Results for tag: "Myozyme"

Myozyme is a drug used to treat endocrine and metabolic disorders. It is a recombinant form of human acid alpha-glucosidase (GAA) enzyme, which is used to treat Pompe disease, a rare genetic disorder. Myozyme is administered intravenously and helps to break down glycogen, a type of sugar, in the body. This helps to reduce the buildup of glycogen in the cells, which can lead to muscle weakness and other symptoms. Myozyme is the only approved treatment for Pompe disease and is used in both adults and children. Myozyme is marketed by Genzyme, a subsidiary of Sanofi, and is available in many countries around the world. Other companies involved in the market include Amicus Therapeutics, Ultragenyx Pharmaceutical, and Audentes Therapeutics. Show Less Read more