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Gene therapy is a form of genomics that involves the introduction of genetic material into a patient's cells to treat or prevent a disease. It is a rapidly growing field of medicine, with the potential to revolutionize the treatment of genetic diseases. Gene therapy works by introducing a healthy gene into a patient's cells, replacing a defective gene or providing a missing gene. This can be done through a variety of methods, such as viral vectors, gene editing, and stem cell therapy.
Gene therapy has the potential to provide long-term, curative treatments for a wide range of genetic diseases, including cancer, cystic fibrosis, and hemophilia. It is also being explored as a potential treatment for other conditions, such as Alzheimer's disease and Parkinson's disease.
Gene therapy is a rapidly growing field, with many companies investing in research and development. Companies in the gene therapy market include Editas Medicine, Intellia Therapeutics, CRISPR Therapeutics, and Spark Therapeutics. Show Less Read more