+353-1-416-8900REST OF WORLD
+44-20-3973-8888REST OF WORLD
1-917-300-0470EAST COAST U.S
1-800-526-8630U.S. (TOLL FREE)
PTC Therapeutics - logo

PTC Therapeutics is a biopharmaceutical company that focuses on the development and commercialization of orally administered, small molecule drugs that target post-transcriptional control processes. The company's lead product candidate is Translarna (ataluren), which is for the treatment of of nonsense mutation Duchenne muscular dystrophy in ambulatory patients. It is currently in Phase III clinical trials to treat cystic fibrosis caused by nonsense mutations. The company was founded in 1998 and is headquartered in South Plainfield, New Jersey.

Leigh Syndrome Treatment Market - Global Strategic Business Report - Product Thumbnail Image

Leigh Syndrome Treatment Market - Global Strategic Business Report

  • Report
  • December 2025
  • 477 Pages
  • Global
From
Duchenne Muscular Dystrophy - Market Insight, Epidemiology and Market Forecast -2030 - Product Thumbnail Image

Duchenne Muscular Dystrophy - Market Insight, Epidemiology and Market Forecast -2030

  • Report
  • October 2021
  • 250 Pages
  • Global
From
Spinal Muscular Atrophy Treatment Market Size, Share & Trends Analysis Report By Type, By Treatment, By Route of Administration, By Region, And Segment Forecasts, 2025 - 2030 - Product Thumbnail Image

Spinal Muscular Atrophy Treatment Market Size, Share & Trends Analysis Report By Type, By Treatment, By Route of Administration, By Region, And Segment Forecasts, 2025 - 2030

  • Report
  • December 2024
  • 100 Pages
  • Global
From
US Orphan Drugs Market, Drugs Sales, Price, Dosage & Clinical Trials Insight 2028 - Product Thumbnail Image

US Orphan Drugs Market, Drugs Sales, Price, Dosage & Clinical Trials Insight 2028

  • Report
  • July 2023
  • 3600 Pages
  • United States
From
Dravet Syndrome Treatment Market 2025-2029 - Product Thumbnail Image

Dravet Syndrome Treatment Market 2025-2029

  • Report
  • May 2025
  • 222 Pages
  • Global
From
Becker Muscular Dystrophy Drug Global Market Insights 2023, Analysis and Forecast to 2028, by Manufacturers, Regions, Technology, Application, Product Type - Product Thumbnail Image

Becker Muscular Dystrophy Drug Global Market Insights 2023, Analysis and Forecast to 2028, by Manufacturers, Regions, Technology, Application, Product Type

  • Report
  • July 2023
  • 84 Pages
  • Global
From
Duchenne Muscular Dystrophy Clinical Trial Analysis by Trial Phase, Trial Status, Trial Counts, End Points, Status, Sponsor Type and Top Countries, 2023 Update - Product Thumbnail Image

Duchenne Muscular Dystrophy Clinical Trial Analysis by Trial Phase, Trial Status, Trial Counts, End Points, Status, Sponsor Type and Top Countries, 2023 Update

  • Report
  • April 2023
  • 231 Pages
  • Global
From
Friedreich Ataxia Clinical Trial Analysis by Trial Phase, Trial Status, Trial Counts, End Points, Status, Sponsor Type and Top Countries, 2023 Update - Product Thumbnail Image

Friedreich Ataxia Clinical Trial Analysis by Trial Phase, Trial Status, Trial Counts, End Points, Status, Sponsor Type and Top Countries, 2023 Update

  • Report
  • January 2023
  • 92 Pages
  • Global
From
Huntington Disease Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update - Product Thumbnail Image

Huntington Disease Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update

  • Report
  • November 2022
  • 299 Pages
  • Global
From
Non-Alcoholic Steatohepatitis (NASH) (Gastrointestinal) - Drugs in Development, 2021 - Product Thumbnail Image

Non-Alcoholic Steatohepatitis (NASH) (Gastrointestinal) - Drugs in Development, 2021

  • Drug Pipelines
  • March 2021
  • Global
From
Amyotrophic Lateral Sclerosis Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update - Product Thumbnail Image

Amyotrophic Lateral Sclerosis Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update

  • Report
  • September 2022
  • 672 Pages
  • Global
From
Spinal Muscular Atrophy Treatment Market - Global Forecast 2025-2032 - Product Thumbnail Image

Spinal Muscular Atrophy Treatment Market - Global Forecast 2025-2032

  • Report
  • November 2025
  • 183 Pages
  • Global
From
Huntington's Disease Therapeutics Market - Global Forecast 2025-2032 - Product Thumbnail Image

Huntington's Disease Therapeutics Market - Global Forecast 2025-2032

  • Report
  • October 2025
  • 186 Pages
  • Global
From
Syndrome Progressive Ataxia Weakness Disorder Treatment Market - Global Forecast 2025-2030 - Product Thumbnail Image

Syndrome Progressive Ataxia Weakness Disorder Treatment Market - Global Forecast 2025-2030

  • Report
  • August 2025
  • 190 Pages
  • Global
From
Drugs for Spinal Muscular Atrophy Market - Global Forecast 2025-2030 - Product Thumbnail Image

Drugs for Spinal Muscular Atrophy Market - Global Forecast 2025-2030

  • Report
  • August 2025
  • 195 Pages
  • Global
From
Peritoneal Cancer Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update - Product Thumbnail Image

Peritoneal Cancer Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update

  • Report
  • June 2022
  • 925 Pages
  • Global
From
Drug-Resistant Epilepsy Market - Global Industry Size, Share, Trends, Opportunity and Forecast, 2020-2030F - Product Thumbnail Image

Drug-Resistant Epilepsy Market - Global Industry Size, Share, Trends, Opportunity and Forecast, 2020-2030F

  • Report
  • April 2025
  • 184 Pages
  • Global
From
Epilepsy - Pipeline Insight, 2025 - Product Thumbnail Image

Epilepsy - Pipeline Insight, 2025

  • Clinical Trials
  • April 2025
  • 280 Pages
  • Global
From
Rett Syndrome - Pipeline Insight, 2025 - Product Thumbnail Image

Rett Syndrome - Pipeline Insight, 2025

  • Clinical Trials
  • April 2025
  • 80 Pages
  • Global
From
Huntington's Disease Treatment Market Forecasts from 2023 to 2028 - Product Thumbnail Image

Huntington's Disease Treatment Market Forecasts from 2023 to 2028

  • Report
  • November 2023
  • 145 Pages
  • Global
From
Loading Indicator