Results for tag: "Exondys 51"

Exondys 51 is a drug used to treat Duchenne muscular dystrophy (DMD), a rare genetic disorder that affects the muscles and causes progressive muscle degeneration. Exondys 51 is the first and only FDA-approved drug for the treatment of DMD. It is a form of exon-skipping therapy, which works by skipping over a mutated section of the dystrophin gene, allowing the body to produce a functional form of the protein. Exondys 51 is a part of the Musculoskeletal Disorders Drugs market, which includes drugs used to treat a variety of conditions, such as arthritis, osteoporosis, and muscular dystrophy. These drugs are used to reduce pain, improve mobility, and slow the progression of the disease. Some companies in the Musculoskeletal Disorders Drugs market include Pfizer, Novartis, Merck, and Johnson & Johnson. These companies are involved in the research, development, and marketing of drugs for the treatment of musculoskeletal disorders. Show Less Read more