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Lysosomal Storage Diseases Market - Global Forecast 2025-2030

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    Report

  • 188 Pages
  • August 2025
  • Region: Global
  • 360iResearch™
  • ID: 5888909
UP TO OFF until Jan 01st 2026
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The lysosomal storage diseases (LSDs) market is experiencing steady expansion, driven by advancements in therapeutic innovation, an evolving regulatory environment, and growing clinical demand across global healthcare systems. Complex, multisystemic pathologies and high unmet needs require strategic foresight from senior decision-makers navigating this challenging therapeutic landscape.

Market Snapshot: Lysosomal Storage Diseases Market

The Lysosomal Storage Diseases Market grew from USD 10.17 billion in 2024 to USD 11.01 billion in 2025. It is expected to continue growing at a CAGR of 8.38%, reaching USD 16.49 billion by 2030. This growth reflects momentum across R&D, commercial partnerships, and regulatory incentives within the rare disease sector.

Scope & Segmentation

This report provides a comprehensive view of the lysosomal storage diseases market, analyzing trends and revenue opportunities across critical segments, regions, and technologies.

  • Disease Types: Fabry, Gaucher, Hunter Syndrome, Mucopolysaccharidosis, Niemann-Pick, Pompe
  • Treatment Types: Enzyme replacement therapy (Agalsidase Beta, Alglucerase, Alglucosidase Alfa), gene therapy, hematopoietic stem cell transplant (allogeneic, autologous), substrate reduction therapy
  • Therapeutic Applications: Cardiovascular involvement, central nervous system interventions, hematological disorders, pulmonary complications, skeletal deformities
  • End Users: Academic and research institutes, biopharmaceutical companies, hospitals, specialty clinics
  • Regional Markets: Americas (with specific coverage for United States states, Canada, Mexico, Brazil, Argentina), Europe, Middle East, Africa (including major economies and healthcare systems), Asia-Pacific (featuring China, India, Japan, and several key Southeast Asian markets)
  • Leading Companies: Abeona Therapeutics Inc., Alexion Pharmaceuticals, Inc., Amicus Therapeutics, Inc., ArmaGen, Inc., BioMarin Pharmaceutical, Inc., CHIESI USA, Inc., Denali Therapeutics Inc., Freeline Therapeutics, Homology Medicines, Inc., Horizon Pharma PLC, Idorsia Pharmaceuticals Ltd., JCR Pharmaceuticals Co., Ltd., Neurogene Inc., Novartis AG, Orchard Therapeutics Limited, Pfizer Inc., Protalix Biotherapeutics Inc., Sangamo Therapeutics, Inc., Sanofi S.A., Spark Therapeutics, Inc., Swedish Orphan Biovitrum AB, Takeda Pharmaceutical Company Limited, Ultragenyx Pharmaceutical Inc., Zevra Therapeutics, Inc.

Key Takeaways for Senior Decision-Makers

  • The convergence of gene and enzyme therapies has begun to shift clinical strategies, opening possibilities for both durable and incremental patient benefit.
  • Collaborative models—linking biopharma, CROs, and academia—are expediting translation from research to bedside and supporting the evolution of innovative business models.
  • New digital health solutions, such as remote monitoring and decentralized trial technology, are being increasingly integrated to enhance patient engagement and streamline data collection in rare disease cohorts.
  • Regional policy diversity requires localized access strategies, from leveraging expedited regulatory pathways in mature markets to adapting tiered pricing in regions with significant healthcare disparities.
  • Targeted segmentation by disease type and therapeutic application improves trial design, informs investment prioritization, and sharpens commercialization approaches for niche populations.

Tariff Impact: Navigating US Policy Shifts

Revised United States tariff regulations for 2025 are expected to impact supply chains for lysosomal storage disease therapies. Import duties on biologic components could prompt manufacturers to reassess sourcing strategies, expand regional manufacturing, or diversify supplier networks. These pressures may also influence payer negotiations and pricing structures, underscoring the need for resilient supply chain infrastructure and proactive engagement with customs authorities.

Methodology & Data Sources

This analysis utilizes a mixed methods framework, combining primary interviews with clinicians, industry leaders, and regulatory experts, as well as secondary research from peer-reviewed literature, clinical trial registries, and financial disclosures. Consensus-building workshops refined the findings and provided additional expert validation.

Why This Report Matters

  • Offers multidimensional insights to support investment, product development, and market entry strategies across the lysosomal storage diseases market.
  • Equips leaders with forward-looking guidance, anticipating the business impact of technological evolution, policy shifts, and emerging patient needs.

Conclusion

The lysosomal storage diseases market is rapidly evolving, shaped by scientific progress, strategic collaboration, and regulatory change. Stakeholders prepared to adapt and innovate can drive improved outcomes and sustainable growth in this dynamic sector.

 

Additional Product Information:

  • Purchase of this report includes 1 year online access with quarterly updates.
  • This report can be updated on request. Please contact our Customer Experience team using the Ask a Question widget on our website.

Table of Contents

1. Preface
1.1. Objectives of the Study
1.2. Market Segmentation & Coverage
1.3. Years Considered for the Study
1.4. Currency & Pricing
1.5. Language
1.6. Stakeholders
2. Research Methodology
2.1. Define: Research Objective
2.2. Determine: Research Design
2.3. Prepare: Research Instrument
2.4. Collect: Data Source
2.5. Analyze: Data Interpretation
2.6. Formulate: Data Verification
2.7. Publish: Research Report
2.8. Repeat: Report Update
3. Executive Summary
4. Market Overview
4.1. Introduction
4.2. Market Sizing & Forecasting
5. Market Dynamics
5.1. Expansion of gene therapy approval pipelines targeting rare lysosomal storage disorders
5.2. Integration of newborn screening programs driving early detection of lysosomal storage diseases
5.3. Emergence of pharmacological chaperones improving enzyme stability in Fabry and Gaucher diseases
5.4. Advancements in CRISPR/Cas9 methodologies targeting CNS manifestations of Tay Sachs
5.5. Collaborations between biotech firms and academic centers accelerating Pompe disease clinical trials
5.6. Increasing use of real-world evidence to assess long-term outcomes of enzyme replacement therapies
5.7. Emerging small molecule substrates reducing glycosphingolipid accumulation in neuronopathic Gaucher disease
6. Market Insights
6.1. Porter’s Five Forces Analysis
6.2. PESTLE Analysis
7. Cumulative Impact of United States Tariffs 2025
8. Lysosomal Storage Diseases Market, by Disease Type
8.1. Introduction
8.2. Fabry Disease
8.3. Gaucher Disease
8.4. Hunter Syndrome
8.5. Mucopolysaccharidosis
8.6. Niemann-Pick Disease
8.7. Pompe Disease
9. Lysosomal Storage Diseases Market, by Treatment Type
9.1. Introduction
9.2. Enzyme Replacement Therapy
9.2.1. Agalsidase Beta
9.2.2. Alglucerase
9.2.3. Alglucosidase Alfa
9.3. Gene Therapy
9.4. Hematopoietic Stem Cell Transplant
9.4.1. Allogeneic Transplant
9.4.2. Autologous Transplant
9.5. Substrate Reduction Therapy
10. Lysosomal Storage Diseases Market, by Therapeutic Application
10.1. Introduction
10.2. Cardiovascular Involvement
10.3. Central Nervous System Involvement
10.4. Hematological Disorders
10.5. Pulmonary Complications
10.6. Skeletal Deformities
11. Lysosomal Storage Diseases Market, by End-User
11.1. Introduction
11.2. Academic & Research Institutes
11.3. Biopharmaceutical Companies
11.4. Hospitals
11.5. Specialty Clinics
12. Americas Lysosomal Storage Diseases Market
12.1. Introduction
12.2. United States
12.3. Canada
12.4. Mexico
12.5. Brazil
12.6. Argentina
13. Europe, Middle East & Africa Lysosomal Storage Diseases Market
13.1. Introduction
13.2. United Kingdom
13.3. Germany
13.4. France
13.5. Russia
13.6. Italy
13.7. Spain
13.8. United Arab Emirates
13.9. Saudi Arabia
13.10. South Africa
13.11. Denmark
13.12. Netherlands
13.13. Qatar
13.14. Finland
13.15. Sweden
13.16. Nigeria
13.17. Egypt
13.18. Turkey
13.19. Israel
13.20. Norway
13.21. Poland
13.22. Switzerland
14. Asia-Pacific Lysosomal Storage Diseases Market
14.1. Introduction
14.2. China
14.3. India
14.4. Japan
14.5. Australia
14.6. South Korea
14.7. Indonesia
14.8. Thailand
14.9. Philippines
14.10. Malaysia
14.11. Singapore
14.12. Vietnam
14.13. Taiwan
15. Competitive Landscape
15.1. Market Share Analysis, 2024
15.2. FPNV Positioning Matrix, 2024
15.3. Competitive Analysis
15.3.1. Abeona Therapeutics Inc.
15.3.2. Alexion Pharmaceuticals, Inc.
15.3.3. Amicus Therapeutics,Inc.
15.3.4. ArmaGen, Inc.
15.3.5. BioMarin Pharmaceutical, Inc.
15.3.6. CHIESI USA, Inc.
15.3.7. Denali Therapeutics Inc.
15.3.8. Freeline Therapeutics
15.3.9. Homology Medicines, Inc.
15.3.10. Horizon Pharma PLC
15.3.11. Idorsia Pharmaceuticals Ltd.
15.3.12. JCR Pharmaceuticals Co., Ltd.
15.3.13. Neurogene Inc.
15.3.14. Novartis AG
15.3.15. Orchard Therapeutics Limited
15.3.16. Pfizer Inc.
15.3.17. Protalix Biotherapeutics Inc.
15.3.18. Sangamo Therapeutics, Inc.
15.3.19. Sanofi S.A.
15.3.20. Spark Therapeutics, Inc.
15.3.21. Swedish Orphan Biovitrum AB
15.3.22. Takeda Pharmaceutical Company Limited
15.3.23. Ultragenyx Pharmaceutical Inc.
15.3.24. Zevra Therapeutics,Inc.
16. ResearchAI
17. ResearchStatistics
18. ResearchContacts
19. ResearchArticles
20. Appendix
List of Figures
FIGURE 1. LYSOSOMAL STORAGE DISEASES MARKET RESEARCH PROCESS
FIGURE 2. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, 2018-2030 (USD MILLION)
FIGURE 3. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY REGION, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 4. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 5. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2024 VS 2030 (%)
FIGURE 6. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 7. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2024 VS 2030 (%)
FIGURE 8. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 9. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2024 VS 2030 (%)
FIGURE 10. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 11. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2024 VS 2030 (%)
FIGURE 12. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 13. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2024 VS 2030 (%)
FIGURE 14. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 15. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY STATE, 2024 VS 2030 (%)
FIGURE 16. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY STATE, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 17. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2024 VS 2030 (%)
FIGURE 18. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 19. ASIA-PACIFIC LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2024 VS 2030 (%)
FIGURE 20. ASIA-PACIFIC LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2024 VS 2025 VS 2030 (USD MILLION)
FIGURE 21. LYSOSOMAL STORAGE DISEASES MARKET SHARE, BY KEY PLAYER, 2024
FIGURE 22. LYSOSOMAL STORAGE DISEASES MARKET, FPNV POSITIONING MATRIX, 2024
FIGURE 23. LYSOSOMAL STORAGE DISEASES MARKET: RESEARCHAI
FIGURE 24. LYSOSOMAL STORAGE DISEASES MARKET: RESEARCHSTATISTICS
FIGURE 25. LYSOSOMAL STORAGE DISEASES MARKET: RESEARCHCONTACTS
FIGURE 26. LYSOSOMAL STORAGE DISEASES MARKET: RESEARCHARTICLES
List of Tables
TABLE 1. LYSOSOMAL STORAGE DISEASES MARKET SEGMENTATION & COVERAGE
TABLE 2. UNITED STATES DOLLAR EXCHANGE RATE, 2018-2024
TABLE 3. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, 2018-2024 (USD MILLION)
TABLE 4. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, 2025-2030 (USD MILLION)
TABLE 5. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY REGION, 2018-2024 (USD MILLION)
TABLE 6. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY REGION, 2025-2030 (USD MILLION)
TABLE 7. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2018-2024 (USD MILLION)
TABLE 8. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2025-2030 (USD MILLION)
TABLE 9. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 10. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 11. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY FABRY DISEASE, BY REGION, 2018-2024 (USD MILLION)
TABLE 12. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY FABRY DISEASE, BY REGION, 2025-2030 (USD MILLION)
TABLE 13. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY GAUCHER DISEASE, BY REGION, 2018-2024 (USD MILLION)
TABLE 14. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY GAUCHER DISEASE, BY REGION, 2025-2030 (USD MILLION)
TABLE 15. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HUNTER SYNDROME, BY REGION, 2018-2024 (USD MILLION)
TABLE 16. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HUNTER SYNDROME, BY REGION, 2025-2030 (USD MILLION)
TABLE 17. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY MUCOPOLYSACCHARIDOSIS, BY REGION, 2018-2024 (USD MILLION)
TABLE 18. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY MUCOPOLYSACCHARIDOSIS, BY REGION, 2025-2030 (USD MILLION)
TABLE 19. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY NIEMANN-PICK DISEASE, BY REGION, 2018-2024 (USD MILLION)
TABLE 20. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY NIEMANN-PICK DISEASE, BY REGION, 2025-2030 (USD MILLION)
TABLE 21. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY POMPE DISEASE, BY REGION, 2018-2024 (USD MILLION)
TABLE 22. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY POMPE DISEASE, BY REGION, 2025-2030 (USD MILLION)
TABLE 23. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 24. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 25. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, BY REGION, 2018-2024 (USD MILLION)
TABLE 26. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, BY REGION, 2025-2030 (USD MILLION)
TABLE 27. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY AGALSIDASE BETA, BY REGION, 2018-2024 (USD MILLION)
TABLE 28. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY AGALSIDASE BETA, BY REGION, 2025-2030 (USD MILLION)
TABLE 29. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ALGLUCERASE, BY REGION, 2018-2024 (USD MILLION)
TABLE 30. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ALGLUCERASE, BY REGION, 2025-2030 (USD MILLION)
TABLE 31. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ALGLUCOSIDASE ALFA, BY REGION, 2018-2024 (USD MILLION)
TABLE 32. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ALGLUCOSIDASE ALFA, BY REGION, 2025-2030 (USD MILLION)
TABLE 33. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 34. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 35. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY GENE THERAPY, BY REGION, 2018-2024 (USD MILLION)
TABLE 36. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY GENE THERAPY, BY REGION, 2025-2030 (USD MILLION)
TABLE 37. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, BY REGION, 2018-2024 (USD MILLION)
TABLE 38. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, BY REGION, 2025-2030 (USD MILLION)
TABLE 39. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ALLOGENEIC TRANSPLANT, BY REGION, 2018-2024 (USD MILLION)
TABLE 40. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ALLOGENEIC TRANSPLANT, BY REGION, 2025-2030 (USD MILLION)
TABLE 41. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY AUTOLOGOUS TRANSPLANT, BY REGION, 2018-2024 (USD MILLION)
TABLE 42. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY AUTOLOGOUS TRANSPLANT, BY REGION, 2025-2030 (USD MILLION)
TABLE 43. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
TABLE 44. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2025-2030 (USD MILLION)
TABLE 45. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, BY REGION, 2018-2024 (USD MILLION)
TABLE 46. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, BY REGION, 2025-2030 (USD MILLION)
TABLE 47. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2024 (USD MILLION)
TABLE 48. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025-2030 (USD MILLION)
TABLE 49. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY CARDIOVASCULAR INVOLVEMENT, BY REGION, 2018-2024 (USD MILLION)
TABLE 50. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY CARDIOVASCULAR INVOLVEMENT, BY REGION, 2025-2030 (USD MILLION)
TABLE 51. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY CENTRAL NERVOUS SYSTEM INVOLVEMENT, BY REGION, 2018-2024 (USD MILLION)
TABLE 52. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY CENTRAL NERVOUS SYSTEM INVOLVEMENT, BY REGION, 2025-2030 (USD MILLION)
TABLE 53. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOLOGICAL DISORDERS, BY REGION, 2018-2024 (USD MILLION)
TABLE 54. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOLOGICAL DISORDERS, BY REGION, 2025-2030 (USD MILLION)
TABLE 55. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY PULMONARY COMPLICATIONS, BY REGION, 2018-2024 (USD MILLION)
TABLE 56. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY PULMONARY COMPLICATIONS, BY REGION, 2025-2030 (USD MILLION)
TABLE 57. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY SKELETAL DEFORMITIES, BY REGION, 2018-2024 (USD MILLION)
TABLE 58. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY SKELETAL DEFORMITIES, BY REGION, 2025-2030 (USD MILLION)
TABLE 59. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2024 (USD MILLION)
TABLE 60. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025-2030 (USD MILLION)
TABLE 61. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ACADEMIC & RESEARCH INSTITUTES, BY REGION, 2018-2024 (USD MILLION)
TABLE 62. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ACADEMIC & RESEARCH INSTITUTES, BY REGION, 2025-2030 (USD MILLION)
TABLE 63. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY BIOPHARMACEUTICAL COMPANIES, BY REGION, 2018-2024 (USD MILLION)
TABLE 64. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY BIOPHARMACEUTICAL COMPANIES, BY REGION, 2025-2030 (USD MILLION)
TABLE 65. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HOSPITALS, BY REGION, 2018-2024 (USD MILLION)
TABLE 66. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HOSPITALS, BY REGION, 2025-2030 (USD MILLION)
TABLE 67. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY SPECIALTY CLINICS, BY REGION, 2018-2024 (USD MILLION)
TABLE 68. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY SPECIALTY CLINICS, BY REGION, 2025-2030 (USD MILLION)
TABLE 69. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 70. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 71. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 72. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 73. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 74. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 75. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
TABLE 76. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2025-2030 (USD MILLION)
TABLE 77. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2024 (USD MILLION)
TABLE 78. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025-2030 (USD MILLION)
TABLE 79. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2024 (USD MILLION)
TABLE 80. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025-2030 (USD MILLION)
TABLE 81. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2018-2024 (USD MILLION)
TABLE 82. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2025-2030 (USD MILLION)
TABLE 83. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 84. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 85. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 86. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 87. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 88. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 89. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
TABLE 90. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2025-2030 (USD MILLION)
TABLE 91. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2024 (USD MILLION)
TABLE 92. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025-2030 (USD MILLION)
TABLE 93. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2024 (USD MILLION)
TABLE 94. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025-2030 (USD MILLION)
TABLE 95. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY STATE, 2018-2024 (USD MILLION)
TABLE 96. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY STATE, 2025-2030 (USD MILLION)
TABLE 97. CANADA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 98. CANADA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 99. CANADA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 100. CANADA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 101. CANADA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 102. CANADA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 103. CANADA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
TABLE 104. CANADA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2025-2030 (USD MILLION)
TABLE 105. CANADA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2024 (USD MILLION)
TABLE 106. CANADA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025-2030 (USD MILLION)
TABLE 107. CANADA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2024 (USD MILLION)
TABLE 108. CANADA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025-2030 (USD MILLION)
TABLE 109. MEXICO LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 110. MEXICO LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 111. MEXICO LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 112. MEXICO LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 113. MEXICO LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 114. MEXICO LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 115. MEXICO LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
TABLE 116. MEXICO LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2025-2030 (USD MILLION)
TABLE 117. MEXICO LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2024 (USD MILLION)
TABLE 118. MEXICO LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025-2030 (USD MILLION)
TABLE 119. MEXICO LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2024 (USD MILLION)
TABLE 120. MEXICO LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025-2030 (USD MILLION)
TABLE 121. BRAZIL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 122. BRAZIL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 123. BRAZIL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 124. BRAZIL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 125. BRAZIL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 126. BRAZIL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 127. BRAZIL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
TABLE 128. BRAZIL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2025-2030 (USD MILLION)
TABLE 129. BRAZIL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2024 (USD MILLION)
TABLE 130. BRAZIL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025-2030 (USD MILLION)
TABLE 131. BRAZIL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2024 (USD MILLION)
TABLE 132. BRAZIL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025-2030 (USD MILLION)
TABLE 133. ARGENTINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 134. ARGENTINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 135. ARGENTINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 136. ARGENTINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 137. ARGENTINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 138. ARGENTINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 139. ARGENTINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
TABLE 140. ARGENTINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2025-2030 (USD MILLION)
TABLE 141. ARGENTINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2024 (USD MILLION)
TABLE 142. ARGENTINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025-2030 (USD MILLION)
TABLE 143. ARGENTINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2024 (USD MILLION)
TABLE 144. ARGENTINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025-2030 (USD MILLION)
TABLE 145. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 146. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 147. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 148. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 149. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 150. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 151. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
TABLE 152. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2025-2030 (USD MILLION)
TABLE 153. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2024 (USD MILLION)
TABLE 154. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025-2030 (USD MILLION)
TABLE 155. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2024 (USD MILLION)
TABLE 156. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025-2030 (USD MILLION)
TABLE 157. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2018-2024 (USD MILLION)
TABLE 158. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2025-2030 (USD MILLION)
TABLE 159. UNITED KINGDOM LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 160. UNITED KINGDOM LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 161. UNITED KINGDOM LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 162. UNITED KINGDOM LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 163. UNITED KINGDOM LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 164. UNITED KINGDOM LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 165. UNITED KINGDOM LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
TABLE 166. UNITED KINGDOM LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2025-2030 (USD MILLION)
TABLE 167. UNITED KINGDOM LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2024 (USD MILLION)
TABLE 168. UNITED KINGDOM LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025-2030 (USD MILLION)
TABLE 169. UNITED KINGDOM LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2024 (USD MILLION)
TABLE 170. UNITED KINGDOM LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025-2030 (USD MILLION)
TABLE 171. GERMANY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 172. GERMANY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 173. GERMANY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 174. GERMANY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 175. GERMANY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 176. GERMANY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 177. GERMANY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
TABLE 178. GERMANY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2025-2030 (USD MILLION)
TABLE 179. GERMANY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2024 (USD MILLION)
TABLE 180. GERMANY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025-2030 (USD MILLION)
TABLE 181. GERMANY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2024 (USD MILLION)
TABLE 182. GERMANY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025-2030 (USD MILLION)
TABLE 183. FRANCE LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 184. FRANCE LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 185. FRANCE LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 186. FRANCE LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 187. FRANCE LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 188. FRANCE LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 189. FRANCE LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
TABLE 190. FRANCE LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2025-2030 (USD MILLION)
TABLE 191. FRANCE LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2024 (USD MILLION)
TABLE 192. FRANCE LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025-2030 (USD MILLION)
TABLE 193. FRANCE LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2024 (USD MILLION)
TABLE 194. FRANCE LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025-2030 (USD MILLION)
TABLE 195. RUSSIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 196. RUSSIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 197. RUSSIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 198. RUSSIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 199. RUSSIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 200. RUSSIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 201. RUSSIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
TABLE 202. RUSSIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2025-2030 (USD MILLION)
TABLE 203. RUSSIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2024 (USD MILLION)
TABLE 204. RUSSIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025-2030 (USD MILLION)
TABLE 205. RUSSIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2024 (USD MILLION)
TABLE 206. RUSSIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025-2030 (USD MILLION)
TABLE 207. ITALY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 208. ITALY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 209. ITALY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 210. ITALY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 211. ITALY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 212. ITALY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 213. ITALY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
TABLE 214. ITALY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2025-2030 (USD MILLION)
TABLE 215. ITALY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2024 (USD MILLION)
TABLE 216. ITALY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025-2030 (USD MILLION)
TABLE 217. ITALY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2024 (USD MILLION)
TABLE 218. ITALY LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025-2030 (USD MILLION)
TABLE 219. SPAIN LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 220. SPAIN LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 221. SPAIN LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 222. SPAIN LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 223. SPAIN LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 224. SPAIN LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 225. SPAIN LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
TABLE 226. SPAIN LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2025-2030 (USD MILLION)
TABLE 227. SPAIN LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2024 (USD MILLION)
TABLE 228. SPAIN LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025-2030 (USD MILLION)
TABLE 229. SPAIN LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2024 (USD MILLION)
TABLE 230. SPAIN LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025-2030 (USD MILLION)
TABLE 231. UNITED ARAB EMIRATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 232. UNITED ARAB EMIRATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 233. UNITED ARAB EMIRATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 234. UNITED ARAB EMIRATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 235. UNITED ARAB EMIRATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 236. UNITED ARAB EMIRATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 237. UNITED ARAB EMIRATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
TABLE 238. UNITED ARAB EMIRATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2025-2030 (USD MILLION)
TABLE 239. UNITED ARAB EMIRATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2024 (USD MILLION)
TABLE 240. UNITED ARAB EMIRATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025-2030 (USD MILLION)
TABLE 241. UNITED ARAB EMIRATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2024 (USD MILLION)
TABLE 242. UNITED ARAB EMIRATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025-2030 (USD MILLION)
TABLE 243. SAUDI ARABIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 244. SAUDI ARABIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 245. SAUDI ARABIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 246. SAUDI ARABIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 247. SAUDI ARABIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 248. SAUDI ARABIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 249. SAUDI ARABIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
TABLE 250. SAUDI ARABIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2025-2030 (USD MILLION)
TABLE 251. SAUDI ARABIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2024 (USD MILLION)
TABLE 252. SAUDI ARABIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025-2030 (USD MILLION)
TABLE 253. SAUDI ARABIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2024 (USD MILLION)
TABLE 254. SAUDI ARABIA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025-2030 (USD MILLION)
TABLE 255. SOUTH AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 256. SOUTH AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 257. SOUTH AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 258. SOUTH AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 259. SOUTH AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 260. SOUTH AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 261. SOUTH AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
TABLE 262. SOUTH AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2025-2030 (USD MILLION)
TABLE 263. SOUTH AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2024 (USD MILLION)
TABLE 264. SOUTH AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025-2030 (USD MILLION)
TABLE 265. SOUTH AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2024 (USD MILLION)
TABLE 266. SOUTH AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025-2030 (USD MILLION)
TABLE 267. DENMARK LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 268. DENMARK LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 269. DENMARK LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 270. DENMARK LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 271. DENMARK LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 272. DENMARK LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 273. DENMARK LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
TABLE 274. DENMARK LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2025-2030 (USD MILLION)
TABLE 275. DENMARK LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2024 (USD MILLION)
TABLE 276. DENMARK LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025-2030 (USD MILLION)
TABLE 277. DENMARK LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2024 (USD MILLION)
TABLE 278. DENMARK LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025-2030 (USD MILLION)
TABLE 279. NETHERLANDS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 280. NETHERLANDS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 281. NETHERLANDS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 282. NETHERLANDS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 283. NETHERLANDS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 284. NETHERLANDS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 285. NETHERLANDS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
TABLE 286. NETHERLANDS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2025-2030 (USD MILLION)
TABLE 287. NETHERLANDS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2024 (USD MILLION)
TABLE 288. NETHERLANDS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025-2030 (USD MILLION)
TABLE 289. NETHERLANDS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2024 (USD MILLION)
TABLE 290. NETHERLANDS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025-2030 (USD MILLION)
TABLE 291. QATAR LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2024 (USD MILLION)
TABLE 292. QATAR LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025-2030 (USD MILLION)
TABLE 293. QATAR LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2024 (USD MILLION)
TABLE 294. QATAR LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025-2030 (USD MILLION)
TABLE 295. QATAR LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2024 (USD MILLION)
TABLE 296. QATAR LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2025-2030 (USD MILLION)
TABLE 297. QATAR LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2024 (USD MILLION)
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Companies Mentioned

The major companies profiled in this Lysosomal Storage Diseases market report include:
  • Abeona Therapeutics Inc.
  • Alexion Pharmaceuticals, Inc.
  • Amicus Therapeutics,Inc.
  • ArmaGen, Inc.
  • BioMarin Pharmaceutical, Inc.
  • CHIESI USA, Inc.
  • Denali Therapeutics Inc.
  • Freeline Therapeutics
  • Homology Medicines, Inc.
  • Horizon Pharma PLC
  • Idorsia Pharmaceuticals Ltd.
  • JCR Pharmaceuticals Co., Ltd.
  • Neurogene Inc.
  • Novartis AG
  • Orchard Therapeutics Limited
  • Pfizer Inc.
  • Protalix Biotherapeutics Inc.
  • Sangamo Therapeutics, Inc.
  • Sanofi S.A.
  • Spark Therapeutics, Inc.
  • Swedish Orphan Biovitrum AB
  • Takeda Pharmaceutical Company Limited
  • Ultragenyx Pharmaceutical Inc.
  • Zevra Therapeutics,Inc.

Table Information