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Results for tag: "Hurler Syndrome Drug"

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Mucopolysaccharidosis I - Pipeline Insight, 2024

  • Clinical Trials
  • April 2024
  • 60 Pages
  • Global
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Hurler Syndrome is a rare genetic disorder that affects the central nervous system. It is caused by a deficiency of the enzyme alpha-L-iduronidase, which is responsible for breaking down certain complex sugars. As a result, these sugars accumulate in the body, leading to a variety of physical and mental disabilities. Treatment for Hurler Syndrome includes enzyme replacement therapy (ERT) and bone marrow transplantation. The Hurler Syndrome Drug market is a niche market within the Central Nervous System Drugs market. It is composed of drugs used to treat the symptoms of Hurler Syndrome, such as enzyme replacement therapy (ERT) and bone marrow transplantation. These drugs are typically used in combination with other treatments, such as physical therapy and occupational therapy. The companies in the Hurler Syndrome Drug market include Shire, Sanofi, and Pfizer. Shire is the leading manufacturer of ERT drugs for Hurler Syndrome, while Sanofi and Pfizer are both involved in the development of bone marrow transplantation drugs. Show Less Read more