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Lysosomal Storage Diseases Market - Global Forecast 2026-2032

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    Report

  • 192 Pages
  • January 2026
  • Region: Global
  • 360iResearch™
  • ID: 5888909
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Senior leaders in life sciences are navigating a pivotal stage in the lysosomal storage diseases market, driven by rapid innovation in diagnostics, evolving therapies, and changing approaches to care and reimbursement. Acting on clear market intelligence is essential for shaping strategic decisions and maintaining an operational edge.

Market Snapshot: Lysosomal Storage Diseases Market Overview

The Lysosomal Storage Diseases Market advanced from USD 11.01 billion in 2025 to USD 11.92 billion in 2026 and is projected to reach USD 19.68 billion by 2032, at a CAGR of 8.64%. Industry momentum is propelled by the complexity of chronic disease presentation and increased focus from diverse stakeholders. Rising adoption of advanced diagnostics and demand for novel treatment modalities are shaping a landscape where global access to emerging therapies is expanding and new commercial models are coming to the forefront.

Scope & Segmentation

  • Disease Types: Covers Fabry disease, Gaucher disease, Hunter syndrome, mucopolysaccharidoses, Niemann-Pick disease, Pompe disease, and other rare, inherited lysosomal storage phenotypes requiring individualized management strategies.
  • Treatment Modalities: Includes enzyme replacement therapy such as agalsidase beta, alglucerase, and alglucosidase alfa, along with gene therapy, hematopoietic stem cell transplant (allogeneic and autologous), and substrate reduction therapy.
  • Therapeutic Applications: Addresses cardiovascular involvement, central nervous system symptoms, hematological disorders, pulmonary complications, and skeletal issues prevalent in lysosomal storage disorders.
  • End-User Segments: Analyzes needs across academic and research institutes, biopharmaceutical companies, hospitals, and specialty clinics, highlighting each group's unique operational and research requirements.
  • Geographical Coverage: Reviews distinct market attributes across the Americas, Europe Middle East & Africa, and Asia-Pacific, with consideration of regional regulatory dynamics and access to innovation.

Key Takeaways: Strategic Insights for Senior Leaders

  • Accelerated use of molecular diagnostic platforms and expanded newborn screening facilitate earlier intervention, reshaping clinical pathways and driving demand for adaptive research protocols.
  • Cutting-edge scientific advances, including development in gene editing and improvements in vector engineering, are expanding available therapeutic options beyond enzyme replacement, supporting the shift toward precision medicine.
  • Value assessment frameworks among payers and health systems are evolving, placing greater emphasis on long-term, real-world data and requiring comprehensive evidence gathering for outcomes-based reimbursement strategies.
  • Resilience in supply networks is achieved through increased localization, development of strategic partnerships with manufacturing experts, and continuous adaptation to minimize operational disruptions.
  • Multi-stakeholder collaborations connecting clinical centers, diagnostic innovators, and biopharmaceutical partners are expediting biomarker validation, streamlining regulatory interactions, and improving the pace of market access for new therapies.
  • Patient advocacy networks increasingly influence registry development, patient recruitment processes, and post-market data collection, bridging the gap between commercial priorities and patient-centered care.

Tariff Impact: United States 2025 Adjustments

The 2025 United States tariff revisions raised duties on essential pharmaceutical imports, disrupting supply chains for rare disease treatments. In response, organizations diversified suppliers, enhanced domestic sourcing, and re-evaluated investments in production capacity. Pricing strategies adapted to shifting cost structures, while payers sought robust pharmacoeconomic evidence to guide reimbursement decisions. These circumstances increased complexity in research and development planning, underscoring the importance of agile resource sourcing and proactive engagement with policy stakeholders.

Methodology & Data Sources

This analysis integrates a systematic review of current literature, regulatory landscape assessment, and structured interviews with clinicians, payers, manufacturers, and advocates. Rigorous triangulation and quality controls ensure all findings represent the latest scientific, manufacturing, and policy developments.

Why This Report Matters

  • Provides a clear view of the evolving clinical and commercial landscape, empowering leaders to proactively align diagnostics and therapeutic programs with new standards.
  • Identifies key operational, regulatory, and reimbursement risks driven by policy change, supporting robust strategic planning and capital allocation.
  • Enables targeted collaboration across the value chain, from discovery and production to real-world patient management, offering actionable intelligence for competitive advantage.

Conclusion

The lysosomal storage diseases market is defined by rapid diagnostic progress, innovative therapy approaches, and a growing focus on collaboration. For organizations planning sustainable growth, investment in early detection, resilient operations, and cross-sector research partnerships is essential.

 

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Table of Contents

1. Preface
1.1. Objectives of the Study
1.2. Market Definition
1.3. Market Segmentation & Coverage
1.4. Years Considered for the Study
1.5. Currency Considered for the Study
1.6. Language Considered for the Study
1.7. Key Stakeholders
2. Research Methodology
2.1. Introduction
2.2. Research Design
2.2.1. Primary Research
2.2.2. Secondary Research
2.3. Research Framework
2.3.1. Qualitative Analysis
2.3.2. Quantitative Analysis
2.4. Market Size Estimation
2.4.1. Top-Down Approach
2.4.2. Bottom-Up Approach
2.5. Data Triangulation
2.6. Research Outcomes
2.7. Research Assumptions
2.8. Research Limitations
3. Executive Summary
3.1. Introduction
3.2. CXO Perspective
3.3. Market Size & Growth Trends
3.4. Market Share Analysis, 2025
3.5. FPNV Positioning Matrix, 2025
3.6. New Revenue Opportunities
3.7. Next-Generation Business Models
3.8. Industry Roadmap
4. Market Overview
4.1. Introduction
4.2. Industry Ecosystem & Value Chain Analysis
4.2.1. Supply-Side Analysis
4.2.2. Demand-Side Analysis
4.2.3. Stakeholder Analysis
4.3. Porter’s Five Forces Analysis
4.4. PESTLE Analysis
4.5. Market Outlook
4.5.1. Near-Term Market Outlook (0-2 Years)
4.5.2. Medium-Term Market Outlook (3-5 Years)
4.5.3. Long-Term Market Outlook (5-10 Years)
4.6. Go-to-Market Strategy
5. Market Insights
5.1. Consumer Insights & End-User Perspective
5.2. Consumer Experience Benchmarking
5.3. Opportunity Mapping
5.4. Distribution Channel Analysis
5.5. Pricing Trend Analysis
5.6. Regulatory Compliance & Standards Framework
5.7. ESG & Sustainability Analysis
5.8. Disruption & Risk Scenarios
5.9. Return on Investment & Cost-Benefit Analysis
6. Cumulative Impact of United States Tariffs 2025
7. Cumulative Impact of Artificial Intelligence 2025
8. Lysosomal Storage Diseases Market, by Disease Type
8.1. Fabry Disease
8.2. Gaucher Disease
8.3. Hunter Syndrome
8.4. Mucopolysaccharidosis
8.5. Niemann-Pick Disease
8.6. Pompe Disease
9. Lysosomal Storage Diseases Market, by Treatment Type
9.1. Enzyme Replacement Therapy
9.1.1. Agalsidase Beta
9.1.2. Alglucerase
9.1.3. Alglucosidase Alfa
9.2. Gene Therapy
9.3. Hematopoietic Stem Cell Transplant
9.3.1. Allogeneic Transplant
9.3.2. Autologous Transplant
9.4. Substrate Reduction Therapy
10. Lysosomal Storage Diseases Market, by Therapeutic Application
10.1. Cardiovascular Involvement
10.2. Central Nervous System Involvement
10.3. Hematological Disorders
10.4. Pulmonary Complications
10.5. Skeletal Deformities
11. Lysosomal Storage Diseases Market, by End-User
11.1. Academic & Research Institutes
11.2. Biopharmaceutical Companies
11.3. Hospitals
11.4. Specialty Clinics
12. Lysosomal Storage Diseases Market, by Region
12.1. Americas
12.1.1. North America
12.1.2. Latin America
12.2. Europe, Middle East & Africa
12.2.1. Europe
12.2.2. Middle East
12.2.3. Africa
12.3. Asia-Pacific
13. Lysosomal Storage Diseases Market, by Group
13.1. ASEAN
13.2. GCC
13.3. European Union
13.4. BRICS
13.5. G7
13.6. NATO
14. Lysosomal Storage Diseases Market, by Country
14.1. United States
14.2. Canada
14.3. Mexico
14.4. Brazil
14.5. United Kingdom
14.6. Germany
14.7. France
14.8. Russia
14.9. Italy
14.10. Spain
14.11. China
14.12. India
14.13. Japan
14.14. Australia
14.15. South Korea
15. United States Lysosomal Storage Diseases Market
16. China Lysosomal Storage Diseases Market
17. Competitive Landscape
17.1. Market Concentration Analysis, 2025
17.1.1. Concentration Ratio (CR)
17.1.2. Herfindahl Hirschman Index (HHI)
17.2. Recent Developments & Impact Analysis, 2025
17.3. Product Portfolio Analysis, 2025
17.4. Benchmarking Analysis, 2025
17.5. Abeona Therapeutics Inc.
17.6. Alexion Pharmaceuticals, Inc.
17.7. Amicus Therapeutics,Inc.
17.8. ArmaGen, Inc.
17.9. BioMarin Pharmaceutical, Inc.
17.10. CHIESI USA, Inc.
17.11. Denali Therapeutics Inc.
17.12. Freeline Therapeutics
17.13. Homology Medicines, Inc.
17.14. Horizon Pharma PLC
17.15. Idorsia Pharmaceuticals Ltd.
17.16. JCR Pharmaceuticals Co., Ltd.
17.17. Neurogene Inc.
17.18. Novartis AG
17.19. Orchard Therapeutics Limited
17.20. Pfizer Inc.
17.21. Protalix Biotherapeutics Inc.
17.22. Sangamo Therapeutics, Inc.
17.23. Sanofi S.A.
17.24. Spark Therapeutics, Inc.
17.25. Swedish Orphan Biovitrum AB
17.26. Takeda Pharmaceutical Company Limited
17.27. Ultragenyx Pharmaceutical Inc.
17.28. Zevra Therapeutics,Inc.
List of Figures
FIGURE 1. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, 2018-2032 (USD MILLION)
FIGURE 2. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SHARE, BY KEY PLAYER, 2025
FIGURE 3. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET, FPNV POSITIONING MATRIX, 2025
FIGURE 4. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2025 VS 2026 VS 2032 (USD MILLION)
FIGURE 5. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2025 VS 2026 VS 2032 (USD MILLION)
FIGURE 6. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2025 VS 2026 VS 2032 (USD MILLION)
FIGURE 7. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2025 VS 2026 VS 2032 (USD MILLION)
FIGURE 8. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY REGION, 2025 VS 2026 VS 2032 (USD MILLION)
FIGURE 9. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY GROUP, 2025 VS 2026 VS 2032 (USD MILLION)
FIGURE 10. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2025 VS 2026 VS 2032 (USD MILLION)
FIGURE 11. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, 2018-2032 (USD MILLION)
FIGURE 12. CHINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, 2018-2032 (USD MILLION)
List of Tables
TABLE 1. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, 2018-2032 (USD MILLION)
TABLE 2. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2032 (USD MILLION)
TABLE 3. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY FABRY DISEASE, BY REGION, 2018-2032 (USD MILLION)
TABLE 4. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY FABRY DISEASE, BY GROUP, 2018-2032 (USD MILLION)
TABLE 5. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY FABRY DISEASE, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 6. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY GAUCHER DISEASE, BY REGION, 2018-2032 (USD MILLION)
TABLE 7. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY GAUCHER DISEASE, BY GROUP, 2018-2032 (USD MILLION)
TABLE 8. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY GAUCHER DISEASE, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 9. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HUNTER SYNDROME, BY REGION, 2018-2032 (USD MILLION)
TABLE 10. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HUNTER SYNDROME, BY GROUP, 2018-2032 (USD MILLION)
TABLE 11. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HUNTER SYNDROME, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 12. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY MUCOPOLYSACCHARIDOSIS, BY REGION, 2018-2032 (USD MILLION)
TABLE 13. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY MUCOPOLYSACCHARIDOSIS, BY GROUP, 2018-2032 (USD MILLION)
TABLE 14. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY MUCOPOLYSACCHARIDOSIS, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 15. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY NIEMANN-PICK DISEASE, BY REGION, 2018-2032 (USD MILLION)
TABLE 16. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY NIEMANN-PICK DISEASE, BY GROUP, 2018-2032 (USD MILLION)
TABLE 17. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY NIEMANN-PICK DISEASE, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 18. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY POMPE DISEASE, BY REGION, 2018-2032 (USD MILLION)
TABLE 19. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY POMPE DISEASE, BY GROUP, 2018-2032 (USD MILLION)
TABLE 20. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY POMPE DISEASE, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 21. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2032 (USD MILLION)
TABLE 22. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, BY REGION, 2018-2032 (USD MILLION)
TABLE 23. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, BY GROUP, 2018-2032 (USD MILLION)
TABLE 24. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 25. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2032 (USD MILLION)
TABLE 26. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY AGALSIDASE BETA, BY REGION, 2018-2032 (USD MILLION)
TABLE 27. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY AGALSIDASE BETA, BY GROUP, 2018-2032 (USD MILLION)
TABLE 28. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY AGALSIDASE BETA, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 29. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ALGLUCERASE, BY REGION, 2018-2032 (USD MILLION)
TABLE 30. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ALGLUCERASE, BY GROUP, 2018-2032 (USD MILLION)
TABLE 31. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ALGLUCERASE, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 32. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ALGLUCOSIDASE ALFA, BY REGION, 2018-2032 (USD MILLION)
TABLE 33. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ALGLUCOSIDASE ALFA, BY GROUP, 2018-2032 (USD MILLION)
TABLE 34. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ALGLUCOSIDASE ALFA, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 35. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY GENE THERAPY, BY REGION, 2018-2032 (USD MILLION)
TABLE 36. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY GENE THERAPY, BY GROUP, 2018-2032 (USD MILLION)
TABLE 37. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY GENE THERAPY, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 38. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, BY REGION, 2018-2032 (USD MILLION)
TABLE 39. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, BY GROUP, 2018-2032 (USD MILLION)
TABLE 40. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 41. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2032 (USD MILLION)
TABLE 42. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ALLOGENEIC TRANSPLANT, BY REGION, 2018-2032 (USD MILLION)
TABLE 43. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ALLOGENEIC TRANSPLANT, BY GROUP, 2018-2032 (USD MILLION)
TABLE 44. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ALLOGENEIC TRANSPLANT, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 45. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY AUTOLOGOUS TRANSPLANT, BY REGION, 2018-2032 (USD MILLION)
TABLE 46. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY AUTOLOGOUS TRANSPLANT, BY GROUP, 2018-2032 (USD MILLION)
TABLE 47. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY AUTOLOGOUS TRANSPLANT, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 48. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, BY REGION, 2018-2032 (USD MILLION)
TABLE 49. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, BY GROUP, 2018-2032 (USD MILLION)
TABLE 50. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY SUBSTRATE REDUCTION THERAPY, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 51. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2032 (USD MILLION)
TABLE 52. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY CARDIOVASCULAR INVOLVEMENT, BY REGION, 2018-2032 (USD MILLION)
TABLE 53. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY CARDIOVASCULAR INVOLVEMENT, BY GROUP, 2018-2032 (USD MILLION)
TABLE 54. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY CARDIOVASCULAR INVOLVEMENT, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 55. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY CENTRAL NERVOUS SYSTEM INVOLVEMENT, BY REGION, 2018-2032 (USD MILLION)
TABLE 56. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY CENTRAL NERVOUS SYSTEM INVOLVEMENT, BY GROUP, 2018-2032 (USD MILLION)
TABLE 57. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY CENTRAL NERVOUS SYSTEM INVOLVEMENT, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 58. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOLOGICAL DISORDERS, BY REGION, 2018-2032 (USD MILLION)
TABLE 59. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOLOGICAL DISORDERS, BY GROUP, 2018-2032 (USD MILLION)
TABLE 60. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOLOGICAL DISORDERS, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 61. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY PULMONARY COMPLICATIONS, BY REGION, 2018-2032 (USD MILLION)
TABLE 62. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY PULMONARY COMPLICATIONS, BY GROUP, 2018-2032 (USD MILLION)
TABLE 63. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY PULMONARY COMPLICATIONS, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 64. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY SKELETAL DEFORMITIES, BY REGION, 2018-2032 (USD MILLION)
TABLE 65. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY SKELETAL DEFORMITIES, BY GROUP, 2018-2032 (USD MILLION)
TABLE 66. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY SKELETAL DEFORMITIES, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 67. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2032 (USD MILLION)
TABLE 68. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ACADEMIC & RESEARCH INSTITUTES, BY REGION, 2018-2032 (USD MILLION)
TABLE 69. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ACADEMIC & RESEARCH INSTITUTES, BY GROUP, 2018-2032 (USD MILLION)
TABLE 70. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ACADEMIC & RESEARCH INSTITUTES, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 71. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY BIOPHARMACEUTICAL COMPANIES, BY REGION, 2018-2032 (USD MILLION)
TABLE 72. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY BIOPHARMACEUTICAL COMPANIES, BY GROUP, 2018-2032 (USD MILLION)
TABLE 73. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY BIOPHARMACEUTICAL COMPANIES, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 74. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HOSPITALS, BY REGION, 2018-2032 (USD MILLION)
TABLE 75. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HOSPITALS, BY GROUP, 2018-2032 (USD MILLION)
TABLE 76. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HOSPITALS, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 77. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY SPECIALTY CLINICS, BY REGION, 2018-2032 (USD MILLION)
TABLE 78. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY SPECIALTY CLINICS, BY GROUP, 2018-2032 (USD MILLION)
TABLE 79. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY SPECIALTY CLINICS, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 80. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY REGION, 2018-2032 (USD MILLION)
TABLE 81. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY SUBREGION, 2018-2032 (USD MILLION)
TABLE 82. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2032 (USD MILLION)
TABLE 83. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2032 (USD MILLION)
TABLE 84. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2032 (USD MILLION)
TABLE 85. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2032 (USD MILLION)
TABLE 86. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2032 (USD MILLION)
TABLE 87. AMERICAS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2032 (USD MILLION)
TABLE 88. NORTH AMERICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 89. NORTH AMERICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2032 (USD MILLION)
TABLE 90. NORTH AMERICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2032 (USD MILLION)
TABLE 91. NORTH AMERICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2032 (USD MILLION)
TABLE 92. NORTH AMERICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2032 (USD MILLION)
TABLE 93. NORTH AMERICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2032 (USD MILLION)
TABLE 94. NORTH AMERICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2032 (USD MILLION)
TABLE 95. LATIN AMERICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 96. LATIN AMERICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2032 (USD MILLION)
TABLE 97. LATIN AMERICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2032 (USD MILLION)
TABLE 98. LATIN AMERICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2032 (USD MILLION)
TABLE 99. LATIN AMERICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2032 (USD MILLION)
TABLE 100. LATIN AMERICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2032 (USD MILLION)
TABLE 101. LATIN AMERICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2032 (USD MILLION)
TABLE 102. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY SUBREGION, 2018-2032 (USD MILLION)
TABLE 103. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2032 (USD MILLION)
TABLE 104. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2032 (USD MILLION)
TABLE 105. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2032 (USD MILLION)
TABLE 106. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2032 (USD MILLION)
TABLE 107. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2032 (USD MILLION)
TABLE 108. EUROPE, MIDDLE EAST & AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2032 (USD MILLION)
TABLE 109. EUROPE LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 110. EUROPE LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2032 (USD MILLION)
TABLE 111. EUROPE LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2032 (USD MILLION)
TABLE 112. EUROPE LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2032 (USD MILLION)
TABLE 113. EUROPE LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2032 (USD MILLION)
TABLE 114. EUROPE LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2032 (USD MILLION)
TABLE 115. EUROPE LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2032 (USD MILLION)
TABLE 116. MIDDLE EAST LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 117. MIDDLE EAST LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2032 (USD MILLION)
TABLE 118. MIDDLE EAST LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2032 (USD MILLION)
TABLE 119. MIDDLE EAST LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2032 (USD MILLION)
TABLE 120. MIDDLE EAST LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2032 (USD MILLION)
TABLE 121. MIDDLE EAST LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2032 (USD MILLION)
TABLE 122. MIDDLE EAST LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2032 (USD MILLION)
TABLE 123. AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 124. AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2032 (USD MILLION)
TABLE 125. AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2032 (USD MILLION)
TABLE 126. AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2032 (USD MILLION)
TABLE 127. AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2032 (USD MILLION)
TABLE 128. AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2032 (USD MILLION)
TABLE 129. AFRICA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2032 (USD MILLION)
TABLE 130. ASIA-PACIFIC LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 131. ASIA-PACIFIC LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2032 (USD MILLION)
TABLE 132. ASIA-PACIFIC LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2032 (USD MILLION)
TABLE 133. ASIA-PACIFIC LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2032 (USD MILLION)
TABLE 134. ASIA-PACIFIC LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2032 (USD MILLION)
TABLE 135. ASIA-PACIFIC LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2032 (USD MILLION)
TABLE 136. ASIA-PACIFIC LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2032 (USD MILLION)
TABLE 137. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY GROUP, 2018-2032 (USD MILLION)
TABLE 138. ASEAN LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 139. ASEAN LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2032 (USD MILLION)
TABLE 140. ASEAN LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2032 (USD MILLION)
TABLE 141. ASEAN LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2032 (USD MILLION)
TABLE 142. ASEAN LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2032 (USD MILLION)
TABLE 143. ASEAN LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2032 (USD MILLION)
TABLE 144. ASEAN LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2032 (USD MILLION)
TABLE 145. GCC LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 146. GCC LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2032 (USD MILLION)
TABLE 147. GCC LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2032 (USD MILLION)
TABLE 148. GCC LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2032 (USD MILLION)
TABLE 149. GCC LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2032 (USD MILLION)
TABLE 150. GCC LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2032 (USD MILLION)
TABLE 151. GCC LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2032 (USD MILLION)
TABLE 152. EUROPEAN UNION LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 153. EUROPEAN UNION LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2032 (USD MILLION)
TABLE 154. EUROPEAN UNION LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2032 (USD MILLION)
TABLE 155. EUROPEAN UNION LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2032 (USD MILLION)
TABLE 156. EUROPEAN UNION LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2032 (USD MILLION)
TABLE 157. EUROPEAN UNION LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2032 (USD MILLION)
TABLE 158. EUROPEAN UNION LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2032 (USD MILLION)
TABLE 159. BRICS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 160. BRICS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2032 (USD MILLION)
TABLE 161. BRICS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2032 (USD MILLION)
TABLE 162. BRICS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2032 (USD MILLION)
TABLE 163. BRICS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2032 (USD MILLION)
TABLE 164. BRICS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2032 (USD MILLION)
TABLE 165. BRICS LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2032 (USD MILLION)
TABLE 166. G7 LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 167. G7 LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2032 (USD MILLION)
TABLE 168. G7 LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2032 (USD MILLION)
TABLE 169. G7 LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2032 (USD MILLION)
TABLE 170. G7 LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2032 (USD MILLION)
TABLE 171. G7 LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2032 (USD MILLION)
TABLE 172. G7 LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2032 (USD MILLION)
TABLE 173. NATO LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 174. NATO LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2032 (USD MILLION)
TABLE 175. NATO LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2032 (USD MILLION)
TABLE 176. NATO LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2032 (USD MILLION)
TABLE 177. NATO LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2032 (USD MILLION)
TABLE 178. NATO LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2032 (USD MILLION)
TABLE 179. NATO LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2032 (USD MILLION)
TABLE 180. GLOBAL LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY COUNTRY, 2018-2032 (USD MILLION)
TABLE 181. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, 2018-2032 (USD MILLION)
TABLE 182. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2032 (USD MILLION)
TABLE 183. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2032 (USD MILLION)
TABLE 184. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2032 (USD MILLION)
TABLE 185. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2032 (USD MILLION)
TABLE 186. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2032 (USD MILLION)
TABLE 187. UNITED STATES LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2032 (USD MILLION)
TABLE 188. CHINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, 2018-2032 (USD MILLION)
TABLE 189. CHINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY DISEASE TYPE, 2018-2032 (USD MILLION)
TABLE 190. CHINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY TREATMENT TYPE, 2018-2032 (USD MILLION)
TABLE 191. CHINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY ENZYME REPLACEMENT THERAPY, 2018-2032 (USD MILLION)
TABLE 192. CHINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY HEMATOPOIETIC STEM CELL TRANSPLANT, 2018-2032 (USD MILLION)
TABLE 193. CHINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY THERAPEUTIC APPLICATION, 2018-2032 (USD MILLION)
TABLE 194. CHINA LYSOSOMAL STORAGE DISEASES MARKET SIZE, BY END-USER, 2018-2032 (USD MILLION)

Companies Mentioned

The key companies profiled in this Lysosomal Storage Diseases market report include:
  • Abeona Therapeutics Inc.
  • Alexion Pharmaceuticals, Inc.
  • Amicus Therapeutics,Inc.
  • ArmaGen, Inc.
  • BioMarin Pharmaceutical, Inc.
  • CHIESI USA, Inc.
  • Denali Therapeutics Inc.
  • Freeline Therapeutics
  • Homology Medicines, Inc.
  • Horizon Pharma PLC
  • Idorsia Pharmaceuticals Ltd.
  • JCR Pharmaceuticals Co., Ltd.
  • Neurogene Inc.
  • Novartis AG
  • Orchard Therapeutics Limited
  • Pfizer Inc.
  • Protalix Biotherapeutics Inc.
  • Sangamo Therapeutics, Inc.
  • Sanofi S.A.
  • Spark Therapeutics, Inc.
  • Swedish Orphan Biovitrum AB
  • Takeda Pharmaceutical Company Limited
  • Ultragenyx Pharmaceutical Inc.
  • Zevra Therapeutics,Inc.

Table Information