+353-1-416-8900REST OF WORLD
+44-20-3973-8888REST OF WORLD
1-917-300-0470EAST COAST U.S
1-800-526-8630U.S. (TOLL FREE)
PTC Therapeutics - logo

PTC Therapeutics is a biopharmaceutical company that focuses on the development and commercialization of orally administered, small molecule drugs that target post-transcriptional control processes. The company's lead product candidate is Translarna (ataluren), which is for the treatment of of nonsense mutation Duchenne muscular dystrophy in ambulatory patients. It is currently in Phase III clinical trials to treat cystic fibrosis caused by nonsense mutations. The company was founded in 1998 and is headquartered in South Plainfield, New Jersey.

Ataxia - Pipeline Insight, 2024 - Product Thumbnail Image

Ataxia - Pipeline Insight, 2024

  • Clinical Trials
  • April 2024
  • 120 Pages
  • Global
From
Huntington's Disease - Pipeline Insight, 2024 - Product Thumbnail Image

Huntington's Disease - Pipeline Insight, 2024

  • Drug Pipelines
  • April 2024
  • 150 Pages
  • Global
From
Acute Myelocytic Leukemia (AML, Acute Myeloblastic Leukemia) Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update - Product Thumbnail Image

Acute Myelocytic Leukemia (AML, Acute Myeloblastic Leukemia) Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update

  • Report
  • December 2022
  • 1560 Pages
  • Global
From
Acute Lymphocytic Leukemia (ALL, Acute Lymphoblastic Leukemia) Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update - Product Thumbnail Image

Acute Lymphocytic Leukemia (ALL, Acute Lymphoblastic Leukemia) Drugs in Development by Stages, Target, MoA, RoA, Molecule Type and Key Players, 2022 Update

  • Report
  • October 2022
  • 820 Pages
  • Global
From
Global Spinal Muscular Atrophy Treatment Market Report and Forecast 2023-2031 - Product Thumbnail Image

Global Spinal Muscular Atrophy Treatment Market Report and Forecast 2023-2031

  • Report
  • May 2023
  • 160 Pages
  • Global
From
Global Dravet Syndrome Treatment Market Report and Forecast 2023-2031 - Product Thumbnail Image

Global Dravet Syndrome Treatment Market Report and Forecast 2023-2031

  • Report
  • April 2023
  • 147 Pages
  • Global
From
Duchenne Muscular Dystrophy Disease - Global Clinical Trials Review, H2, 2020 - Product Thumbnail Image

Duchenne Muscular Dystrophy Disease - Global Clinical Trials Review, H2, 2020

  • Clinical Trials
  • October 2020
  • 211 Pages
  • Global
From
Amyotrophic Lateral Sclerosis - Pipeline Insight, 2024 - Product Thumbnail Image

Amyotrophic Lateral Sclerosis - Pipeline Insight, 2024

  • Clinical Trials
  • April 2024
  • 250 Pages
  • Global
From
Global Spinal Muscular Atrophy Treatment Market (2023-2028) Competitive Analysis, Impact of Covid-19, Impact of Economic Slowdown & Impending Recession, Ansoff Analysis - Product Thumbnail Image

Global Spinal Muscular Atrophy Treatment Market (2023-2028) Competitive Analysis, Impact of Covid-19, Impact of Economic Slowdown & Impending Recession, Ansoff Analysis

  • Report
  • February 2024
  • 209 Pages
  • Global
From
Friedreich Ataxia - Pipeline Insight, 2024 - Product Thumbnail Image

Friedreich Ataxia - Pipeline Insight, 2024

  • Clinical Trials
  • April 2024
  • 50 Pages
  • Global
From
Drug Resistant Epilepsy - Pipeline Insight, 2024 - Product Thumbnail Image

Drug Resistant Epilepsy - Pipeline Insight, 2024

  • Clinical Trials
  • April 2024
  • 80 Pages
  • Global
From
Rett Syndrome - Pipeline Insight, 2024 - Product Thumbnail Image

Rett Syndrome - Pipeline Insight, 2024

  • Clinical Trials
  • February 2024
  • 60 Pages
  • Global
From
Spinal Muscular Atrophy (SMA) Global Clinical Trials Review, H1, 2020 - Product Thumbnail Image

Spinal Muscular Atrophy (SMA) Global Clinical Trials Review, H1, 2020

  • Clinical Trials
  • February 2020
  • 105 Pages
  • Global
From
Leiomyosarcoma - Pipeline Insight, 2024 - Product Thumbnail Image

Leiomyosarcoma - Pipeline Insight, 2024

  • Clinical Trials
  • April 2024
  • 60 Pages
  • Global
From
Global Spinal Muscular Atrophy Treatment Market Size, Share & Industry Trends Analysis Report By Type (Type 1, Type 2, Type 3 and Type 4), By Route of Administration, By Treatment Type (Drug and Gene Therapy), By Drug Type, By Regional Outlook and Forecast, 2022 - 2028 - Product Thumbnail Image

Global Spinal Muscular Atrophy Treatment Market Size, Share & Industry Trends Analysis Report By Type (Type 1, Type 2, Type 3 and Type 4), By Route of Administration, By Treatment Type (Drug and Gene Therapy), By Drug Type, By Regional Outlook and Forecast, 2022 - 2028

  • Report
  • November 2022
  • 252 Pages
  • Global
From
Leigh disease - Pipeline Insight, 2024 - Product Thumbnail Image

Leigh disease - Pipeline Insight, 2024

  • Clinical Trials
  • April 2024
  • 60 Pages
  • Global
From
Prefilled Syringes Market, Industry Trends and Global Forecasts, till 2035: Distribution by Purpose of Syringe, Therapeutic Area, Type of Molecule, Type of Needle System, Usability of Syringe, Type of Syringe, Type of Packaging and Key Geographical Regions - Product Thumbnail Image

Prefilled Syringes Market, Industry Trends and Global Forecasts, till 2035: Distribution by Purpose of Syringe, Therapeutic Area, Type of Molecule, Type of Needle System, Usability of Syringe, Type of Syringe, Type of Packaging and Key Geographical Regions

  • Report
  • February 2024
  • 867 Pages
  • Global
From
Europe Spinal Muscular Atrophy Treatment Market Size, Share & Industry Trends Analysis Report By Type (Type 1, Type 2, Type 3 and Type 4), By Route of Administration, By Treatment Type (Drug and Gene Therapy), By Drug Type, By Country and Growth Forecast, 2022 - 2028 - Product Thumbnail Image

Europe Spinal Muscular Atrophy Treatment Market Size, Share & Industry Trends Analysis Report By Type (Type 1, Type 2, Type 3 and Type 4), By Route of Administration, By Treatment Type (Drug and Gene Therapy), By Drug Type, By Country and Growth Forecast, 2022 - 2028

  • Report
  • November 2022
  • 98 Pages
  • Europe
From
LAMEA Spinal Muscular Atrophy Treatment Market Size, Share & Industry Trends Analysis Report By Type (Type 1, Type 2, Type 3 and Type 4), By Route of Administration, By Treatment Type (Drug and Gene Therapy), By Drug Type, By Country and Growth Forecast, 2022 - 2028 - Product Thumbnail Image

LAMEA Spinal Muscular Atrophy Treatment Market Size, Share & Industry Trends Analysis Report By Type (Type 1, Type 2, Type 3 and Type 4), By Route of Administration, By Treatment Type (Drug and Gene Therapy), By Drug Type, By Country and Growth Forecast, 2022 - 2028

  • Report
  • November 2022
  • 99 Pages
  • Middle East, Africa
From
Asia Pacific Spinal Muscular Atrophy Treatment Market Size, Share & Industry Trends Analysis Report By Type (Type 1, Type 2, Type 3 and Type 4), By Route of Administration, By Treatment Type (Drug and Gene Therapy), By Drug Type, By Country and Growth Forecast, 2022 - 2028 - Product Thumbnail Image

Asia Pacific Spinal Muscular Atrophy Treatment Market Size, Share & Industry Trends Analysis Report By Type (Type 1, Type 2, Type 3 and Type 4), By Route of Administration, By Treatment Type (Drug and Gene Therapy), By Drug Type, By Country and Growth Forecast, 2022 - 2028

  • Report
  • November 2022
  • 99 Pages
  • Asia Pacific
From
Loading Indicator