approaches built on oligonucleotides and small molecules, and a spectrum of symptomatic treatments encompassing antiepileptics, pain management modalities, and rehabilitative physical therapies. Each subsegment reflects distinct development pathways, regulatory requirements, and cost structures, necessitating tailored strategies for investors and developers.

Clinical form distinctions-from adult-onset to juvenile, infantile, and late infantile presentations-further complicate therapeutic targeting and reimbursement frameworks. While adult cohorts may tolerate oral regimens for symptom management, infantile and late infantile cases demand aggressive, often invasive delivery methods to slow rapid neurodegeneration. Similarly, route of administration considerations influence patient adherence and caregiver burden, as intrathecal infusions offer direct central nervous system access at the cost of procedural risk, whereas oral formulations prioritize convenience.

Distribution networks also play a pivotal role, with hospital pharmacies, retail outlets, and specialty pharmacies each serving unique logistical and clinical needs. Home care providers, hospitals, and specialized clinics form the end-user landscape, highlighting the necessity for coordinated care models and robust patient support programs. Understanding these interlocking segments is essential for stakeholders seeking to align product design, commercialization tactics, and service offerings with real-world demands.

Unearthing Regional Trends Across Global Markets

Regional market behaviors reflect heterogeneous healthcare infrastructures, policy environments, and patient demographics. In the Americas, robust funding mechanisms and well-established reimbursement pathways have accelerated the adoption of novel therapies, driving collaborative research hubs and expanded clinical trial networks. The ability to leverage real-world evidence and data analytics further solidifies North America as a leading innovation engine.

Europe, the Middle East and Africa display a tapestry of market maturity levels, where regulatory harmonization efforts coexist with payer fragmentation. Countries with centralized health technology assessment agencies establish rigorous value frameworks, while emerging economies balance affordability pressures with the desire to cultivate local biotech sectors. These dynamics encourage adaptive pricing models and public-private partnerships aimed at sustaining access across diverse populations.

Asia-Pacific encompasses dynamic growth influenced by government initiatives to bolster rare disease research and enhance domestic manufacturing capabilities. Patient advocacy is ascending, fostering awareness campaigns and stakeholder coalitions that promote policy reforms. Still, economic variability and regulatory divergence necessitate nimble market entry strategies and nuanced engagement with regional healthcare authorities.

Profiling Leading Innovators in Batten Disease Therapies

Leading innovators are defining the competitive contours of Batten disease therapeutic development. Companies with advanced enzyme replacement platforms continue to invest in refining delivery systems to enhance central nervous system penetration, while pioneers in gene therapy vie for first regulatory approvals, leveraging strategic partnerships to expand manufacturing scale and geographic reach. Asset-centric players are diversifying through acquisitions of complementary assets, creating integrated portfolios that span early-stage research to late-stage clinical development.

Collaboration patterns underscore the value of cross-sector synergies, as pharmaceutical giants partner with niche biotech firms to access cutting-edge vector technologies. Meanwhile, patient-centric organizations contribute to clinical trial design and post-market surveillance, demonstrating a shift toward co-creation of therapeutic solutions. Observing these strategic maneuvers provides clear indicators of where capital is flowing, which modalities are gaining traction, and how competitive positioning is evolving in response to scientific breakthroughs and market access pressures.

Strategic Imperatives for Next-Level Industry Impact

Industry leaders must prioritize investment in scalable gene therapy platforms, ensuring readiness to transition from pilot-scale production to commercial volumes. Establishing flexible manufacturing networks that integrate onshore and offshore sites will enhance supply chain resilience and mitigate tariff-related disruptions. Concurrently, embracing real-world data collection will strengthen value propositions for payers, enabling outcome-based payment models that align reimbursement with therapeutic efficacy.

Building robust patient engagement programs is equally essential, as proactive education and support initiatives foster adherence and reduce care fragmentation. Engaging with health technology assessment bodies early in development can streamline evidence generation and accelerate favorable coverage decisions. Finally, cultivating strategic alliances-whether through co-development agreements, licensing partnerships, or consortium memberships-will enable companies to share risk, pool expertise, and amplify impact across the Batten disease ecosystem.

Rigorous Methodology Underpinning Our Insights

This analysis integrates a blend of primary and secondary research methodologies. Extensive literature reviews and data mining of peer-reviewed journals, regulatory filings, and policy documents established foundational insights. Complementing this desk research, in-depth interviews with clinical experts, payers, supply chain specialists, and patient advocacy leaders provided qualitative validation and nuanced perspectives on evolving trends.

Quantitative data were triangulated across multiple sources, ensuring consistency in segmentation, regional analysis, and tariff impact assessments. A proprietary framework guided the evaluation of company strategies, therapeutic modalities, and regulatory developments. Rigorous peer review and iterative validation exercises with external stakeholders bolstered the credibility of findings, delivering a robust and actionable executive summary for decision-makers.

Synthesizing Key Takeaways to Propel Future Progress

In synthesizing the critical elements of Batten disease research, it becomes evident that therapeutic innovation, policy dynamics, and strategic execution are inextricably linked. The advent of gene and substrate reduction therapies heralds a new era of targeted interventions, while evolving tariff landscapes underscore the necessity for resilient supply chains and agile pricing models. Segmentation and regional analyses illuminate the diverse needs of patient populations and healthcare systems, guiding optimized market entry and commercialization tactics.

Moving from analysis to action, industry stakeholders are poised to harness collaborative networks, leverage real-world evidence, and refine operational frameworks to accelerate progress. The insights presented herein offer a roadmap for aligning scientific promise with market realities, ensuring that breakthroughs translate into meaningful improvements for individuals living with Batten disease.

Market Segmentation & Coverage

This research report categorizes to forecast the revenues and analyze trends in each of the following sub-segmentations:
  • Product Type
    • Enzyme Replacement Therapy
      • Intrathecal
      • Intravenous
    • Gene Therapy
      • AAV-Based
      • Lentiviral-Based
    • Substrate Reduction Therapy
      • Oligonucleotides
      • Small Molecules
    • Symptomatic Therapy
      • Antiepileptics
      • Pain Management
      • Physical Therapy
  • Clinical Form
    • Adult
    • Infantile
    • Juvenile
    • Late Infantile
  • Route Of Administration
    • Intrathecal
    • Intravenous
    • Oral
  • Distribution Channel
    • Hospital Pharmacies
    • Retail Pharmacies
    • Specialty Pharmacies
  • End User
    • Home Care Providers
    • Hospitals
    • Specialized Clinics
This research report categorizes to forecast the revenues and analyze trends in each of the following sub-regions:
  • Americas
    • United States
      • California
      • Texas
      • New York
      • Florida
      • Illinois
      • Pennsylvania
      • Ohio
    • Canada
    • Mexico
    • Brazil
    • Argentina
  • Europe, Middle East & Africa
    • United Kingdom
    • Germany
    • France
    • Russia
    • Italy
    • Spain
    • United Arab Emirates
    • Saudi Arabia
    • South Africa
    • Denmark
    • Netherlands
    • Qatar
    • Finland
    • Sweden
    • Nigeria
    • Egypt
    • Turkey
    • Israel
    • Norway
    • Poland
    • Switzerland
  • Asia-Pacific
    • China
    • India
    • Japan
    • Australia
    • South Korea
    • Indonesia
    • Thailand
    • Philippines
    • Malaysia
    • Singapore
    • Vietnam
    • Taiwan
This research report categorizes to delves into recent significant developments and analyze trends in each of the following companies:
  • BioMarin Pharmaceutical Inc.
  • Astellas Pharma Inc.
  • Spark Therapeutics, Inc.
  • Regenxbio Inc.
  • Lysogene SA
  • uniQure NV
  • Ultragenyx Pharmaceutical Inc.
  • Orchard Therapeutics Ltd.
  • Abeona Therapeutics, Inc.
  • Neurogene, Inc.

Table of Contents

1. Preface
1.1. Objectives of the Study
1.2. Market Segmentation & Coverage
1.3. Years Considered for the Study
1.4. Currency & Pricing
1.5. Language
1.6. Stakeholders
2. Research Methodology
2.1. Define: Research Objective
2.2. Determine: Research Design
2.3. Prepare: Research Instrument
2.4. Collect: Data Source
2.5. Analyze: Data Interpretation
2.6. Formulate: Data Verification
2.7. Publish: Research Report
2.8. Repeat: Report Update
3. Executive Summary
4. Market Overview
4.1. Introduction
4.2. Market Sizing & Forecasting
5. Market Dynamics
6. Market Insights
6.1. Porter’s Five Forces Analysis
6.2. PESTLE Analysis
7. Cumulative Impact of United States Tariffs 2025
8. Batten Disease Market, by Product Type
8.1. Introduction
8.2. Enzyme Replacement Therapy
8.2.1. Intrathecal
8.2.2. Intravenous
8.3. Gene Therapy
8.3.1. AAV-Based
8.3.2. Lentiviral-Based
8.4. Substrate Reduction Therapy
8.4.1. Oligonucleotides
8.4.2. Small Molecules
8.5. Symptomatic Therapy
8.5.1. Antiepileptics
8.5.2. Pain Management
8.5.3. Physical Therapy
9. Batten Disease Market, by Clinical Form
9.1. Introduction
9.2. Adult
9.3. Infantile
9.4. Juvenile
9.5. Late Infantile
10. Batten Disease Market, by Route Of Administration
10.1. Introduction
10.2. Intrathecal
10.3. Intravenous
10.4. Oral
11. Batten Disease Market, by Distribution Channel
11.1. Introduction
11.2. Hospital Pharmacies
11.3. Retail Pharmacies
11.4. Specialty Pharmacies
12. Batten Disease Market, by End User
12.1. Introduction
12.2. Home Care Providers
12.3. Hospitals
12.4. Specialized Clinics
13. Americas Batten Disease Market
13.1. Introduction
13.2. United States
13.3. Canada
13.4. Mexico
13.5. Brazil
13.6. Argentina
14. Europe, Middle East & Africa Batten Disease Market
14.1. Introduction
14.2. United Kingdom
14.3. Germany
14.4. France
14.5. Russia
14.6. Italy
14.7. Spain
14.8. United Arab Emirates
14.9. Saudi Arabia
14.10. South Africa
14.11. Denmark
14.12. Netherlands
14.13. Qatar
14.14. Finland
14.15. Sweden
14.16. Nigeria
14.17. Egypt
14.18. Turkey
14.19. Israel
14.20. Norway
14.21. Poland
14.22. Switzerland
15. Asia-Pacific Batten Disease Market
15.1. Introduction
15.2. China
15.3. India
15.4. Japan
15.5. Australia
15.6. South Korea
15.7. Indonesia
15.8. Thailand
15.9. Philippines
15.10. Malaysia
15.11. Singapore
15.12. Vietnam
15.13. Taiwan
16. Competitive Landscape
16.1. Market Share Analysis, 2024
16.2. FPNV Positioning Matrix, 2024
16.3. Competitive Analysis
16.3.1. BioMarin Pharmaceutical Inc.
16.3.2. Astellas Pharma Inc.
16.3.3. Spark Therapeutics, Inc.
16.3.4. Regenxbio Inc.
16.3.5. Lysogene SA
16.3.6. uniQure NV
16.3.7. Ultragenyx Pharmaceutical Inc.
16.3.8. Orchard Therapeutics Ltd.
16.3.9. Abeona Therapeutics, Inc.
16.3.10. Neurogene, Inc.
17. ResearchAI
18. ResearchStatistics
19. ResearchContacts
20. ResearchArticles
21. Appendix
List of Figures
FIGURE 1. BATTEN DISEASE MARKET MULTI-CURRENCY
FIGURE 2. BATTEN DISEASE MARKET MULTI-LANGUAGE
FIGURE 3. BATTEN DISEASE MARKET RESEARCH PROCESS
FIGURE 4. GLOBAL BATTEN DISEASE MARKET SIZE, 2018-2030 (USD MILLION)
FIGURE 5. GLOBAL BATTEN DISEASE MARKET SIZE, BY REGION, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 6. GLOBAL BATTEN DISEASE MARKET SIZE, BY COUNTRY, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 7. GLOBAL BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2024 VS 2030 (%)
FIGURE 8. GLOBAL BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 9. GLOBAL BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2024 VS 2030 (%)
FIGURE 10. GLOBAL BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 11. GLOBAL BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2024 VS 2030 (%)
FIGURE 12. GLOBAL BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 13. GLOBAL BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2024 VS 2030 (%)
FIGURE 14. GLOBAL BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 15. GLOBAL BATTEN DISEASE MARKET SIZE, BY END USER, 2024 VS 2030 (%)
FIGURE 16. GLOBAL BATTEN DISEASE MARKET SIZE, BY END USER, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 17. AMERICAS BATTEN DISEASE MARKET SIZE, BY COUNTRY, 2024 VS 2030 (%)
FIGURE 18. AMERICAS BATTEN DISEASE MARKET SIZE, BY COUNTRY, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 19. UNITED STATES BATTEN DISEASE MARKET SIZE, BY STATE, 2024 VS 2030 (%)
FIGURE 20. UNITED STATES BATTEN DISEASE MARKET SIZE, BY STATE, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 21. EUROPE, MIDDLE EAST & AFRICA BATTEN DISEASE MARKET SIZE, BY COUNTRY, 2024 VS 2030 (%)
FIGURE 22. EUROPE, MIDDLE EAST & AFRICA BATTEN DISEASE MARKET SIZE, BY COUNTRY, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 23. ASIA-PACIFIC BATTEN DISEASE MARKET SIZE, BY COUNTRY, 2024 VS 2030 (%)
FIGURE 24. ASIA-PACIFIC BATTEN DISEASE MARKET SIZE, BY COUNTRY, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 25. BATTEN DISEASE MARKET SHARE, BY KEY PLAYER, 2024
FIGURE 26. BATTEN DISEASE MARKET, FPNV POSITIONING MATRIX, 2024
List of Tables
TABLE 1. BATTEN DISEASE MARKET SEGMENTATION & COVERAGE
TABLE 2. UNITED STATES DOLLAR EXCHANGE RATE, 2018-2024
TABLE 3. GLOBAL BATTEN DISEASE MARKET SIZE, 2018-2030 (USD MILLION)
TABLE 4. GLOBAL BATTEN DISEASE MARKET SIZE, BY REGION, 2018-2030 (USD MILLION)
TABLE 5. GLOBAL BATTEN DISEASE MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
TABLE 6. GLOBAL BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 7. GLOBAL BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, BY REGION, 2018-2030 (USD MILLION)
TABLE 8. GLOBAL BATTEN DISEASE MARKET SIZE, BY INTRATHECAL, BY REGION, 2018-2030 (USD MILLION)
TABLE 9. GLOBAL BATTEN DISEASE MARKET SIZE, BY INTRAVENOUS, BY REGION, 2018-2030 (USD MILLION)
TABLE 10. GLOBAL BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 11. GLOBAL BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, BY REGION, 2018-2030 (USD MILLION)
TABLE 12. GLOBAL BATTEN DISEASE MARKET SIZE, BY AAV-BASED, BY REGION, 2018-2030 (USD MILLION)
TABLE 13. GLOBAL BATTEN DISEASE MARKET SIZE, BY LENTIVIRAL-BASED, BY REGION, 2018-2030 (USD MILLION)
TABLE 14. GLOBAL BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 15. GLOBAL BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, BY REGION, 2018-2030 (USD MILLION)
TABLE 16. GLOBAL BATTEN DISEASE MARKET SIZE, BY OLIGONUCLEOTIDES, BY REGION, 2018-2030 (USD MILLION)
TABLE 17. GLOBAL BATTEN DISEASE MARKET SIZE, BY SMALL MOLECULES, BY REGION, 2018-2030 (USD MILLION)
TABLE 18. GLOBAL BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 19. GLOBAL BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, BY REGION, 2018-2030 (USD MILLION)
TABLE 20. GLOBAL BATTEN DISEASE MARKET SIZE, BY ANTIEPILEPTICS, BY REGION, 2018-2030 (USD MILLION)
TABLE 21. GLOBAL BATTEN DISEASE MARKET SIZE, BY PAIN MANAGEMENT, BY REGION, 2018-2030 (USD MILLION)
TABLE 22. GLOBAL BATTEN DISEASE MARKET SIZE, BY PHYSICAL THERAPY, BY REGION, 2018-2030 (USD MILLION)
TABLE 23. GLOBAL BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 24. GLOBAL BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 25. GLOBAL BATTEN DISEASE MARKET SIZE, BY ADULT, BY REGION, 2018-2030 (USD MILLION)
TABLE 26. GLOBAL BATTEN DISEASE MARKET SIZE, BY INFANTILE, BY REGION, 2018-2030 (USD MILLION)
TABLE 27. GLOBAL BATTEN DISEASE MARKET SIZE, BY JUVENILE, BY REGION, 2018-2030 (USD MILLION)
TABLE 28. GLOBAL BATTEN DISEASE MARKET SIZE, BY LATE INFANTILE, BY REGION, 2018-2030 (USD MILLION)
TABLE 29. GLOBAL BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 30. GLOBAL BATTEN DISEASE MARKET SIZE, BY INTRATHECAL, BY REGION, 2018-2030 (USD MILLION)
TABLE 31. GLOBAL BATTEN DISEASE MARKET SIZE, BY INTRAVENOUS, BY REGION, 2018-2030 (USD MILLION)
TABLE 32. GLOBAL BATTEN DISEASE MARKET SIZE, BY ORAL, BY REGION, 2018-2030 (USD MILLION)
TABLE 33. GLOBAL BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 34. GLOBAL BATTEN DISEASE MARKET SIZE, BY HOSPITAL PHARMACIES, BY REGION, 2018-2030 (USD MILLION)
TABLE 35. GLOBAL BATTEN DISEASE MARKET SIZE, BY RETAIL PHARMACIES, BY REGION, 2018-2030 (USD MILLION)
TABLE 36. GLOBAL BATTEN DISEASE MARKET SIZE, BY SPECIALTY PHARMACIES, BY REGION, 2018-2030 (USD MILLION)
TABLE 37. GLOBAL BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 38. GLOBAL BATTEN DISEASE MARKET SIZE, BY HOME CARE PROVIDERS, BY REGION, 2018-2030 (USD MILLION)
TABLE 39. GLOBAL BATTEN DISEASE MARKET SIZE, BY HOSPITALS, BY REGION, 2018-2030 (USD MILLION)
TABLE 40. GLOBAL BATTEN DISEASE MARKET SIZE, BY SPECIALIZED CLINICS, BY REGION, 2018-2030 (USD MILLION)
TABLE 41. AMERICAS BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 42. AMERICAS BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 43. AMERICAS BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 44. AMERICAS BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 45. AMERICAS BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 46. AMERICAS BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 47. AMERICAS BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 48. AMERICAS BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 49. AMERICAS BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 50. AMERICAS BATTEN DISEASE MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
TABLE 51. UNITED STATES BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 52. UNITED STATES BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 53. UNITED STATES BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 54. UNITED STATES BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 55. UNITED STATES BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 56. UNITED STATES BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 57. UNITED STATES BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 58. UNITED STATES BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 59. UNITED STATES BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 60. UNITED STATES BATTEN DISEASE MARKET SIZE, BY STATE, 2018-2030 (USD MILLION)
TABLE 61. CANADA BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 62. CANADA BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 63. CANADA BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 64. CANADA BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 65. CANADA BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 66. CANADA BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 67. CANADA BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 68. CANADA BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 69. CANADA BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 70. MEXICO BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 71. MEXICO BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 72. MEXICO BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 73. MEXICO BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 74. MEXICO BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 75. MEXICO BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 76. MEXICO BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 77. MEXICO BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 78. MEXICO BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 79. BRAZIL BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 80. BRAZIL BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 81. BRAZIL BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 82. BRAZIL BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 83. BRAZIL BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 84. BRAZIL BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 85. BRAZIL BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 86. BRAZIL BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 87. BRAZIL BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 88. ARGENTINA BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 89. ARGENTINA BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 90. ARGENTINA BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 91. ARGENTINA BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 92. ARGENTINA BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 93. ARGENTINA BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 94. ARGENTINA BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 95. ARGENTINA BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 96. ARGENTINA BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 97. EUROPE, MIDDLE EAST & AFRICA BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 98. EUROPE, MIDDLE EAST & AFRICA BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 99. EUROPE, MIDDLE EAST & AFRICA BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 100. EUROPE, MIDDLE EAST & AFRICA BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 101. EUROPE, MIDDLE EAST & AFRICA BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 102. EUROPE, MIDDLE EAST & AFRICA BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 103. EUROPE, MIDDLE EAST & AFRICA BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 104. EUROPE, MIDDLE EAST & AFRICA BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 105. EUROPE, MIDDLE EAST & AFRICA BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 106. EUROPE, MIDDLE EAST & AFRICA BATTEN DISEASE MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
TABLE 107. UNITED KINGDOM BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 108. UNITED KINGDOM BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 109. UNITED KINGDOM BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 110. UNITED KINGDOM BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 111. UNITED KINGDOM BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 112. UNITED KINGDOM BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 113. UNITED KINGDOM BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 114. UNITED KINGDOM BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 115. UNITED KINGDOM BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 116. GERMANY BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 117. GERMANY BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 118. GERMANY BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 119. GERMANY BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 120. GERMANY BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 121. GERMANY BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 122. GERMANY BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 123. GERMANY BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 124. GERMANY BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 125. FRANCE BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 126. FRANCE BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 127. FRANCE BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 128. FRANCE BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 129. FRANCE BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 130. FRANCE BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 131. FRANCE BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 132. FRANCE BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 133. FRANCE BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 134. RUSSIA BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 135. RUSSIA BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 136. RUSSIA BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 137. RUSSIA BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 138. RUSSIA BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 139. RUSSIA BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 140. RUSSIA BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 141. RUSSIA BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 142. RUSSIA BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 143. ITALY BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 144. ITALY BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 145. ITALY BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 146. ITALY BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 147. ITALY BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 148. ITALY BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 149. ITALY BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 150. ITALY BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 151. ITALY BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 152. SPAIN BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 153. SPAIN BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 154. SPAIN BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 155. SPAIN BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 156. SPAIN BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 157. SPAIN BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 158. SPAIN BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 159. SPAIN BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 160. SPAIN BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 161. UNITED ARAB EMIRATES BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 162. UNITED ARAB EMIRATES BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 163. UNITED ARAB EMIRATES BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 164. UNITED ARAB EMIRATES BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 165. UNITED ARAB EMIRATES BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 166. UNITED ARAB EMIRATES BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 167. UNITED ARAB EMIRATES BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 168. UNITED ARAB EMIRATES BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 169. UNITED ARAB EMIRATES BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 170. SAUDI ARABIA BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 171. SAUDI ARABIA BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 172. SAUDI ARABIA BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 173. SAUDI ARABIA BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 174. SAUDI ARABIA BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 175. SAUDI ARABIA BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 176. SAUDI ARABIA BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 177. SAUDI ARABIA BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 178. SAUDI ARABIA BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 179. SOUTH AFRICA BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 180. SOUTH AFRICA BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 181. SOUTH AFRICA BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 182. SOUTH AFRICA BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 183. SOUTH AFRICA BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 184. SOUTH AFRICA BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 185. SOUTH AFRICA BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 186. SOUTH AFRICA BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 187. SOUTH AFRICA BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 188. DENMARK BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 189. DENMARK BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 190. DENMARK BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 191. DENMARK BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 192. DENMARK BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 193. DENMARK BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 194. DENMARK BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 195. DENMARK BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 196. DENMARK BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 197. NETHERLANDS BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 198. NETHERLANDS BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 199. NETHERLANDS BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 200. NETHERLANDS BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 201. NETHERLANDS BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 202. NETHERLANDS BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 203. NETHERLANDS BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 204. NETHERLANDS BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 205. NETHERLANDS BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 206. QATAR BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 207. QATAR BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 208. QATAR BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 209. QATAR BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 210. QATAR BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 211. QATAR BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 212. QATAR BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 213. QATAR BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 214. QATAR BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 215. FINLAND BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 216. FINLAND BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 217. FINLAND BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 218. FINLAND BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 219. FINLAND BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 220. FINLAND BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 221. FINLAND BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 222. FINLAND BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 223. FINLAND BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 224. SWEDEN BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 225. SWEDEN BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 226. SWEDEN BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 227. SWEDEN BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 228. SWEDEN BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 229. SWEDEN BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 230. SWEDEN BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 231. SWEDEN BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 232. SWEDEN BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 233. NIGERIA BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 234. NIGERIA BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 235. NIGERIA BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 236. NIGERIA BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 237. NIGERIA BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 238. NIGERIA BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 239. NIGERIA BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 240. NIGERIA BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 241. NIGERIA BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 242. EGYPT BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 243. EGYPT BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 244. EGYPT BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 245. EGYPT BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 246. EGYPT BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 247. EGYPT BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 248. EGYPT BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 249. EGYPT BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 250. EGYPT BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 251. TURKEY BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 252. TURKEY BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 253. TURKEY BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 254. TURKEY BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 255. TURKEY BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 256. TURKEY BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 257. TURKEY BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 258. TURKEY BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 259. TURKEY BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 260. ISRAEL BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 261. ISRAEL BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 262. ISRAEL BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 263. ISRAEL BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 264. ISRAEL BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 265. ISRAEL BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 266. ISRAEL BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 267. ISRAEL BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 268. ISRAEL BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 269. NORWAY BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 270. NORWAY BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 271. NORWAY BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 272. NORWAY BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 273. NORWAY BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 274. NORWAY BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 275. NORWAY BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 276. NORWAY BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 277. NORWAY BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 278. POLAND BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 279. POLAND BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 280. POLAND BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 281. POLAND BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 282. POLAND BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 283. POLAND BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 284. POLAND BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 285. POLAND BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 286. POLAND BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 287. SWITZERLAND BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 288. SWITZERLAND BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 289. SWITZERLAND BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 290. SWITZERLAND BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 291. SWITZERLAND BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 292. SWITZERLAND BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 293. SWITZERLAND BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 294. SWITZERLAND BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 295. SWITZERLAND BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 296. ASIA-PACIFIC BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 297. ASIA-PACIFIC BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 298. ASIA-PACIFIC BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 299. ASIA-PACIFIC BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 300. ASIA-PACIFIC BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 301. ASIA-PACIFIC BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 302. ASIA-PACIFIC BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 303. ASIA-PACIFIC BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 304. ASIA-PACIFIC BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 305. ASIA-PACIFIC BATTEN DISEASE MARKET SIZE, BY COUNTRY, 2018-2030 (USD MILLION)
TABLE 306. CHINA BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 307. CHINA BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 308. CHINA BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 309. CHINA BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 310. CHINA BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 311. CHINA BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 312. CHINA BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 313. CHINA BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 314. CHINA BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 315. INDIA BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 316. INDIA BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 317. INDIA BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 318. INDIA BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 319. INDIA BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 320. INDIA BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 321. INDIA BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 322. INDIA BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 323. INDIA BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 324. JAPAN BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 325. JAPAN BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 326. JAPAN BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 327. JAPAN BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 328. JAPAN BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 329. JAPAN BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 330. JAPAN BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 331. JAPAN BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 332. JAPAN BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 333. AUSTRALIA BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 334. AUSTRALIA BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 335. AUSTRALIA BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 336. AUSTRALIA BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 337. AUSTRALIA BATTEN DISEASE MARKET SIZE, BY SYMPTOMATIC THERAPY, 2018-2030 (USD MILLION)
TABLE 338. AUSTRALIA BATTEN DISEASE MARKET SIZE, BY CLINICAL FORM, 2018-2030 (USD MILLION)
TABLE 339. AUSTRALIA BATTEN DISEASE MARKET SIZE, BY ROUTE OF ADMINISTRATION, 2018-2030 (USD MILLION)
TABLE 340. AUSTRALIA BATTEN DISEASE MARKET SIZE, BY DISTRIBUTION CHANNEL, 2018-2030 (USD MILLION)
TABLE 341. AUSTRALIA BATTEN DISEASE MARKET SIZE, BY END USER, 2018-2030 (USD MILLION)
TABLE 342. SOUTH KOREA BATTEN DISEASE MARKET SIZE, BY PRODUCT TYPE, 2018-2030 (USD MILLION)
TABLE 343. SOUTH KOREA BATTEN DISEASE MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2030 (USD MILLION)
TABLE 344. SOUTH KOREA BATTEN DISEASE MARKET SIZE, BY GENE THERAPY, 2018-2030 (USD MILLION)
TABLE 345. SOUTH KOREA BATTEN DISEASE MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, 2018-2030 (USD MILLION)
TABLE 346. S

Companies Mentioned

The companies profiled in this Batten Disease market report include:
  • BioMarin Pharmaceutical Inc.
  • Astellas Pharma Inc.
  • Spark Therapeutics, Inc.
  • Regenxbio Inc.
  • Lysogene SA
  • uniQure NV
  • Ultragenyx Pharmaceutical Inc.
  • Orchard Therapeutics Ltd.
  • Abeona Therapeutics, Inc.
  • Neurogene, Inc.

Methodology

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Table Information